المؤلفون: Brugada Vilà, Pau

المساهمون: University/Department: Universitat Ramon Llull. IQS SE - Bioenginyeria

Thesis Advisors: Borrós i Gómez, Salvador, Cascante Cirera, Anna, Fillat Fonts, Cristina

المصدر: TDX (Tesis Doctorals en Xarxa)

مصطلحات موضوعية: Virotherapy, Gene therapy, Oncology, Viral vectors, Biomaterials, Surface engineering, Ciències naturals, químiques, físiques i matemàtiques

وصف الملف: application/pdf

URL الوصول: http://hdl.handle.net/10803/664008

المؤلفون: Patil, Shruti, Kaipa, Balasankara, Ranshing, Sujata, Sundaresan, Yogapriya, Millar, J, Nagarajan, Bhavani, Kiehlbauch, Charles, Zhang, Qihong, Jain, Ankur, Searby, Charles, Scheetz, Todd, Clark, Abbot, Sheffield, Val, Zode, Gulab

المصدر: Scientific Reports. 14(1)

مصطلحات موضوعية: ER stress, Gene therapy, Genome editing for glaucoma, Intraocular pressure, Lentiviral particles, Myocilin-associated Glaucoma, Trabecular meshwork, Viral vectors, Animals, Mice, CRISPR-Cas Systems, Cytoskeletal Proteins, Disease Models, Animal, Eye Proteins, Glaucoma, Open-Angle, Glycoproteins, Intraocular Pressure, Lentivirus, Trabecular Meshwork

وصف الملف: application/pdf

URL الوصول: https://escholarship.org/uc/item/3s33307s
https://escholarship.org/content/qt3s33307s/qt3s33307s.pdf

المؤلفون: Pagès i Pi, Gemma

المساهمون: University/Department: Universitat Autònoma de Barcelona. Departament de Bioquímica i Biologia Molecular

Thesis Advisors: Bosch Merino, Assumpció

المصدر: TDX (Tesis Doctorals en Xarxa)

مصطلحات موضوعية: Mucopolisacaridosi tipus VII, Mucopolisacaridosis tipo VII, Mucopolysaccharidosis type VII, Vectors virals adeno-associats, Vectores virales adeno-asociados, Adeno-associated viral vectors, Ciències Experimentals

وصف الملف: application/pdf

URL الوصول: http://hdl.handle.net/10803/300733

المؤلفون: Shirin Eshghi, Mahsa Mousakhan Bakhtiari, Maryam Behfar, Elaheh Izadi, Parisa Naji, Leila Jafari, Rashin Mohseni, Zohreh Saltanatpour, Amir Ali Hamidieh

المصدر: Regenerative Therapy, Vol 28, Iss , Pp 262-279 (2025)

مصطلحات موضوعية: Gene therapy, Viral gene delivery, Viral vectors, Clinical trials, Immune deficiency, Blood disorder, Medicine (General), R5-920, Cytology, QH573-671

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S235232042400227X; https://doaj.org/toc/2352-3204

URL الوصول: https://doaj.org/article/68f9323a24f244809185d7ffa88ffb1e

المؤلفون: Guan JX, Wang YL, Wang JL

المصدر: International Journal of Nanomedicine, Vol Volume 19, Pp 9273-9289 (2024)

مصطلحات موضوعية: nanoparticles, subretinal injection, drug delivery, non-viral vectors, nanomedicine, gene therapy, Medicine (General), R5-920

وصف الملف: electronic resource

Relation: https://www.dovepress.com/how-advanced-are-nanocarriers-for-effective-subretinal-injection-peer-reviewed-fulltext-article-IJN; https://doaj.org/toc/1178-2013

URL الوصول: https://doaj.org/article/a04e15dcbb294c86a975436a991b7e65

المؤلفون: Borgo, Gina M, Rutishauser, Rachel L

المصدر: Current Opinion in HIV and AIDS. 18(6)

مصطلحات موضوعية: Medical Microbiology, Biomedical and Clinical Sciences, Immunology, Prevention, Sexually Transmitted Infections, Women's Health, Biotechnology, Vaccine Related, Immunization, Vaccine Related (AIDS), Infectious Diseases, HIV/AIDS, 3.4 Vaccines, Infection, Good Health and Well Being, Humans, AIDS Vaccines, HIV Infections, CD8-Positive T-Lymphocytes, Genetic Vectors, Epitopes, CD8(+) T cell, HIV vaccine, nucleic acid vaccine platforms, T cell quality, viral vectors, Public Health and Health Services, Virology, Clinical sciences, Medical microbiology, Epidemiology

وصف الملف: application/pdf

URL الوصول: https://escholarship.org/uc/item/80c1v3w5
https://escholarship.org/content/qt80c1v3w5/qt80c1v3w5.pdf

المؤلفون: Nadia Tavakolidakhrabadi, Wen Y. Ding, Moin A. Saleem, Gavin I. Welsh, Carl May

المصدر: Molecular Therapy: Methods & Clinical Development, Vol 32, Iss 4, Pp 101333- (2024)

