المؤلفون: Heather L. Gray-Edwards, Xuntian Jiang, Ashley N. Randle, Amanda R. Taylor, Taylor L. Voss, Aime K. Johnson, Victoria J. McCurdy, Miguel Sena-Esteves, Daniel S. Ory, Douglas R. Martin

المصدر: Molecular Therapy: Methods & Clinical Development, Vol 6, Iss C, Pp 135-142 (2017)

مصطلحات موضوعية: adeno-associated virus, AAV, biomarkers, feline, gene therapy, GM1 gangliosidosis, lipidomics, neurologic disease, Genetics, QH426-470, Cytology, QH573-671

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050117300888; https://doaj.org/toc/2329-0501

URL الوصول: https://doaj.org/article/3e3a1ecbcf1a457a8a1a35bcff0c25d7

المؤلفون: Hannah E. Rockwell, Victoria J. McCurdy, Samuel C. Eaton, Diane U. Wilson, Aime K. Johnson, Ashley N. Randle, Allison M. Bradbury, Heather L. Gray-Edwards, Henry J. Baker, Judith A. Hudson, Nancy R. Cox, Miguel Sena-Esteves, Thomas N. Seyfried, Douglas R. Martin

المصدر: ASN Neuro, Vol 7 (2015)

مصطلحات موضوعية: Neurosciences. Biological psychiatry. Neuropsychiatry, RC321-571

وصف الملف: electronic resource

Relation: https://doaj.org/toc/1759-0914

URL الوصول: https://doaj.org/article/ca9dfbf3374b4466a2748535a40d9de2

المؤلفون: Victoria J. McCurdy, Aime K. Johnson, Miguel Sena-Esteves, Nancy E. Morrison, Douglas R. Martin, Ashley N. Randle, Allison M. Bradbury, Heather L. Gray-Edwards, Misako Hwang, Henry J. Baker, Nancy R. Cox

المصدر: Gene therapy

مصطلحات موضوعية: 0301 basic medicine, medicine.medical_specialty, Genetic enhancement, Central nervous system, Genetic Vectors, Disease, Biology, Sandhoff disease, Gastroenterology, Virus, Article, 03 medical and health sciences, 0302 clinical medicine, Internal medicine, Genetics, medicine, Lysosomal storage disease, Animals, Humans, Molecular Biology, Ganglioside, CATS, Sandhoff Disease, Genetic Therapy, Dependovirus, medicine.disease, beta-N-Acetylhexosaminidases, Disease Models, Animal, 030104 developmental biology, medicine.anatomical_structure, 030220 oncology & carcinogenesis, Cats, Molecular Medicine

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::3ffc0513e7ab2f1a80457dc8f0368107
https://pubmed.ncbi.nlm.nih.gov/32884151

المؤلفون: Aime K. Johnson, Tiffany A. Peterson, Ashley N. Randle, Victoria J. McCurdy, Allison M. Bradbury, Brandon L. Brunson, Edward E. Morrison, Karen G. Wolfe, Heather L. Gray-Edwards, Henry J. Baker, Miguel Sena-Esteves, Stephen Z. Wells, Nancy R. Cox, John C. Dennis, Douglas R. Martin, Amanda L. Gross

المصدر: Neuroscience. 340:117-125

مصطلحات موضوعية: 0301 basic medicine, Chemokine, Genes, MHC Class II, Genetic Vectors, Population, Central nervous system, Sandhoff disease, Gene delivery, Polymerase Chain Reaction, Article, 03 medical and health sciences, 0302 clinical medicine, medicine, Animals, Gliosis, education, Neuroinflammation, Adaptor Proteins, Signal Transducing, Neurons, education.field_of_study, biology, Microglia, General Neuroscience, Neurodegeneration, Brain, Sandhoff Disease, Genetic Therapy, Dependovirus, medicine.disease, Immunohistochemistry, Disease Models, Animal, 030104 developmental biology, medicine.anatomical_structure, Astrocytes, Immunology, Cats, biology.protein, 030217 neurology & neurosurgery, Transcription Factors

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::a1ff8b63f6755be48fe91262068ff31b
https://doi.org/10.1016/j.neuroscience.2016.10.047

المؤلفون: Ashley N. Randle, Heather L. Gray-Edwards, Ronald J. Beyers, Henry J. Baker, Judith A. Hudson, Adrien-Maxence Hespel, Merrilee Holland, Miguel Sena-Esteves, Victoria J. McCurdy, Douglas R. Martin, Thomas S. Denney, Meredith L. Voyles, Nancy R. Cox, Diane U. Wilson, Brandon L. Brunson, Allison M. Bradbury, Nouha Salibi, Ronald D. Montgomery, Aime K. Johnson, Patricia M. Beadlescomb

