-
1Academic Journal
المؤلفون: Kishnani PS, Byrne BJ, Claeys KG, Diaz-Manera J, Dimachkie MM, Kushlaf H, Mozaffar T, Roberts M, Schoser B, Hummel N, Kopiec A, Holdbrook F, Shohet S, Toscano A, Chien Y-H, Loscher W, Laszlo V, Sawada T, Ruck T, Burrow T, Hiwot T, Dearmey S, Wenninger S, Attarian S, Fecarotta S, Sacconi S, Hopkin R, Henderson R, Roxburgh R, Clemens PR, Deegan P, Goker-Alpan O, Musumeci O, Vidal-Fernandez N, Longo N, Freimer M, Tchan M, Tarnopolsky M, Wencel M, Molnar MJ, Gutschmidt K, Kornblum C, Berthy J, Janszky J, Alonso-Perez J, Cauci J, Shin J-H, Avelar J, Vengoechea J, Tarnev I, Kobayashi H, Shiraishi H, Amartino H, Andersen H, Pedro H, Lau H, Akihiro H, Bartosik-Psujek H, Parenti G, Papadimas GK, Kim G, Bouhour F, Butler E, Salort-Campana E, Stefanescu E, Hughes D, Reyes-Leiva D, Bodkin C, Eldridge C, Quinn C, Lindberg C, Tard C, Koritnik B, Khan A, Dominovic-Kovacevic A, Pestronk A, Sebok A
المصدر: Journal of Patient-Reported Outcomes, December 2024
وصف الملف: application/pdf
Relation: https://eprints.ncl.ac.uk/302625; https://eprints.ncl.ac.uk/fulltext.aspx?url=302625/CDBCAC4C-D28B-4C92-AFF8-F4C4E945249B.pdf&pub_id=302625
الاتاحة: https://eprints.ncl.ac.uk/302625
-
2Academic Journal
المؤلفون: Renette, S, Lewis, M P, Wencel, M M, Farahani, A, Tomé, A
المصدر: Radiocarbon ; volume 65, issue 1, page 209-231 ; ISSN 0033-8222 1945-5755
-
3Academic Journal
-
4Academic Journal
المؤلفون: Schoser B., Roberts M., Byrne B. J., Sitaraman S., Jiang H., Laforet P., Toscano A., Castelli J., Diaz-Manera J., Goldman M., van der Ploeg A. T., Bratkovic D., Kuchipudi S., Mozaffar T., Kishnani P. S., Sebok A., Pestronk A., Dominovic-Kovacevic A., Khan A., Koritnik B., Tard C., Lindberg C., Quinn C., Eldridge C., Bodkin C., Reyes-Leiva D., Hughes D., Stefanescu E., SALORT-CAMPANA E., Butler E., Bouhour F., Kim G., Konstantinos Papadimas G., Parenti G., Bartosik-Psujek H., Kushlaf H., Akihiro H., Lau H., Pedro H., Andersen H., Amartino H., Shiraishi H., Kobayashi H., Tarnev I., Vengoechea J., Avelar J., Shin J. -H., Cauci J., Alonso-Perez J., Janszky J., Berthy J., Cornelia K., Gutschmidt K., Claeys K., Judit Molnar M., Wencel M., Tarnopolsky M., Dimachkie M., Tchan M., Freimer M., Longo N., Vidal-Fernandez N., Musumeci O., Goker-Alpan O., Deegan P., Clemens P. R., Roxburgh R., Henderson R., Hopkin R., Sacconi S., Fecarotta S., Attarian S., Wenninger S., Dearmey S., Hiwot T., Burrow T., Ruck T., Sawada T., Laszlo V., Loscher W., Chien Y. -H.