مصطلحات موضوعية: gene therapy, kidney disease, targeted gene delivery, viral vectors, nanodelivery systems, Genetics, QH426-470, Cytology, QH573-671

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050124001499; https://doaj.org/toc/2329-0501

URL الوصول: https://doaj.org/article/35ec8e53f7f8421a86be1722d96a5daf

المؤلفون: Gabriel Dagotto, Jana L. Fisher, David Li, Zhenyu Li, Simon Jenni, Zongli Li, Lawrence J. Tartaglia, Peter Abbink, Dan H. Barouch

المصدر: Molecular Therapy: Methods & Clinical Development, Vol 32, Iss 4, Pp 101350- (2024)

مصطلحات موضوعية: adeno-associated virus, AAV, capsid neutralization epitope, anti-vector immunity, viral vectors, novel AAV capsid discovery, Genetics, QH426-470, Cytology, QH573-671

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050124001669; https://doaj.org/toc/2329-0501

URL الوصول: https://doaj.org/article/bb79628a310c4d358f90adeb46aad779

المؤلفون: Stahl, Elizabeth, Sabo, Jennifer, Kang, Min, Allen, Ryan, Applegate, Elizabeth, Kim, Shin, Kwon, Yoonjin, Seth, Anmol, Lemus, Nicholas, Salinas-Rios, Viviana, Soczek, Katarzyna, Trinidad, Marena, Vo, Linda, Jeans, Chris, Wozniak, Anna, Morris, Timothy, Kimberlin, Athen, Foti, Thomas, Savage, David, Doudna, Jennifer

المصدر: Molecular Therapy. 31(8)

مصطلحات موضوعية: CRISPR-Cas9, brain, endotoxin/LPS, genome editing, host immune response, microglia, mouse, neurons, non-viral delivery, viral vectors, Animals, Mice, Gene Editing, CRISPR-Cas Systems, Ribonucleoproteins, CRISPR-Associated Protein 9, Brain

وصف الملف: application/pdf

URL الوصول: https://escholarship.org/uc/item/5f39h490
https://escholarship.org/content/qt5f39h490/qt5f39h490.pdf

المؤلفون: Gabriella Guelfi, Camilla Capaccia, Polina Anipchenko, Francesco Ciancabilla, Oommen Podiyan Oommen, Antonello Bufalari, Massimo Zerani, Margherita Maranesi

المصدر: Macromol, Vol 4, Iss 2, Pp 165-189 (2024)

مصطلحات موضوعية: mimic miRNA, anti-miRNA, viral vectors, non-viral vectors, 3D scaffold, bone regeneration, Chemical technology, TP1-1185, Biochemistry, QD415-436

وصف الملف: electronic resource

Relation: https://www.mdpi.com/2673-6209/4/2/9; https://doaj.org/toc/2673-6209

URL الوصول: https://doaj.org/article/05445fbcfd294db1b9e790d17bc1f923

المؤلفون: Ashish Khaparde, Grace P Mathias, B Poornachandra, M B Thirumalesh, Rohit Shetty, Arkasubhra Ghosh

المصدر: Indian Journal of Ophthalmology, Vol 72, Iss 8, Pp 1091-1101 (2024)

مصطلحات موضوعية: clinical trials, inherited retinal disorders, retinal gene therapy, viral vectors, Ophthalmology, RE1-994

وصف الملف: electronic resource

Relation: https://journals.lww.com/10.4103/IJO.IJO_2902_23; https://doaj.org/toc/0301-4738; https://doaj.org/toc/1998-3689

URL الوصول: https://doaj.org/article/6c1c05b394bf4243a2cb6fdb17943791

المؤلفون: Olivier Dionne, Salomé Sabatié, Fléchère Fortin, François Corbin, Benoit Laurent

المصدر: Frontiers in Cell and Developmental Biology, Vol 12 (2024)

مصطلحات موضوعية: reprogramming, urine, Fragile X syndrome, Sendai viral vectors, induced pluripotent stem cells, Biology (General), QH301-705.5

وصف الملف: electronic resource

Relation: https://www.frontiersin.org/articles/10.3389/fcell.2024.1489190/full; https://doaj.org/toc/2296-634X

URL الوصول: https://doaj.org/article/158b4d9480644760bbd3c644070748e8

المؤلفون: Jason M. Tonne, Karol Budzik, Talia Fernandez Carrasco, Landon Ebbert, Jill Thompson, Rebecca Nace, Benjamin Kendall, Rosa M. Diaz, Stephen J. Russell, Richard G. Vile

المصدر: Molecular Therapy: Oncology, Vol 32, Iss 3, Pp 200852- (2024)

مصطلحات موضوعية: MT: Regular Issue, CAR T-cell, Simian foamy virus, cancer, oncolytic virotherapy, viral vectors, Neoplasms. Tumors. Oncology. Including cancer and carcinogens, RC254-282

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2950329924000948; https://doaj.org/toc/2950-3299

