CRISPR/Cas9-mediated editing for dominant genetic disorders: efficient excision of trinucleotide repeat expansion in myotonic dystrophy

التفاصيل البيبلوغرافية
العنوان: CRISPR/Cas9-mediated editing for dominant genetic disorders: efficient excision of trinucleotide repeat expansion in myotonic dystrophy
المؤلفون: Dastidar, S., Ardui, S., Singh, K., Nair, N., Fu, Y., Reyon, D., Samara, E., Gerli, M. F. M., Klein, A. F., DeSchrijver, W., Majumdar, D., Tipanee, J., Seneca, S., Tulalamba, W., Wang, H., Chai, Y. C., In't Veld, P., Furling, D., Tedesco, F. S., Vermeesch, J. R., Joung, J. K., Chuah, M. K., VandenDriessche, T.
المساهمون: Faculty of Medicine and Pharmacy, Basic (bio-) Medical Sciences, Division of Gene Therapy & Regenerative Medicine, Physics, Medicine and Pharmacy academic/administration, Faculty of Sciences and Bioengineering Sciences, Clinical sciences, Medical Genetics, Reproduction and Genetics, Experimental Pathology, Pathology/molecular and cellular medicine, Diabetes Pathology & Therapy, Vrije Universiteit Brussel
سنة النشر: 2017
اللغة: English
URL الوصول: https://explore.openaire.eu/search/publication?articleId=od______3848::d64f4670d4aa4f13802ff277599a49b5
https://biblio.vub.ac.be/vubir/crisprcas9mediated-editing-for-dominant-genetic-disorders-efficient-excision-of-trinucleotide-repeat-expansion-in-myotonic-dystrophy(6e85b2b3-07af-404e-b79d-b3c83653a6e0).html
Rights: RESTRICTED
رقم الانضمام: edsair.od......3848..d64f4670d4aa4f13802ff277599a49b5
قاعدة البيانات: OpenAIRE