المساهمون: Schoser, B., Roberts, M., Byrne, B. J., Sitaraman, S., Jiang, H., Laforet, P., Toscano, A., Castelli, J., Diaz-Manera, J., Goldman, M., van der Ploeg, A. T., Bratkovic, D., Kuchipudi, S., Mozaffar, T., Kishnani, P. S., Sebok, A., Pestronk, A., Dominovic-Kovacevic, A., Khan, A., Koritnik, B., Tard, C., Lindberg, C., Quinn, C., Eldridge, C., Bodkin, C., Reyes-Leiva, D., Hughes, D., Stefanescu, E., SALORT-CAMPANA, E., Butler, E., Bouhour, F., Kim, G., Konstantinos Papadimas, G., Parenti, G., Bartosik-Psujek, H., Kushlaf, H., Akihiro, H., Lau, H., Pedro, H., Andersen, H., Amartino, H., Shiraishi, H., Kobayashi, H., Tarnev, I., Vengoechea, J., Avelar, J., Shin, J. -H., Cauci, J., Alonso-Perez, J., Janszky, J., Berthy, J., Cornelia, K., Gutschmidt, K., Claeys, K., Judit Molnar, M., Wencel, M., Tarnopolsky, M., Dimachkie, M., Tchan, M., Freimer, M., Longo, N., Vidal-Fernandez, N., Musumeci, O., Goker-Alpan, O., Deegan, P., Clemens, P. R., Roxburgh, R., Henderson, R., Hopkin, R., Sacconi, S., Fecarotta, S., Attarian, S., Wenninger, S., Dearmey, S., Hiwot, T., Burrow, T., Ruck, T., Sawada, T., Laszlo, V., Loscher, W., Chien, Y. -H.
Relation: info:eu-repo/semantics/altIdentifier/wos/WOS:000755602800027; volume:20; issue:12; firstpage:1027; lastpage:1037; numberofpages:11; journal:LANCET NEUROLOGY; http://hdl.handle.net/11588/870280; info:eu-repo/semantics/altIdentifier/scopus/2-s2.0-85119194577
الاتاحة: http://hdl.handle.net/11588/870280
https://doi.org/10.1016/S1474-4422(21)00331-8 -
5Academic Journal
المؤلفون: Diaz-Manera J, Kishnani PS, Kushlaf H, Ladha S, Mozaffar T, Straub V, Toscano A, van der Ploeg AT, Berger KI, Clemens PR, Chien Y-H, Day JW, Illarioshkin S, Roberts M, Attarian S, Borges JL, Bouhour F, Choi YC, Erdem-Ozdamar S, Goker-Alpan O, Kostera-Pruszczyk A, Haack KA, Hug C, Huynh-Ba O, Johnson J, Thibault N, Zhou T, Dimachkie MM, Schoser B, Behin A, Boentert M, Carvalho G, Chahin N, Charrow J, Deegan P, Durmus Tekce H, Duval F, Genge A, Gutmann L, Henderson RD, Hennermann JB, Hiwot T, Hughes D, Karaa A, Karam C, Kautzky-Willer A, Komaki H, Laforet P, Longo N, Malinova V, Mare R, Maxit C, Mengel E, Moggio MG, Molnar MJ, Mongini TE, Nadaj-Pakleza A, Nascimento Osorio A, Noury J-B, Oliveira ASB, Parman Y, Pena L, Remiche G, Sciacco M, Shieh PB, Smith C, Stulnig T, Taithe F, Tard C, Tarnopolsky M, Vorgerd M, Whitley C, Young P, Alonso-Perez J, Altemus P, Aube-Nathier A-C, Avelar JB, Bailey C, Bekircan-Kurt CE, Billy J, Boschi S, Brown KE, Carrera Garcia L, Chase L, Cirne H, Danjoux L, Davion J-B, DeArmey S, Fedotova E, Gandolfo E, Grosz Z, Guellec D, Guettsches A-K, Guglieri M, Hatcher E, Helms S, Hufgard-Leitner M, Klyushnikov SA, Langton J, Linkova L, Mavroudakis N, Mazurova S, Mori M, Muller-Miny L, Musumeci O, Nance CS, Natera-de Benito D, Neel R, Niizawa GA, Noll L, Ortega E, Pasnoor M, Pautot V, Potulska-Chromik A, Pugliese A, Questienne C, Ramos Lopes M, Reyes-Leiva D, Riedl M, Rugiero MF, Salort-Campana E, Sgobbi Souza PV, Sole G, Solera L, Souto Lopes S, Specht S, Statland J, Swenson A, Tan CY, Tizon S, van der Beek NAME, van Kooten HA, Wencel M, Wenninger S, Zagnoli F
المصدر: The Lancet Neurology, December 2021
Relation: https://eprints.ncl.ac.uk/278594
