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1Academic Journal
المؤلفون: Parker, MM, Damrauer, SM, Tcheandjieu, C, Erbe, D, Aldinc, E, Hawkins, PN, Gillmore, JD, Hull, LE, Lynch, JA, Joseph, J, Ticau, S, Flynn-Carroll, AO, Deaton, AM, Ward, LD, Assimes, TL, Tsao, PS, Chang, K-M, Rader, DJ, Fitzgerald, K, Vaishnaw, AK, Hinkle, G, Nioi, P
المصدر: Scientific Reports , 11 (1) , Article 11645. (2021)
مصطلحات موضوعية: Computational biology and bioinformatics, Diseases, Drug discovery, Genetics, Physiology, Signs and symptoms
وصف الملف: text
Relation: https://discovery.ucl.ac.uk/id/eprint/10129733/1/Gillmore_s41598-021-91113-6.pdf; https://discovery.ucl.ac.uk/id/eprint/10129733/
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2Academic Journal
المؤلفون: Judge, DP, Kristen, AV, Grogan, M, Maurer, MS, Falk, RH, Hanna, M, Gillmore, J, Garg, P, Vaishnaw, AK, Harrop, J, Powell, C, Karsten, V, Zhang, X, Sweetser, MT, Vest, J, Hawkins, PN
المصدر: Cardiovascular Drugs and Therapy (2020)
مصطلحات موضوعية: ATTR amyloidosis, Cardiomyopathy, RNA interference, Revusiran
وصف الملف: text
Relation: https://discovery.ucl.ac.uk/id/eprint/10092222/1/Judge2020_Article_Phase3MulticenterStudyOfRevusi.pdf; https://discovery.ucl.ac.uk/id/eprint/10092222/7/Judge2020_Article_CorrectionToPhase3MulticenterS.pdf; https://discovery.ucl.ac.uk/id/eprint/10092222/
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3Academic Journal
المؤلفون: Adams, D, Gonzalez-Duarte, A, O'Riordan, WD, Yang, C-C, Ueda, M, Kristen, AV, Tournev, I, Schmidt, HH, Coelho, T, Berk, JL, Lin, K-P, Vita, G, Attarian, S, Planté-Bordeneuve, V, Mezei, MM, Campistol, JM, Buades, J, Brannagan, TH, Kim, BJ, Oh, J, Parman, Y, Sekijima, Y, Hawkins, PN, Solomon, SD, Polydefkis, M, Dyck, PJ, Gandhi, PJ, Goyal, S, Chen, J, Strahs, AL, Nochur, SV, Sweetser, MT, Garg, PP, Vaishnaw, AK, Gollob, JA, Suhr, OB
المصدر: The New England Journal of Medicine , 379 (1) pp. 11-21. (2018)
مصطلحات موضوعية: Administration, Intravenous, Adult, Aged, 80 and over, Amyloid Neuropathies, Familial, Disease Progression, Double-Blind Method, Edema, Female, Gait Disorders, Neurologic, Humans, Infusions, Least-Squares Analysis, Male, Middle Aged, Polyneuropathies, Prealbumin, Quality of Life, RNA, Small Interfering, RNAi Therapeutics, Severity of Illness Index, Walk Test
وصف الملف: text
Relation: https://discovery.ucl.ac.uk/id/eprint/10053003/5/nejmoa1716153.pdf; https://discovery.ucl.ac.uk/id/eprint/10053003/11/nejmoa1716153_protocol.pdf; https://discovery.ucl.ac.uk/id/eprint/10053003/16/nejmoa1716153_appendix.pdf; https://discovery.ucl.ac.uk/id/eprint/10053003/21/Mebrahtu_and_infant%20cognitive_development.pdf; https://discovery.ucl.ac.uk/id/eprint/10053003/
الاتاحة: https://discovery.ucl.ac.uk/id/eprint/10053003/5/nejmoa1716153.pdf
https://discovery.ucl.ac.uk/id/eprint/10053003/11/nejmoa1716153_protocol.pdf
https://discovery.ucl.ac.uk/id/eprint/10053003/16/nejmoa1716153_appendix.pdf
https://discovery.ucl.ac.uk/id/eprint/10053003/21/Mebrahtu_and_infant%20cognitive_development.pdf
https://discovery.ucl.ac.uk/id/eprint/10053003/ -
4Conference
المؤلفون: Kraan, MC, Dinant, HJ, van Kuijk, AWR, Goedkoop, AY, Smeets, TJM, de Rie, MA, Dijkmans, BAC, Vaishnaw, AK, Tak, PP
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5Dissertation/ Thesis