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1Academic Journal
المؤلفون: Riedmayr, Lisa Maria, Hinrichsmeyer, Klara Sonnie, Thalhammer, Stefan Bernhard, Mittas, David Manuel, Karguth, Nina, Otify, Dina Yehia, Böhm, Sybille, Weber, Valentin Johannes, Bartoschek, Michael David, Splith, Victoria, Brümmer, Manuela, Ferreira, Raphael, Boon, Nanda, Wögenstein, Gabriele Maria, Grimm, Christian, Wijnholds, Jan, Mehlfeld, Verena, Michalakis, Stylianos, Fenske, Stefanie, Biel, Martin, Becirovic, Elvir
المصدر: Riedmayr, Lisa Maria; Hinrichsmeyer, Klara Sonnie; Thalhammer, Stefan Bernhard; Mittas, David Manuel; Karguth, Nina; Otify, Dina Yehia; Böhm, Sybille; Weber, Valentin Johannes; Bartoschek, Michael David; Splith, Victoria; Brümmer, Manuela; Ferreira, Raphael; Boon, Nanda; Wögenstein, Gabriele Maria; Grimm, Christian; Wijnholds, Jan; Mehlfeld, Verena; Michalakis, Stylianos; Fenske, Stefanie; Biel, Martin; Becirovic, Elvir (2023). mRNA trans-splicing dual AAV vectors for (epi)genome editing and gene therapy. Nature Communications, 14(1):6578.
مصطلحات موضوعية: Ophthalmology Clinic, 610 Medicine & health
وصف الملف: application/pdf
Relation: https://www.zora.uzh.ch/id/eprint/237872/1/ZORA237872.pdf; info:pmid/37852949; urn:issn:2041-1723
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2Academic Journal
المؤلفون: Böhm, Sybille, Splith, Victoria, Riedmayr, Lisa Maria, Rötzer, René Dominik, Gasparoni, Gilles, Nordström, Karl J V, Wagner, Johanna Elisabeth, Hinrichsmeyer, Klara Sonnie, Walter, Jörn, Wahl-Schott, Christian, Fenske, Stefanie, Biel, Martin, Michalakis, Stylianos, Becirovic, Elvir
المصدر: Böhm, Sybille; Splith, Victoria; Riedmayr, Lisa Maria; Rötzer, René Dominik; Gasparoni, Gilles; Nordström, Karl J V; Wagner, Johanna Elisabeth; Hinrichsmeyer, Klara Sonnie; Walter, Jörn; Wahl-Schott, Christian; Fenske, Stefanie; Biel, Martin; Michalakis, Stylianos; Becirovic, Elvir (2020). A gene therapy for inherited blindness using dCas9-VPR–mediated transcriptional activation. Science Advances, 6(34):eaba5614.
مصطلحات موضوعية: Ophthalmology Clinic, 610 Medicine & health
وصف الملف: application/pdf
Relation: https://www.zora.uzh.ch/id/eprint/254922/1/ZORA_254922.pdf; info:pmid/32875106; urn:issn:2375-2548
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3Electronic Resource
المؤلفون: Riedmayr, Lisa Maria; https://orcid.org/0000-0002-0307-2507, Hinrichsmeyer, Klara Sonnie; https://orcid.org/0000-0001-8284-1775, Thalhammer, Stefan Bernhard, Mittas, David Manuel, Karguth, Nina, Otify, Dina Yehia, Böhm, Sybille, Weber, Valentin Johannes, Bartoschek, Michael David; https://orcid.org/0000-0003-4238-3970, Splith, Victoria, Brümmer, Manuela, Ferreira, Raphael, Boon, Nanda; https://orcid.org/0000-0001-9756-8898, Wögenstein, Gabriele Maria, Grimm, Christian; https://orcid.org/0000-0001-9318-4352, Wijnholds, Jan; https://orcid.org/0000-0003-0099-460X, Mehlfeld, Verena, Michalakis, Stylianos; https://orcid.org/0000-0001-5092-9238, Fenske, Stefanie; https://orcid.org/0000-0002-6994-8401, Biel, Martin, Becirovic, Elvir; https://orcid.org/0000-0001-8801-0649
المصدر: Riedmayr, Lisa Maria; Hinrichsmeyer, Klara Sonnie; Thalhammer, Stefan Bernhard; Mittas, David Manuel; Karguth, Nina; Otify, Dina Yehia; Böhm, Sybille; Weber, Valentin Johannes; Bartoschek, Michael David; Splith, Victoria; Brümmer, Manuela; Ferreira, Raphael; Boon, Nanda; Wögenstein, Gabriele Maria; Grimm, Christian; Wijnholds, Jan; Mehlfeld, Verena; Michalakis, Stylianos; Fenske, Stefanie; Biel, Martin; Becirovic, Elvir (2023). mRNA trans-splicing dual AAV vectors for (epi)genome editing and gene therapy. Nature Communications, 14(1):6578.
