المؤلفون: Strauss, Kevin A, Farrar, Michelle A, Muntoni, Francesco, Saito, Kayoko, Mendell, Jerry R, Servais, Laurent, McMillan, Hugh J, Finkel, Richard S, Swoboda, Kathryn J, Kwon, Jennifer M, Zaidman, Craig M, Chiriboga, Claudia A, Iannaccone, Susan T, Krueger, Jena M, Parsons, Julie A, Shieh, Perry B, Kavanagh, Sarah, Wigderson, Melissa, Tauscher-Wisniewski, Sitra, McGill, Bryan E, Macek, Thomas A

المساهمون: Molecular, Cell and Cancer Biology, Pediatrics

المصدر: Nature medicine ; 28 ; 7 ; 1390 ; 1397 ; United States

مصطلحات موضوعية: Development, Gene therapy

Relation: Nature Medicine; https://doi.org/10.1038/s41591-022-01867-3; Strauss KA, Farrar MA, Muntoni F, Saito K, Mendell JR, Servais L, McMillan HJ, Finkel RS, Swoboda KJ, Kwon JM, Zaidman CM, Chiriboga CA, Iannaccone ST, Krueger JM, Parsons JA, Shieh PB, Kavanagh S, Wigderson M, Tauscher-Wisniewski S, McGill BE, Macek TA. Onasemnogene abeparvovec for presymptomatic infants with three copies of SMN2 at risk for spinal muscular atrophy: the Phase III SPR1NT trial. Nat Med. 2022 Jul;28(7):1390-1397. doi:10.1038/s41591-022-01867-3. Epub 2022 Jun 17. PMID: 35715567; PMCID: PMC9205287.; http://hdl.handle.net/20.500.14038/52709

الاتاحة: https://doi.org/10.1038/s41591-022-01867-3
https://hdl.handle.net/20.500.14038/52709

المؤلفون: Strauss, Kevin A, Farrar, Michelle A, Muntoni, Francesco, Saito, Kayoko, Mendell, Jerry R, Servais, Laurent, McMillan, Hugh J, Finkel, Richard S, Swoboda, Kathryn J, Kwon, Jennifer M, Zaidman, Craig M, Chiriboga, Claudia A, Iannaccone, Susan T, Krueger, Jena M, Parsons, Julie A, Shieh, Perry B, Kavanagh, Sarah, Wigderson, Melissa, Tauscher-Wisniewski, Sitra, McGill, Bryan E, Macek, Thomas A

المصدر: Nature Medicine (2022) (In press).

مصطلحات موضوعية: Science & Technology, Life Sciences & Biomedicine, Biochemistry & Molecular Biology, Cell Biology, Medicine, Research & Experimental, Research & Experimental Medicine, GENE-THERAPY, GENOMIC MEDICINE, NATURAL-HISTORY, COPY NUMBER, SINGLE-ARM, OPEN-LABEL, SMA, TYPE-2, MULTICENTER

وصف الملف: application/pdf

Relation: https://discovery.ucl.ac.uk/id/eprint/10151103/1/s41591-022-01867-3.pdf; https://discovery.ucl.ac.uk/id/eprint/10151103/

الاتاحة: https://discovery.ucl.ac.uk/id/eprint/10151103/1/s41591-022-01867-3.pdf
https://discovery.ucl.ac.uk/id/eprint/10151103/

المؤلفون: Heerspink, Hiddo J L, Parving, Hans-Henrik, Andress, Dennis L, Bakris, George, Correa-Rotter, Ricardo, Hou, Fan-Fan, Kitzman, Dalane W, Kohan, Donald, Makino, Hirofumi, McMurray, John J V, Melnick, Joel Z, Miller, Michael G, Pergola, Pablo E, Perkovic, Vlado, Tobe, Sheldon, Yi, Tingting, Wigderson, Melissa, de Zeeuw, Dick, SONAR Committees and Investigators, Jadoul, Michel

المساهمون: UCL - SSS/IREC/NEFR - Pôle de Néphrologie, UCL - (SLuc) Service de néphrologie

المصدر: Lancet, Vol. 393, no. 10184, p. 1937-1947 (2019)

مصطلحات موضوعية: General Medicine

Relation: boreal:221788; http://hdl.handle.net/2078.1/221788; info:pmid/; urn:ISSN:0140-6736; urn:EISSN:1474-547X

الاتاحة: http://hdl.handle.net/2078.1/221788
https://doi.org/10.1016/s0140-6736(19)30772-x

المؤلفون: Mendell, Jerry, Wigderson, Melissa, Alecu, Iulian, Yang, Lina, Mehl, Lesa, Connolly, Anne

