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1Academic Journal
المؤلفون: Saba Shahin, Hui Xu, Bin Lu, Augustus Mercado, Melissa K. Jones, Benjamin Bakondi, Shaomei Wang
المصدر: Pharmaceutics; Volume 14; Issue 4; Pages: 824
مصطلحات موضوعية: autosomal dominant retinitis pigmentosa, Rhodopsin P23H, CRISPR/Cas9, AAV delivery, allele-specific ablation, photoreceptors, rod cells, ER-stress, autophagy, long-term vision preservation
وصف الملف: application/pdf
Relation: Drug Delivery and Controlled Release; https://dx.doi.org/10.3390/pharmaceutics14040824