مصطلحات الفهرس: Ophthalmology Clinic, 610 Medicine & health, Journal Article, PeerReviewed, info:eu-repo/semantics/article, info:eu-repo/semantics/publishedVersion
URL:
https://www.zora.uzh.ch/id/eprint/237872/ https://www.zora.uzh.ch/id/eprint/237872
10.1038/s41467-023-42386-0 -
4Academic Journal
المؤلفون: Riedmayr, Lisa M, Hinrichsmeyer, Klara S, Karguth, Nina, Böhm, Sybille, Splith, Victoria, Michalakis, Stylianos, Becirovic, Elvir
المصدر: Riedmayr, Lisa M; Hinrichsmeyer, Klara S; Karguth, Nina; Böhm, Sybille; Splith, Victoria; Michalakis, Stylianos; Becirovic, Elvir (2022). dCas9-VPR-mediated transcriptional activation of functionally equivalent genes for gene therapy. Nature Protocols, 17(3):781-818.
مصطلحات موضوعية: Ophthalmology Clinic, 610 Medicine & health
Relation: https://www.zora.uzh.ch/223129; info:pmid/35132255; urn:issn:1750-2799
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5Academic Journal
المؤلفون: Riedmayr, Lisa M., Hinrichsmeyer, Klara S., Karguth, Nina, Böhm, Sybille, Splith, Victoria, Michalakis, Stylianos, Becirovic, Elvir
المساهمون: Deutsche Forschungsgemeinschaft
المصدر: Nature Protocols ; volume 17, issue 3, page 781-818 ; ISSN 1754-2189 1750-2799
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6Electronic Resource
المؤلفون: Böhm, Sybille; https://orcid.org/0000-0002-3654-3846, Splith, Victoria, Riedmayr, Lisa Maria; https://orcid.org/0000-0002-0307-2507, Rötzer, René Dominik; https://orcid.org/0000-0002-4862-9073, Gasparoni, Gilles; https://orcid.org/0000-0002-6423-4637, Nordström, Karl J V; https://orcid.org/0000-0001-6231-4417, Wagner, Johanna Elisabeth, Hinrichsmeyer, Klara Sonnie, Walter, Jörn, Wahl-Schott, Christian, Fenske, Stefanie; https://orcid.org/0000-0002-6994-8401, Biel, Martin, Michalakis, Stylianos; https://orcid.org/0000-0001-5092-9238, Becirovic, Elvir; https://orcid.org/0000-0001-8801-0649
المصدر: Böhm, Sybille; Splith, Victoria; Riedmayr, Lisa Maria; Rötzer, René Dominik; Gasparoni, Gilles; Nordström, Karl J V; Wagner, Johanna Elisabeth; Hinrichsmeyer, Klara Sonnie; Walter, Jörn; Wahl-Schott, Christian; Fenske, Stefanie; Biel, Martin; Michalakis, Stylianos; Becirovic, Elvir (2020). A gene therapy for inherited blindness using dCas9-VPR–mediated transcriptional activation. Science Advances, 6(34):eaba5614.
