Academic Journal
Impact of elosulfase alfa treatment on patient-reported outcomes in Morquio syndrome type A: Results from the first year of a managed access agreement in England
| العنوان: | Impact of elosulfase alfa treatment on patient-reported outcomes in Morquio syndrome type A: Results from the first year of a managed access agreement in England |
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| المؤلفون: | Lavery, Christine, Jones, Simon A., Hughes, Derralynn, Murphy, Elaine, Jovanovic, Ana, Hendriksz, Christian J., Cleary, Maureen, Geberhiwot, Tarekegn, Vijay, Suresh |
| المصدر: | Molecular Genetics and Metabolism ; volume 123, issue 2, page S83-S84 ; ISSN 1096-7192 |
| بيانات النشر: | Elsevier BV |
| سنة النشر: | 2018 |
| المجموعة: | ScienceDirect (Elsevier - Open Access Articles via Crossref) |
| نوع الوثيقة: | article in journal/newspaper |
| اللغة: | English |
| DOI: | 10.1016/j.ymgme.2017.12.213 |
| الاتاحة: | http://dx.doi.org/10.1016/j.ymgme.2017.12.213 https://api.elsevier.com/content/article/PII:S1096719217309885?httpAccept=text/xml https://api.elsevier.com/content/article/PII:S1096719217309885?httpAccept=text/plain |
| Rights: | https://www.elsevier.com/tdm/userlicense/1.0/ |
| رقم الانضمام: | edsbas.62A6A560 |
| قاعدة البيانات: | BASE |
| DOI: | 10.1016/j.ymgme.2017.12.213 |
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