المصدر: Neurology ; volume 100, issue 17_supplement_2 ; ISSN 0028-3878 1526-632X

الاتاحة: http://dx.doi.org/10.1212/wnl.0000000000202549
https://syndication.highwire.org/content/doi/10.1212/WNL.0000000000202549

المؤلفون: Darras, Basil, Mercuri, Eugenio, Strauss, Kevin, Day, John, Chien, Yin-Hsiu, Masson, Ricardo, Wigderson, Melissa, Alecu, Iulian, Ballarini, Nicolas, Mehl, Lesa, Marra, Jonathan, Connolly, Anne

المصدر: Neurology ; volume 100, issue 17_supplement_2 ; ISSN 0028-3878 1526-632X

الاتاحة: http://dx.doi.org/10.1212/wnl.0000000000202555
https://syndication.highwire.org/content/doi/10.1212/WNL.0000000000202555

المؤلفون: Heerspink, Hiddo J L, Andress, Dennis L, Bakris, George, Brennan, John J, Correa-Rotter, Ricardo, Dey, Jyotirmoy, Hou, Fan Fan, Kitzman, Dalane W, Kohan, Donald, Makino, Hirofumi, McMurray, John, Perkovic, Vlado, Tobe, Sheldon, Wigderson, Melissa, Parving, Hans-Henrik, de Zeeuw, Dick

المصدر: Heerspink , H J L , Andress , D L , Bakris , G , Brennan , J J , Correa-Rotter , R , Dey , J , Hou , F F , Kitzman , D W , Kohan , D , Makino , H , McMurray , J , Perkovic , V , Tobe , S , Wigderson , M , Parving , H-H & de Zeeuw , D 2018 , ' Rationale and protocol of the Study Of diabetic Nephropathy with AtRasentan (SONAR) trial : A clinical trial design novel to diabetic nephropathy ' , Diabetes obesity ....

مصطلحات موضوعية: PREDICTORS, ANTAGONIST, CHRONIC KIDNEY-DISEASE, MULTIPLE RISK MARKERS, HEART-FAILURE, ALBUMINURIA, INHIBITION

وصف الملف: application/pdf

الاتاحة: https://hdl.handle.net/11370/783a33a7-6f18-4967-aefd-5d6243ee5ef3
https://research.rug.nl/en/publications/783a33a7-6f18-4967-aefd-5d6243ee5ef3
https://doi.org/10.1111/dom.13245
https://pure.rug.nl/ws/files/66219909/Heerspink_et_al_2018_Diabetes_2C_Obesity_and_Metabolism_1_.pdf

المؤلفون: Heerspink, Hiddo J L, Andress, Dennis L, Bakris, George, Brennan, John J, Correa-Rotter, Ricardo, Hou, Fan Fan, Kitzman, Dalane W, Kohan, Donald, Makino, Hirofumi, McMurray, John, Perkovic, Vlado, Tobe, Sheldon, Wigderson, Melissa, Yi, Tingting, Parving, Hans-Henrik, de Zeeuw, Dick

المصدر: Heerspink , H J L , Andress , D L , Bakris , G , Brennan , J J , Correa-Rotter , R , Hou , F F , Kitzman , D W , Kohan , D , Makino , H , McMurray , J , Perkovic , V , Tobe , S , Wigderson , M , Yi , T , Parving , H-H & de Zeeuw , D 2018 , ' Baseline characteristics and enrichment results from the SONAR trial ' , Diabetes obesity & metabolism , vol. 20 , no. 8 , pp. 1829-1835 . https://doi.org/10.1111/dom.13315

وصف الملف: application/pdf

Relation: https://research.rug.nl/en/publications/ce19db3b-4642-4b2a-acd6-e83ff4baf925

الاتاحة: https://hdl.handle.net/11370/ce19db3b-4642-4b2a-acd6-e83ff4baf925
https://research.rug.nl/en/publications/ce19db3b-4642-4b2a-acd6-e83ff4baf925
https://doi.org/10.1111/dom.13315
https://pure.rug.nl/ws/files/66213499/Heerspink_et_al_2018_Diabetes_2C_Obesity_and_Metabolism.pdf

المؤلفون: Heerspink, Hiddo J.L., Andress, Dennis L., Bakris, George, Brennan, John J., Correa-Rotter, Ricardo, Hou, Fan Fan, Kitzman, Dalane W., Kohan, Donald, Makino, Hirofumi, McMurray, John, Perkovic, Vlado, Tobe, Sheldon, Wigderson, Melissa, Yi, Tingting, Parving, Hans-Henrik, de Zeeuw, Dick

