التفاصيل البيبلوغرافية
العنوان: |
Effect of nusinersen after 3 years of treatment in 57 young children with SMA in terms of SMN2 copy number or type |
المؤلفون: |
Audic, Frédérique, Dubois, Sonia M., Durigneux, Julien, Barnerias, Christine, Isapof, Arnaud, Nougues, Marie-Christine, Davion, Jean-Baptiste, Richelme, Christian, Vuillerot, Carole, Legoff, Laure, Sabouraud, Pascal, Cances, Claude, Laugel, Vincent, Ropars, Juliette, Espil-Taris, Caroline, Trommsdorff, Valérie, Pervillé, Anne, Garcia-de-la-Banda, Marta Gomez, Testard, Hervé, Chouchane, Mondher, Walther-Louvier, Ulrike, Schweizer, Cyril, Halbert, Cécile, Badri, Myriam, Quijano-Roy, Susana, Chabrol, Brigitte, Desguerre, Isabelle |
المصدر: |
Archives de Pédiatrie ; volume 31, issue 2, page 117-123 ; ISSN 0929-693X |
بيانات النشر: |
Elsevier BV |
سنة النشر: |
2024 |
المجموعة: |
ScienceDirect (Elsevier - Open Access Articles via Crossref) |
نوع الوثيقة: |
article in journal/newspaper |
اللغة: |
English |
DOI: |
10.1016/j.arcped.2023.10.009 |
الاتاحة: |
http://dx.doi.org/10.1016/j.arcped.2023.10.009 https://api.elsevier.com/content/article/PII:S0929693X23002117?httpAccept=text/xml https://api.elsevier.com/content/article/PII:S0929693X23002117?httpAccept=text/plain |
Rights: |
https://www.elsevier.com/tdm/userlicense/1.0/ |
رقم الانضمام: |
edsbas.281EDB03 |
قاعدة البيانات: |
BASE |