الاتاحة: https://eprints.ncl.ac.uk/278594
-
6Academic Journal
المؤلفون: Diaz-Manera J., Kishnani P. S., Kushlaf H., Ladha S., Mozaffar T., Straub V., Toscano A., van der Ploeg A. T., Berger K. I., Clemens P. R., Chien Y. -H., Day J. W., Illarioshkin S., Roberts M., Attarian S., Borges J. L., Bouhour F., Choi Y. C., Erdem-Ozdamar S., Goker-Alpan O., Kostera-Pruszczyk A., Haack K. A., Hug C., Huynh-Ba O., Johnson J., Thibault N., Zhou T., Dimachkie M. M., Schoser B., Behin A., Boentert M., Carvalho G., Chahin N., Charrow J., Deegan P., Durmus Tekce H., Duval F., Genge A., Gutmann L., Henderson R. D., Hennermann J. B., Hiwot T., Hughes D., Karaa A., Karam C., Kautzky-Willer A., Komaki H., Laforet P., Longo N., Malinova V., Mare R., Maxit C., Mengel E., Moggio M. G., Molnar M. J., Mongini T. E., Nadaj-Pakleza A., Nascimento Osorio A., Noury J. -B., Oliveira A. S. B., Parman Y., Pena L., Remiche G., Sciacco M., Shieh P. B., Smith C., Stulnig T., Taithe F., Tard C., Tarnopolsky M., Vorgerd M., Whitley C., Young P., Alonso-Perez J., Altemus P., Aube-Nathier A. -C., Avelar J. B., Bailey C., Bekircan-Kurt C. E., Billy J., Boschi S., Brown K. E., Carrera Garcia L., Chase L., Cirne H., Danjoux L., Davion J. -B., DeArmey S., Fedotova E., Gandolfo E., Grosz Z., Guellec D., Guettsches A. -K., Guglieri M., Hatcher E., Helms S., Hufgard-Leitner M., Klyushnikov S. A., Langton J., Linkova L., Mavroudakis N., Mazurova S., Mori M., Muller-Miny L., Musumeci O., Nance C. S., Natera-de Benito D., Neel R., Niizawa G. A., Noll L., Ortega E., Pasnoor M., Pautot V., Potulska-Chromik A., Pugliese A., Questienne C., Ramos Lopes M., Reyes-Leiva D., Riedl M., Rugiero M. F., Salort-Campana E., Sgobbi Souza P. V., Sole G., Solera L., Souto Lopes S., Specht S., Statland J., Swenson A., Tan C. Y., Tizon S., van der Beek N. A. M. E., van Kooten H. A., Wencel M., Wenninger S., Zagnoli F.
المساهمون: Diaz-Manera J., Kishnani P.S., Kushlaf H., Ladha S., Mozaffar T., Straub V., Toscano A., van der Ploeg A.T., Berger K.I., Clemens P.R., Chien Y.-H., Day J.W., Illarioshkin S., Roberts M., Attarian S., Borges J.L., Bouhour F., Choi Y.C., Erdem-Ozdamar S., Goker-Alpan O., Kostera-Pruszczyk A., Haack K.A., Hug C., Huynh-Ba O., Johnson J., Thibault N., Zhou T., Dimachkie M.M., Schoser B., Behin A., Boentert M., Carvalho G., Chahin N., Charrow J., Deegan P., Durmus Tekce H., Duval F., Genge A., Gutmann L., Henderson R.D., Hennermann J.B., Hiwot T., Hughes D., Karaa A., Karam C., Kautzky-Willer A., Komaki H., Laforet P., Longo N., Malinova V., Mare R., Maxit C., Mengel E., Moggio M.G., Molnar M.J., Mongini T.E., Nadaj-Pakleza A., Nascimento Osorio A., Noury J.-B., Oliveira A.S.B., Parman Y., Pena L., Remiche G., Sciacco M., Shieh P.B., Smith C., Stulnig T., Taithe F., Tard C., Tarnopolsky M., Vorgerd M., Whitley C., Young P., Alonso-Perez J., Altemus P., Aube-Nathier A.-C., Avelar J.B., Bailey C., Bekircan-Kurt C.E., Billy J., Boschi S., Brown K.E., Carrera Garcia L., Chase L., Cirne H., Danjoux L., Davion J.-B., DeArmey S., Fedotova E., Gandolfo E., Grosz Z., Guellec D., Guettsches A.-K., Guglieri M., Hatcher E., Helms S., Hufgard-Leitner M., Klyushnikov S.A., Langton J., Linkova L.