URL الوصول: https://doaj.org/article/32c9747a81a4467cac125fdb100cfb25

المؤلفون: Anna Mateu-Bosch, Eulàlia Segur-Bailach, Emma Muñoz-Moreno, María José Barallobre, Maria Lourdes Arbonés, Sabrina Gea-Sorlí, Frederic Tort, Antonia Ribes, Judit García-Villoria, Cristina Fillat

المصدر: Molecular Therapy: Methods & Clinical Development, Vol 32, Iss 3, Pp 101276- (2024)

مصطلحات موضوعية: glutaric aciduria, metabolic disease, viral vectors, gene replacement, adeno-associated virus, AAV, Genetics, QH426-470, Cytology, QH573-671

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050124000925; https://doaj.org/toc/2329-0501

URL الوصول: https://doaj.org/article/592b220094f1481fa456c9ea81e1525a

المؤلفون: Robert D.E. Clark, Felix Rabito, Ferris T. Munyonho, T. Parks Remcho, Jay K. Kolls

المصدر: Molecular Therapy: Methods & Clinical Development, Vol 32, Iss 3, Pp 101286- (2024)

مصطلحات موضوعية: cystic fibrosis, inhaled gene therapy, viral vectors, anti-CD20, host immune response, adenovirus, Genetics, QH426-470, Cytology, QH573-671

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050124001025; https://doaj.org/toc/2329-0501

URL الوصول: https://doaj.org/article/472d5f630d7b4844bbaea67e9bc44cca

المؤلفون: Campos, Lillian J, Arokiaraj, Cynthia M, Chuapoco, Miguel R, Chen, Xinhong, Goeden, Nick, Gradinaru, Viviana, Fox, Andrew S

مصطلحات موضوعية: Adeno-associated viral vectors, Brain, Capsid variants, Enhancers, Gene delivery, Nonhuman primate, Genetics, Neurosciences, Gene Therapy, Biotechnology, Neurological

URL الوصول: https://escholarship.org/uc/item/91f409j9

المؤلفون: Mohadeseh Khoshandam, Hossein Soltaninejad, Marziyeh Mousazadeh, Amir Ali Hamidieh, Saman Hosseinkhani

المصدر: Genes and Diseases, Vol 11, Iss 1, Pp 268-282 (2024)

مصطلحات موضوعية: Clinical trials, CRISPR/Cas9, Gene therapy, Non-viral vectors, Viral vectors, Medicine (General), R5-920, Genetics, QH426-470

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S235230422300079X; https://doaj.org/toc/2352-3042

URL الوصول: https://doaj.org/article/a480fc411a3e49abb2d077a999880501

المؤلفون: Jonathan J. Campbell, Neil Almond, Young-Kyong Bae, Ravneet Bhuller, Andrea Briones, Sang-Joon Cho, Megan H. Cleveland, Thomas E. Cleveland, Francis Galaway, Hua-Jun He, Ulrike Herbrand, Jim F. Huggett, Sarah Kempster, Ibolya E. Kepiro, Arifa S. Khan, Edward Kwee, Wilson Li, Sheng Lin-Gibson, Luise Luckau, Caterina Minelli, Maxim G. Ryadnov, Isobel Searing, Lili Wang, Alexandra S. Whale, Julian H. Braybrook

المصدر: Biologics, Vol 4, Iss 2, Pp 187-201 (2024)

مصطلحات موضوعية: viral vectors, metrology, standards, measurement, analytical methods, characterisation, Biology (General), QH301-705.5

وصف الملف: electronic resource

Relation: https://www.mdpi.com/2673-8449/4/2/13; https://doaj.org/toc/2673-8449

URL الوصول: https://doaj.org/article/74b849504e464deaa369ec4a4b340589

المؤلفون: I. H. Shaikhutdinov, P. V. Ilyasov, O. V. Gribkova, L. V. Limareva

المصدر: Вавиловский журнал генетики и селекции, Vol 28, Iss 2, Pp 239-248 (2024)

مصطلحات موضوعية: metal-organic frameworks, vesicles, nanoparticles, viral vectors, gene editing, Genetics, QH426-470

وصف الملف: electronic resource

Relation: https://vavilov.elpub.ru/jour/article/view/4094; https://doaj.org/toc/2500-3259

URL الوصول: https://doaj.org/article/c9ccc75028a24fdfb002c0c5de33cfb3

المؤلفون: Shruti V. Patil, Balasankara Reddy Kaipa, Sujata Ranshing, Yogapriya Sundaresan, J. Cameron Millar, Bhavani Nagarajan, Charles Kiehlbauch, Qihong Zhang, Ankur Jain, Charles C. Searby, Todd E. Scheetz, Abbot F. Clark, Val C. Sheffield, Gulab S. Zode

المصدر: Scientific Reports, Vol 14, Iss 1, Pp 1-13 (2024)

مصطلحات موضوعية: Myocilin-associated Glaucoma, Gene therapy, Genome editing for glaucoma, Trabecular meshwork, Intraocular pressure, Viral vectors, Medicine, Science

وصف الملف: electronic resource

Relation: https://doaj.org/toc/2045-2322

URL الوصول: https://doaj.org/article/30e1fedfb0d445a39df2b98bbdbfd4a5