المصدر: Molecular Genetics and Metabolism. 116:80-87

مصطلحات موضوعية: medicine.medical_specialty, Pathology, Endocrinology, Diabetes and Metabolism, Genetic enhancement, Mucopolysaccharidosis, Genetic Vectors, Central nervous system, Sandhoff disease, Biochemistry, Adenoviridae, Endocrinology, Spinal cord compression, Genetics, medicine, Lysosomal storage disease, Animals, Humans, Molecular Biology, Kidney, business.industry, Animal Structures, Sandhoff Disease, Genetic Therapy, Mucopolysaccharidoses, medicine.disease, beta-N-Acetylhexosaminidases, Disease Models, Animal, Phenotype, medicine.anatomical_structure, Cats, Histopathology, business

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::5c2346f38fe74a8a3aedefb430f1bdff
https://doi.org/10.1016/j.ymgme.2015.05.003

المؤلفون: Victoria J. McCurdy, Gretchen Golas, Yvonne L. Latour, Douglas R. Martin, Allison M. Bradbury, Cynthia J. Tifft, Ashley N. Randle, Brandon L. Brunson, Donald C. Sorjonen, Amanda R. Taylor, Miguel Sena-Esteves, Henry J. Baker, Nouha Salibi, Annie S. Maguire, Sarah E. Thomas, Heather L. Gray-Edwards, Jamie L. Shirley, Ronald J. Beyers, Pete W. Christopherson, Aime K. Johnson, Jean M. Johnston, Nancy R. Cox, Debra S Regier, Thomas S. Denney

المصدر: Molecular therapy : the journal of the American Society of Gene Therapy. 25(4)

مصطلحات موضوعية: 0301 basic medicine, Magnetic Resonance Spectroscopy, Genetic enhancement, Genetic Vectors, Disease, Gangliosidosis, Microgliosis, Bioinformatics, 03 medical and health sciences, 0302 clinical medicine, Cerebrospinal fluid, Drug Discovery, Genetics, medicine, Animals, Humans, Molecular Biology, Pharmacology, CATS, Gangliosidosis, GM1, Hypocalcemia, business.industry, Neurodegeneration, Electroencephalography, Genetic Therapy, Dependovirus, medicine.disease, Magnetic Resonance Imaging, Clinical trial, Disease Models, Animal, 030104 developmental biology, Treatment Outcome, Immunology, Cats, Molecular Medicine, Original Article, business, 030217 neurology & neurosurgery, Biomarkers

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::a6f557ff00d43afc494923b7679a934f
https://pubmed.ncbi.nlm.nih.gov/28236574

المؤلفون: Aime K. Johnson, Hannah E. Rockwell, Ashley N. Randle, Miguel Sena-Esteves, Judith A. Hudson, Douglas R. Martin, Heather L. Gray-Edwards, Victoria J. McCurdy, Allison M. Bradbury, Samuel Eaton, Henry J. Baker, Nancy R. Cox, Diane U. Wilson, Thomas N. Seyfried

المصدر: ASN NEURO
ASN Neuro, Vol 7 (2015)

مصطلحات موضوعية: Central Nervous System, medicine.medical_specialty, Genetic enhancement, Central nervous system, Genetic Vectors, G(M2) Ganglioside, adeno-associated virus, Biology, Gene delivery, Sandhoff disease, medicine.disease_cause, Severity of Illness Index, lcsh:RC321-571, Cerebrosides, Internal medicine, Gangliosides, medicine, Animals, lcsh:Neurosciences. Biological psychiatry. Neuropsychiatry, Adeno-associated virus, Homeodomain Proteins, Ganglioside, β-hexosaminidase, Sulfoglycosphingolipids, ganglioside, General Neuroscience, Brain, Sandhoff Disease, Genetic Therapy, Dependovirus, medicine.disease, Spinal cord, gene therapy, Ganglioside GM2, 3. Good health, Disease Models, Animal, medicine.anatomical_structure, Endocrinology, Treatment Outcome, Spinal Cord, Immunology, Cats, Disease Progression, Quality of Life, Original Article, Neurology (clinical), Lysosomes

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::00cada2388a7fa1d37bd90a5ed34804e
http://europepmc.org/articles/PMC4720176

المؤلفون: Nancy E. Morrison, Thomas N. Seyfried, Misako Hwang, Julian R. Arthur, Hannah E. Rockwell, Brandon L. Brunson, Nancy R. Cox, Victoria J. McCurdy, Allison M. Bradbury, Henry J. Baker, Ashley N. Randle, Douglas R. Martin, Aime K. Johnson, Jacob A. Johnson, Miguel Sena-Esteves, Heather L. Gray-Edwards

المصدر: Gene therapy. 22(2)

مصطلحات موضوعية: Pathology, medicine.medical_specialty, Genetic enhancement, Central nervous system, Genetic Vectors, Disease, Biology, Sandhoff disease, Central nervous system disease, Cerebrospinal fluid, Immune system, Transduction, Genetic, Gangliosides, Genetics, medicine, Animals, Humans, Molecular Biology, Injections, Intraventricular, Ganglioside, Sandhoff Disease, Genetic Therapy, Dependovirus, medicine.disease, beta-N-Acetylhexosaminidases, Immunity, Humoral, medicine.anatomical_structure, Treatment Outcome, Immunology, Cats, Disease Progression, Molecular Medicine

