Academic Journal

Base editing-mediated splicing correction therapy for spinal muscular atrophy

التفاصيل البيبلوغرافية
العنوان: Base editing-mediated splicing correction therapy for spinal muscular atrophy
المؤلفون: Lin, Xiang, Chen, Haizhu, Lu, Ying-Qian, Hong, Shunyan, Hu, Xinde, Gao, Yanxia, Lai, Lu-Lu, Li, Jin-Jing, Wang, Zishuai, Ying, Wenqin, Ma, Lixiang, Wang, Ning, Zuo, Erwei, Yang, Hui, Chen, Wan-Jin
المصدر: Cell Research ; volume 30, issue 6, page 548-550 ; ISSN 1001-0602 1748-7838
بيانات النشر: Springer Science and Business Media LLC
سنة النشر: 2020
نوع الوثيقة: article in journal/newspaper
اللغة: English
DOI: 10.1038/s41422-020-0304-y
الاتاحة: http://dx.doi.org/10.1038/s41422-020-0304-y
http://www.nature.com/articles/s41422-020-0304-y.pdf
http://www.nature.com/articles/s41422-020-0304-y
Rights: http://www.springer.com/tdm ; http://www.springer.com/tdm
رقم الانضمام: edsbas.38B16913
قاعدة البيانات: BASE
الوصف
DOI:10.1038/s41422-020-0304-y