Academic Journal
Base editing-mediated splicing correction therapy for spinal muscular atrophy
العنوان: | Base editing-mediated splicing correction therapy for spinal muscular atrophy |
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المؤلفون: | Lin, Xiang, Chen, Haizhu, Lu, Ying-Qian, Hong, Shunyan, Hu, Xinde, Gao, Yanxia, Lai, Lu-Lu, Li, Jin-Jing, Wang, Zishuai, Ying, Wenqin, Ma, Lixiang, Wang, Ning, Zuo, Erwei, Yang, Hui, Chen, Wan-Jin |
المصدر: | Cell Research ; volume 30, issue 6, page 548-550 ; ISSN 1001-0602 1748-7838 |
بيانات النشر: | Springer Science and Business Media LLC |
سنة النشر: | 2020 |
نوع الوثيقة: | article in journal/newspaper |
اللغة: | English |
DOI: | 10.1038/s41422-020-0304-y |
الاتاحة: | http://dx.doi.org/10.1038/s41422-020-0304-y http://www.nature.com/articles/s41422-020-0304-y.pdf http://www.nature.com/articles/s41422-020-0304-y |
Rights: | http://www.springer.com/tdm ; http://www.springer.com/tdm |
رقم الانضمام: | edsbas.38B16913 |
قاعدة البيانات: | BASE |
DOI: | 10.1038/s41422-020-0304-y |
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