مصطلحات موضوعية: Child, Preschool, Double-Blind Method, Enzyme Replacement Therapy, Human, Treatment Outcome, Walking, Glycogen Storage Disease Type II, alpha-Glucosidases
Relation: info:eu-repo/semantics/altIdentifier/pmid/34800399; info:eu-repo/semantics/altIdentifier/wos/WOS:000755602800026; volume:20; issue:12; firstpage:1012; lastpage:1026; numberofpages:15; journal:LANCET NEUROLOGY; http://hdl.handle.net/2318/1858772; info:eu-repo/semantics/altIdentifier/scopus/2-s2.0-85119210138
الاتاحة: http://hdl.handle.net/2318/1858772
https://doi.org/10.1016/S1474-4422(21)00241-6 -
7Academic JournalMacitentan for the treatment of idiopathic pulmonary fibrosis: The randomised controlled MUSIC trial
المؤلفون: Raghu G., Million-Rousseau R., Morganti A., Perchenet L., Behr J., Goh N., Glanville A., Musk M., Hopkins P., Lien D. C., Chan C., Rolf J. D., Wilcox P., Cox P. G., Manganas H., Cottin V., Valeyre D., Walleart B., Andreas S., Neurohr C., Guenther A., Schonfeld N., Koch A., Kramer M., Breuer R., Ben-Dov I., Fink G., Schwarz Y., Albera C., Confalonieri M., Saltini C., Harari S., Flezar M., Greenblatt M., Ras G. J., Morell F., Alvarez-Sala J. L., Xaubet A., Sueiro A., Linares M. J., Skold M., Kayacan O., Mogulkoc N., Chan A., Chapman J., Parambil J., Ettinger N., Golden J., Meyer K. C., Swigris J. J., Yung G. L., Antin-Ozerkis D., Mohabir P. K., Wesselius L. J., De Andrade J., Cordova F., Safdar Z., Wencel M.
المساهمون: G. Raghu, R. Million-Rousseau, A. Morganti, L. Perchenet, J. Behr, N. Goh, A. Glanville, M. Musk, P. Hopkin, D.C. Lien, C. Chan, J.D. Rolf, P. Wilcox, P.G. Cox, H. Mangana, V. Cottin, D. Valeyre, B. Walleart, S. Andrea, C. Neurohr, A. Guenther, N. Schonfeld, A. Koch, M. Kramer, R. Breuer, I. Ben-Dov, G. Fink, Y. Schwarz, C. Albera, M. Confalonieri, C. Saltini, S. Harari, M. Flezar, M. Greenblatt, G.J. Ra, F. Morell, J.L. Alvarez-Sala, A. Xaubet, A. Sueiro, M.J. Linare, M. Skold, O. Kayacan, N. Mogulkoc, A. Chan, J. Chapman, J. Parambil, N. Ettinger, J. Golden, K.C. Meyer, J.J. Swigri, G.L. Yung, D. Antin-Ozerki, P.K. Mohabir, L.J. Wesseliu, J. De Andrade, F. Cordova, Z. Safdar, M. Wencel
مصطلحات موضوعية: Settore MED/10 - Malattie dell'Apparato Respiratorio
Relation: info:eu-repo/semantics/altIdentifier/wos/WOS:000327919900026; volume:42; issue:6; firstpage:1622; lastpage:1632; numberofpages:11; journal:EUROPEAN RESPIRATORY JOURNAL; http://hdl.handle.net/2434/749092; info:eu-repo/semantics/altIdentifier/scopus/2-s2.0-84888166435
