Conference
S61 Onasemnogene abeparvovec gene-replacement therapy (GRT) for spinal muscular atrophy type 1 (SMA1): preliminary pulmonary and ventilatory findings from the phase 3 study (STR1VE)
| العنوان: | S61 Onasemnogene abeparvovec gene-replacement therapy (GRT) for spinal muscular atrophy type 1 (SMA1): preliminary pulmonary and ventilatory findings from the phase 3 study (STR1VE) |
|---|---|
| المؤلفون: | Shell, R, Day, JW, Chiriboga, CA, Crawford, TO, Darras, BT, Finkel, RS, Connolly, AM, Iannaccone, ST, Kuntz, NL, Peña, LDM, Shieh, PB, Smith, EC, Kausar, I, Schultz, M, Feltner, DE, Ogrinc, FG, Macek, TA, Kernbauer, E, L’Italien, J, Sproule, DM, Kaspar, BK, Mendell, JR |
| المصدر: | Diagnostic and therapeutic advances in paediatrics ; page A42.1-A42 |
| بيانات النشر: | BMJ Publishing Group Ltd and British Thoracic Society |
| سنة النشر: | 2019 |
| نوع الوثيقة: | conference object |
| اللغة: | unknown |
| DOI: | 10.1136/thorax-2019-btsabstracts2019.67 |
| DOI: | 10.1136/thorax-2019-BTSabstracts2019.67 |
| الاتاحة: | http://dx.doi.org/10.1136/thorax-2019-btsabstracts2019.67 https://syndication.highwire.org/content/doi/10.1136/thorax-2019-BTSabstracts2019.67 |
| رقم الانضمام: | edsbas.42C8A357 |
| قاعدة البيانات: | BASE |
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