Academic Journal
Effect of velmanase alfa (human recombinant alpha-mannosidase) enzyme-replacement therapy on quality of life and disease burden of patients with alpha-mannosidosis: Results from caregiver feedback
| العنوان: | Effect of velmanase alfa (human recombinant alpha-mannosidase) enzyme-replacement therapy on quality of life and disease burden of patients with alpha-mannosidosis: Results from caregiver feedback |
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| المؤلفون: | Lund, Allan, Guffon, Nathalie, Gil-Campos, Mercedes, Cattaneo, Frederica, Heron, Benedicte, Tylki-Szymanska, Anna, Borgwardt, Line, Regal, Luc, Cole, Duncan, Hennermann, Julia |
| المصدر: | Molecular Genetics and Metabolism ; volume 132, issue 2, page S67 ; ISSN 1096-7192 |
| بيانات النشر: | Elsevier BV |
| سنة النشر: | 2021 |
| المجموعة: | ScienceDirect (Elsevier - Open Access Articles via Crossref) |
| نوع الوثيقة: | article in journal/newspaper |
| اللغة: | English |
| DOI: | 10.1016/j.ymgme.2020.12.153 |
| الاتاحة: | http://dx.doi.org/10.1016/j.ymgme.2020.12.153 https://api.elsevier.com/content/article/PII:S1096719220304212?httpAccept=text/xml https://api.elsevier.com/content/article/PII:S1096719220304212?httpAccept=text/plain |
| Rights: | https://www.elsevier.com/tdm/userlicense/1.0/ |
| رقم الانضمام: | edsbas.37C4EBE1 |
| قاعدة البيانات: | BASE |
| DOI: | 10.1016/j.ymgme.2020.12.153 |
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