Academic Journal
Ex vivo lentiviral transduction of hematopoietic stem cells in mucopolysaccharidosis type II (MPS II) mice achieves high levels of systemic iduronate-2-sulfatase (IDS) enzyme activity and normalization of glycosaminoglycans (GAGs)
| العنوان: | Ex vivo lentiviral transduction of hematopoietic stem cells in mucopolysaccharidosis type II (MPS II) mice achieves high levels of systemic iduronate-2-sulfatase (IDS) enzyme activity and normalization of glycosaminoglycans (GAGs) |
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| المؤلفون: | Smith, Miles C., Belur, Lalitha, Erlanson, Olivia, Podetz-Pedersen, Kelly, Karlen, Andrea, McKenzie, Jessica, Detellis, Jenn, Gagnidze, Khatuna, Parsons, Geoff, Robinson, Nick, Labarre, Shelby, Scarglia, Gina, Shah, Saumil, Tsai, Hsing-Chen, McIvor, R. Scott, Bonner, Melissa |
| المصدر: | Molecular Genetics and Metabolism ; volume 132, issue 2, page S102 ; ISSN 1096-7192 |
| بيانات النشر: | Elsevier BV |
| سنة النشر: | 2021 |
| المجموعة: | ScienceDirect (Elsevier - Open Access Articles via Crossref) |
| نوع الوثيقة: | article in journal/newspaper |
| اللغة: | English |
| DOI: | 10.1016/j.ymgme.2020.12.247 |
| الاتاحة: | http://dx.doi.org/10.1016/j.ymgme.2020.12.247 https://api.elsevier.com/content/article/PII:S1096719220305151?httpAccept=text/xml https://api.elsevier.com/content/article/PII:S1096719220305151?httpAccept=text/plain |
| Rights: | https://www.elsevier.com/tdm/userlicense/1.0/ |
| رقم الانضمام: | edsbas.2BF4A0E0 |
| قاعدة البيانات: | BASE |
| DOI: | 10.1016/j.ymgme.2020.12.247 |
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