-
8Academic Journal
المؤلفون: Kimonis, VE, Nalbandian, A, Llewellyn, K, Khare, M, Dec, E, Wencel, M, Yin, H, Caiozzo, V, Martin, B, Smith, C, Rafi, S, Wang, A, Mozaffar, T, Weiss, J
المساهمون: Washington, HS, Castillo Jimenez, CE
وصف الملف: application/pdf
Relation: qt1tp6w3n1; https://escholarship.org/uc/item/1tp6w3n1
-
9Periodical
المؤلفون: Renette, S, Lewis, M P, Wencel, M M, Farahani, A, Tomé, A
المصدر: Radiocarbon; February 2023, Vol. 65 Issue: 1 p209-231, 23p
-
10Academic Journal
المؤلفون: Herrera, M.1 (AUTHOR), Wencel, M.1 (AUTHOR), Hernandez, I.1 (AUTHOR), Goyal, N.1 (AUTHOR), Dimachkie, M.2 (AUTHOR), Lloyd, T.3 (AUTHOR), Mohassel, P.3 (AUTHOR), Weihl, C.4 (AUTHOR), Freimer, M.5 (AUTHOR), Shaibani, A.6 (AUTHOR), Wicklund, M.7 (AUTHOR), Dixon, S.8 (AUTHOR), Chahin, N.9 (AUTHOR), Wang, L.10 (AUTHOR), Shieh, P.11 (AUTHOR), Amato, A.12 (AUTHOR), Quinn, C.13 (AUTHOR), Carbunar, O.14 (AUTHOR), Mozaffar, T.1 (AUTHOR)
المصدر: Neuromuscular Disorders. 2024 Supplement 1, Vol. 43, pN.PAG-N.PAG. 1p.
مصطلحات موضوعية: *CYTOTOXIC T cells, *INCLUSION body myositis, *KILLER cell receptors, *T cells, *T cell differentiation
-
11Academic Journal
المؤلفون: Herrera, M.1 (AUTHOR), Wencel, M.1 (AUTHOR), Hernandez, I.1 (AUTHOR), Goyal, N.1 (AUTHOR), Dimachkie, M.2 (AUTHOR), Lloyd, T.3 (AUTHOR), Mohassel, P.3 (AUTHOR), Weihl, C.4 (AUTHOR), Freimer, M.5 (AUTHOR), Shaibani, A.6 (AUTHOR), Wicklund, M.7 (AUTHOR), Dixon, S.8 (AUTHOR), Chahin, N.9 (AUTHOR), Wang, L.10 (AUTHOR), Shieh, P.11 (AUTHOR), Amato, A.12 (AUTHOR), Quinn, C.13 (AUTHOR), Carbunar, O.14 (AUTHOR), Mozaffar, T.1 (AUTHOR)
المصدر: Neuromuscular Disorders. 2024 Supplement 1, Vol. 43, pN.PAG-N.PAG. 1p.
مصطلحات موضوعية: *DISEASE duration, *SKELETAL muscle, *DISEASE progression, *FUNCTIONAL assessment, *SEROCONVERSION
-
12Academic Journal
المؤلفون: Wencel, M.1 (AUTHOR), Goyal, N.1 (AUTHOR), Carbunar, O.2 (AUTHOR), Freimer, M.3 (AUTHOR), Dimachkie, M.4 (AUTHOR), Quinn, C.5 (AUTHOR), Lloyd, T.6 (AUTHOR), Mohassel, P.6 (AUTHOR), Weihl, C.7 (AUTHOR), Shaibani, A.8 (AUTHOR), Wang, L.9 (AUTHOR), Nizar, C.10 (AUTHOR), Amato, A.11 (AUTHOR), Wicklund, M.12 (AUTHOR), Dixon, S.12 (AUTHOR), Shieh, P.13 (AUTHOR), Herbelin, L.14 (AUTHOR), Mozaffar, T.1 (AUTHOR)
المصدر: Neuromuscular Disorders. 2024 Supplement 1, Vol. 43, pN.PAG-N.PAG. 1p.