وصف الملف: text

Relation: http://eprints.gla.ac.uk/160155/13/160155.pdf; Heerspink, H. J.L. et al. (2018) Baseline characteristics and enrichment results from the SONAR trial. Diabetes, Obesity and Metabolism , 20(8), pp. 1829-1835. (doi:10.1111/dom.13315 ) (PMID:29604160)

الاتاحة: http://eprints.gla.ac.uk/160155/
http://eprints.gla.ac.uk/160155/13/160155.pdf

المؤلفون: Heerspink, Hiddo J.L., Andress, Dennis L., Bakris, George, Brennan, John J., Correa-Rotter, Ricardo, Dey, Jyotirmoy, Hou, Fan-Fan, Kitzman, Dalane W., Kohan, Donald, Makino, Hirofumi, McMurray, John, Perkovic, Vlado, Tobe, Sheldon, Wigderson, Melissa, Parving, Hans-Henrik, de Zeeuw, Dick

وصف الملف: text

Relation: http://eprints.gla.ac.uk/157084/7/157084.pdf; Heerspink, H. J.L. et al. (2018) Rationale and protocol of the Study of Diabetic Nephropathy with Atrasentan (SONAR) trial: A clinical trial design novel to diabetic nephropathy. Diabetes, Obesity and Metabolism , 20(6), pp. 1369-1376. (doi:10.1111/dom.13245 ) (PMID:29405626)

الاتاحة: http://eprints.gla.ac.uk/157084/
http://eprints.gla.ac.uk/157084/7/157084.pdf

المؤلفون: Strauss, Kevin A., Farrar, Michelle A., Muntoni, Francesco, Saito, Kayoko, Mendell, Jerry R., Servais, Laurent, McMillan, Hugh J., Finkel, Richard S., Swoboda, Kathryn J., Kwon, Jennifer M., Zaidman, Craig M., Chiriboga, Claudia A., Iannaccone, Susan T., Krueger, Jena M., Parsons, Julie A., Shieh, Perry B., Kavanagh, Sarah, Wigderson, Melissa, Tauscher-Wisniewski, Sitra, McGill, Bryan E., Macek, Thomas A.

المصدر: Nature Medicine; July 2022, Vol. 28 Issue: 7 p1390-1397, 8p

المؤلفون: Heerspink, Hiddo H.L., Parving, Hans-Henrik, Andress, Dennis L., Bakris, George, Correa-Rotter, Ricardo, Hou, Fan-Fan, Kitzman, Dalane W., Kohan, Donald, Makino, Hirofumi, McMurray, John J.V., Melnick, Joel Z., Miller, Michael G., Pergola, Pablo E., Perkovic, Vlado, Tobe, Sheldon, Yi, Tingting, Wigderson, Melissa, de Zeeuw, Dick

Relation: Heerspink, H. H.L. et al. (2019) Atrasentan and renal events in patients with type 2 diabetes and chronic kidney disease (SONAR): a double-blind, randomised, placebo-controlled trial. Lancet , 393(10184), pp. 1937-1947. (doi:10.1016/S0140-6736(19)30772-X ) (PMID:30995972)

الاتاحة: http://eprints.gla.ac.uk/185687/

المؤلفون: UCL - SSS/IREC/NEFR - Pôle de Néphrologie, UCL - (SLuc) Service de néphrologie, Heerspink, Hiddo J L, Parving, Hans-Henrik, Andress, Dennis L, Bakris, George, Correa-Rotter, Ricardo, Hou, Fan-Fan, Kitzman, Dalane W, Kohan, Donald, Makino, Hirofumi, McMurray, John J V, Melnick, Joel Z, Miller, Michael G, Pergola, Pablo E, Perkovic, Vlado, Tobe, Sheldon, Yi, Tingting, Wigderson, Melissa, de Zeeuw, Dick, SONAR Committees and Investigators, Jadoul, Michel

المصدر: Lancet, Vol. 393, no. 10184, p. 1937-1947 (2019)