مصطلحات الفهرس: Ophthalmology Clinic, 610 Medicine & health, Journal Article, PeerReviewed, info:eu-repo/semantics/article, info:eu-repo/semantics/publishedVersion
URL:
https://www.zora.uzh.ch/id/eprint/254922/ https://www.zora.uzh.ch/id/eprint/254922
10.1126/sciadv.aba5614 -
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8
المؤلفون: Postel, Kai, Bellmann, Jessica, Splith, Victoria, Ader, Marius
المصدر: Molecular Vision
مصطلحات موضوعية: Aging, genetic structures, Staining and Labeling, Cell Membrane, Gene Expression Regulation, Developmental, Molecular Sequence Annotation, Cadherins, eye diseases, Mice, Inbred C57BL, Mice, Retinal Rod Photoreceptor Cells, Animals, sense organs, Biomarkers, In Situ Hybridization, Research Article, Oligonucleotide Array Sequence Analysis
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9Academic Journal
المؤلفون: Karimova, Madina, Splith, Victoria, Karpinski, Janet, Pisabarro, M. Teresa, Buchholz, Frank
المصدر: Scientific Reports
مصطلحات موضوعية: Department für Pharmazie - Zentrum für Pharmaforschung, ddc:540
وصف الملف: application/pdf
Relation: Karimova, Madina; Splith, Victoria; Karpinski, Janet; Pisabarro, M. Teresa; Buchholz, Frank (2016): Discovery of Nigri/nox and Panto/pox site-specific recombinase systems facilitates advanced genome engineering. In: Scientific Reports, Vol. 6, 30130 [PDF, 1MB]; https://epub.ub.uni-muenchen.de/37692/1/10.1038_srep30130.pdf; http://nbn-resolving.de/urn:nbn:de:bvb:19-epub-37692-8; https://epub.ub.uni-muenchen.de/37692/
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10Academic Journal
المؤلفون: Perera, Arshan, Eisen, David, Wagner, Mirko, Laube, Silvia K., Künzel, Andrea F., Koch, Susanne, Steinbacher, Jessica, Schulze, Elisabeth, Splith, Victoria, Mittermeier, Nana, Mueller, Markus, Biel, Martin, Carell, Thomas, Michalakis, Stylianos
المصدر: Cell Reports
مصطلحات موضوعية: Department Chemie, ddc:540
وصف الملف: application/pdf
Relation: Perera, Arshan; Eisen, David; Wagner, Mirko; Laube, Silvia K.; Künzel, Andrea F.; Koch, Susanne; Steinbacher, Jessica; Schulze, Elisabeth; Splith, Victoria; Mittermeier, Nana; Mueller, Markus; Biel, Martin; Carell, Thomas; Michalakis, Stylianos (2015): TET3 Is Recruited by REST for Context-Specific Hydroxymethylation and Induction of Gene Expression. In: Cell Reports, Vol. 11, Nr. 2: S. 283-294 [PDF, 3MB]; https://epub.ub.uni-muenchen.de/34324/1/10.1016_j.celrep.2015.03.020.pdf; http://nbn-resolving.de/urn:nbn:de:bvb:19-epub-34324-4; https://epub.ub.uni-muenchen.de/34324/
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11Academic Journal
المؤلفون: Witte, Kristina, Kaiser, Anette, Schmidt, Peter, Splith, Victoria, Thomas, Lars, Berndt, Sandra, Huster, Daniel, Beck-Sickinger, Annette G.
المصدر: bchm ; volume 394, issue 8, page 1045-1056 ; ISSN 1437-4315 1431-6730
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12Periodical
المؤلفون: Perera, Arshan, Eisen, David, Wagner, Mirko, Laube, Silvia K., Künzel, Andrea F., Koch, Susanne, Steinbacher, Jessica, Schulze, Elisabeth, Splith, Victoria, Mittermeier, Nana, Müller, Markus, Biel, Martin, Carell, Thomas, Michalakis, Stylianos
المصدر: Cell Reports; 20240101, Issue: Preprints