مصطلحات موضوعية: *INCLUSION body myositis, *NATURAL history, *GRIP strength, *PULMONARY function tests, *IMMUNOPHENOTYPING
-
13Academic Journal
المؤلفون: Wencel, M.1 (AUTHOR), Bjazevic, K.1 (AUTHOR), Goyal, N.1 (AUTHOR), Carbunar, O.2 (AUTHOR), Freimer, M.3 (AUTHOR), Dimachkie, M.4 (AUTHOR), Quinn, C.5 (AUTHOR), LLoyd, T.6 (AUTHOR), Mohassel, P.6 (AUTHOR), Weihl, C.7 (AUTHOR), Shaibani, A.8 (AUTHOR), Wang, L.9 (AUTHOR), Chahin, N.10 (AUTHOR), Amato, A.11 (AUTHOR), Wicklund, M.12 (AUTHOR), Shieh, P.13 (AUTHOR), Herbelin, L.14 (AUTHOR), Barohn, R.14 (AUTHOR), Mozaffar, T.1 (AUTHOR)
المصدر: Neuromuscular Disorders. 2024 Supplement 1, Vol. 43, pN.PAG-N.PAG. 1p.
مصطلحات موضوعية: *INCLUSION body myositis, *PULMONARY function tests, *VITAL capacity (Respiration), *MUSCLE diseases, *RESPIRATORY insufficiency
-
14Academic Journal
المؤلفون: Gaid, P.1 (AUTHOR), Wencel, M.1 (AUTHOR), Hernandez, I.1 (AUTHOR), Goyal, N.1 (AUTHOR), Dimachkie, M.2 (AUTHOR), Lloyd, T.3 (AUTHOR), Mohassel, P.3 (AUTHOR), Weihl, C.4 (AUTHOR), Freimer, M.5 (AUTHOR), Shaibani, A.6 (AUTHOR), Wicklund, M.7 (AUTHOR), Dixon, S.8 (AUTHOR), Chahin, N.9 (AUTHOR), Wang, L.10 (AUTHOR), Shieh, P.11 (AUTHOR), Amato, A.12 (AUTHOR), Quinn, C.13 (AUTHOR), Carbunar, O.14 (AUTHOR), Mozaffar, T.1 (AUTHOR)
المصدر: Neuromuscular Disorders. 2024 Supplement 1, Vol. 43, pN.PAG-N.PAG. 1p.
مصطلحات موضوعية: *INCLUSION body myositis, *PULMONARY function tests, *MUSCLE weakness, *PATIENTS' attitudes, *MUSCULAR atrophy
-
15Academic Journal
المؤلفون: Mathew, V., Wencel, M., Habib, A.A., Goyal, N.A., Needham, M., Mozaffar, T.
Relation: ispartof: Journal of Clinical Neuromuscular Disease spage 246 epage 247 issue 4 vol 21; https://doi.org/10.1097/CND.0000000000000293; 991005546336107891; https://researchportal.murdoch.edu.au/esploro/outputs/journalArticle/Attitudes-toward-non-interventional-observational-studies-in/991005546336107891; alma:61MUN_INST/bibs/991005546336107891
-
16Academic Journal
المؤلفون: Goyal, N., Greenberg, S., Cauchi, J., Araujo, N., Li, V., Wencel, M., Irani, T., Wang, L., Coulis, G., Villalta, A., Mozaffar, T.
المصدر: Neuromuscular Disorders ; volume 30, page S136 ; ISSN 0960-8966
-
17Academic Journal
المؤلفون: Araujo, N., Wencel, M., Medina, E., Zhang, L., Nguyen, D., Habib, A., Mozaffar, T., Goyal, N.
المصدر: Neuromuscular Disorders ; volume 29, page S67-S68 ; ISSN 0960-8966
-
18Academic Journal
المؤلفون: Araujo, N., Wencel, M., Medina, E., Zhang, L., Nguyen, D., Habib, A., Mozaffar, T., Goyal, N.
المصدر: Neuromuscular Disorders ; volume 29, page S42-S43 ; ISSN 0960-8966
-
19Academic Journal
المؤلفون: Goyal, N., Wencel, M., Araujo, N., Medina, E., Zhang, L., Nguyen, D., Mozaffar, T.
المصدر: Neuromuscular Disorders ; volume 28, page S76-S77 ; ISSN 0960-8966
-
20Academic Journal
المؤلفون: Goyal, N., Wencel, M., Araujo, N., Medina, E., Nguyen, D., Zhang, L., Mozaffar, T.
المصدر: Neuromuscular Disorders ; volume 28, page S135 ; ISSN 0960-8966