مصطلحات الفهرس: General Medicine, info:eu-repo/semantics/article

URL: http://hdl.handle.net/2078.1/221788

المؤلفون: Heerspink, Hiddo J.L., Parving, Hans Henrik, Andress, Dennis L., Bakris, George, Correa-Rotter, Ricardo, Hou, Fan Fan, Kitzman, Dalane W., Kohan, Donald, Makino, Hirofumi, McMurray, John J.V., Melnick, Joel Z., Miller, Michael G., Pergola, Pablo E., Perkovic, Vlado, Tobe, Sheldon, Yi, Tingting, Wigderson, Melissa, de Zeeuw, Dick, Elbert, Alicia, Vallejos, Augusto, Alvarisqueta, Andres, Maffei, Laura, Juncos, Luis, de Arteaga, Javier, Greloni, Gustavo, Farias, Eduardo, Zucchini, Alfredo, Vogel, Daniel, Cusumano, Ana, Santos, Juan, Fraenkel, Margaret, Gallagher, Martin, Davis, Tim, Acharya, Shamasunder, Cooke, Duncan, Suranyi, Michael, Roger, Simon, Toussaint, Nigel, Pollock, Carol, Chan, Doris, Stranks, Stephen, MacIsaac, Richard, Endre, Zoltan, Schmidt, Alice, Prager, Rudolf, Mayer, Gert, Warling, Xavier, Jadoul, Michel, Egstrup, Kenneth, Oczachowska-Kulik, Anna Ewa, Rossing, Peter, Ono, Yasuhirov, Yalcin, Murat, Karim, Shahana

المصدر: Heerspink , H J L , Parving , H H , Andress , D L , Bakris , G , Correa-Rotter , R , Hou , F F , Kitzman , D W , Kohan , D , Makino , H , McMurray , J J V , Melnick , J Z , Miller , M G , Pergola , P E , Perkovic , V , Tobe , S , Yi , T , Wigderson , M , de Zeeuw , D , SONAR Committees and Investigators , Elbert , A , Vallejos , A , Alvarisqueta , A , Maffei , L , Juncos , L , de Arteaga , J , Greloni , G , Farias , E , Zucchini , A , Vogel , D , Cusumano , A , Santos , J , Fraenkel , M , Gallagher , M , Davis , T , Acharya , S , Cooke , D , Suranyi , M , Roger , S , Toussaint , N , Pollock , C , Chan , D , Stranks , S , MacIsaac , R , Endre , Z , Schmidt , A , Prager , R , Mayer , G , Warling , X , Jadoul , M , Egstrup , K , Oczachowska-Kulik , A E , Rossing , P , Ono , Y , Yalcin , M & Karim , S 2019 , ' Atrasentan and renal events in patients with type 2 diabetes and chronic kidney disease (SONAR) : a double-blind, randomised, placebo-controlled trial ' , The Lancet , vol. 393 , no. 10184 , pp. 1937-1947 .

مصطلحات الفهرس: article

URL: https://curis.ku.dk/portal/da/publications/atrasentan-and-renal-events-in-patients-with-type-2-diabetes-and-chronic-kidney-disease-sonar(e9a12770-15c4-4657-b044-93367a607cc1).html
https://doi.org/10.1016/S0140-6736(19)30772-X
http://www.scopus.com/inward/record.url?scp=85065234142&partnerID=8YFLogxK

المؤلفون: Heerspink, Hiddo J. L., Andress, Dennis L., Bakris, George, Brennan, John J., Correa‐Rotter, Ricardo, Hou, Fan Fan, Kitzman, Dalane W., Kohan, Donald, Makino, Hirofumi, McMurray, John, Perkovic, Vlado, Tobe, Sheldon, Wigderson, Melissa, Yi, Tingting, Parving, Hans‐Henrik, de Zeeuw, Dick

المصدر: Diabetes, Obesity & Metabolism; Aug2018, Vol. 20 Issue 8, p1829-1835, 7p

مصطلحات موضوعية: ENDOTHELIN receptors, ALBUMINS, CREATININE, SODIUM in the body, GLOMERULAR filtration rate, DIABETIC nephropathies, INDIVIDUALIZED medicine, RANDOMIZED controlled trials

المؤلفون: Heerspink, Hiddo J. L., de Zeeuw, Dick, Perkovic, Vlado, Tobe, Sheldon, Parving, Hans‐Henrik, Andress, Dennis L., Brennan, John J., Dey, Jyotirmoy, Wigderson, Melissa, Bakris, George, Correa‐Rotter, Ricardo, Hou, Fan Fan, Kitzman, Dalane W., Kohan, Donald, Makino, Hirofumi, McMurray, John

المصدر: Diabetes, Obesity & Metabolism; Jun2018, Vol. 20 Issue 6, p1369-1376, 8p

مصطلحات موضوعية: DIABETIC nephropathies, CLINICAL trials, KIDNEY disease risk factors, ENDOTHELINS, CHRONIC kidney failure, DISEASE progression, INDIVIDUALIZED medicine, TYPE 2 diabetes