Academic Journal

DEVOTE Study Exploring Higher Dose of Nusinersen in Spinal Muscular Atrophy: Study Design and Part A Results.

التفاصيل البيبلوغرافية
العنوان: DEVOTE Study Exploring Higher Dose of Nusinersen in Spinal Muscular Atrophy: Study Design and Part A Results.
المؤلفون: Finkel, Richard S., Day, John W., Pascual Pascual, Samuel Ignacio, Ryan, Monique M., Mercuri, Eugenio, De Vivo, Darryl C., Montes, Jacqueline, Gurgel-Giannetti, Juliana, Monine, Michael, Gambino, Giulia, Makepeace, Corinne, Foster, Richard, Berger, Zdenek
المصدر: Journal of Neuromuscular Diseases; 2023, Vol. 10 Issue 5, p813-823, 11p
قاعدة البيانات: Complementary Index
الوصف
تدمد:22143599
DOI:10.3233/JND-221667