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::3732a58287626553f8190e4dd8964aae
https://pubmed.ncbi.nlm.nih.gov/25474439

المؤلفون: Allison E. Church Bird, Ashley N. Randle, Miguel Sena-Esteves, Brandon L. Brunson, Alexandria Colaco, Frances M. Platt, Douglas R. Martin, Allison M. Bradbury, Judith A. Hudson, Mylvaganam Jeyakumar, Donald C. Sorjonen, Jamie L. Shirley, Henry J. Baker, Nicholas L. De Pompa, Nancy R. Cox, Diane U. Wilson, Pete W. Christopherson, Aime K. Johnson, Heather L. Gray-Edwards, Victoria J. McCurdy

المصدر: Experimental neurology. 263

مصطلحات موضوعية: Pathology, medicine.medical_specialty, Genetic enhancement, Genetic Vectors, Sandhoff disease, Gangliosidosis, Peripheral blood mononuclear cell, Article, Gangliosidoses, Cerebrospinal fluid, Developmental Neuroscience, Medicine, Animals, GM2 gangliosidoses, business.industry, Brain, Sandhoff Disease, Genetic Therapy, Dependovirus, medicine.disease, Magnetic Resonance Imaging, beta-N-Acetylhexosaminidases, Disease Models, Animal, Neurology, Immunology, Cats, Disease Progression, Leukocytes, Mononuclear, Biomarker (medicine), business, Lysosomes, Biomarkers

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::5dd65101287da3a03642c023647aa05f
https://pubmed.ncbi.nlm.nih.gov/25284324

المؤلفون: Miguel Sena-Esteves, Ronald J. Beyers, Stanley G. LeRoy, Nouha Salibi, Brandon L. Brunson, Ashley N. Randle, Nancy E. Morrison, Thomas S. Denney, Jacob A. Johnson, Victoria J. McCurdy, Misako Hwang, Heather L. Gray-Edwards, Stacy Maitland, Henry J. Baker, Aime K. Johnson, Douglas R. Martin, Nancy R. Cox

المصدر: Science Translational Medicine. 6

مصطلحات موضوعية: Male, Pathology, medicine.medical_specialty, Genetic enhancement, Disease, Breeding, Biology, Gangliosidosis, Deep cerebellar nuclei, Article, Viral vector, Lysosomal storage disease, medicine, Animals, Humans, Survival analysis, Brain, Genetic Therapy, General Medicine, Dependovirus, beta-Galactosidase, medicine.disease, Spinal cord, Magnetic Resonance Imaging, Survival Analysis, Disease Models, Animal, medicine.anatomical_structure, Organ Specificity, Cats, Disease Progression, Female, Nervous System Diseases, Lysosomes

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::d0f3807a9e044b072af195056e201845
https://doi.org/10.1126/scitranslmed.3007733

المؤلفون: Nancy R. Cox, Diane U. Wilson, Eleanor M. Josephson, Thomas S. Denney, Ronald J. Beyers, Ashley N. Randle, Heather L. Gray-Edwards, Judith A. Hudson, Victoria J. McCurdy, Douglas R. Martin, Allison M. Bradbury, Nouha Salibi

مصطلحات موضوعية: Inferior colliculus, Male, Pathology, medicine.medical_specialty, Neuroscience(all), Lateral geniculate nucleus, Reticular formation, Article, Temporal lobe, Imaging, Three-Dimensional, Vestibular nuclei, Medicine, Animals, Animal model, medicine.diagnostic_test, business.industry, General Neuroscience, Cranial nerves, Translational, Brain, Magnetic resonance imaging, Cat, Anatomy, Magnetic Resonance Imaging, medicine.anatomical_structure, Central nervous system, Cats, business, Optic radiation, MRI

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::ad4222a245193c261a64538e29bf68aa
https://europepmc.org/articles/PMC4060963/

المؤلفون: Ashley N. Randle, Aime K. Johnson, Miguel Sena-Esteves, Heather L. Gray-Edwards, Misako Hwang, Judith A. Hudson, Douglas R. Martin, Victoria J. McCurdy

المصدر: Molecular Genetics and Metabolism. 117:S52

مصطلحات موضوعية: Oncology, medicine.medical_specialty, business.industry, Endocrinology, Diabetes and Metabolism, Genetic enhancement, Sandhoff disease, medicine.disease, Biochemistry, Endocrinology, Internal medicine, Long term survival, Genetics, Medicine, business, Molecular Biology

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::2f10172340990e8d1d86e7d1704cf32f
https://doi.org/10.1016/j.ymgme.2015.12.275