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1Academic Journal
المؤلفون: Funes, Salome, Jung, Jonathan, Gadd, Del Hayden, Mosqueda, Michelle, Zhong, Jianjun, Shankaracharya, Unger, Matthew, Stallworth, Karly, Cameron, Debra, Rotunno, Melissa S, Dawes, Pepper, Fowler-Magaw, Megan, Keagle, Pamela J, McDonough, Justin A, Boopathy, Sivakumar, Sena-Esteves, Miguel, Nickerson, Jeffrey A, Lutz, Cathleen, Skarnes, William C, Lim, Elaine T, Schafer, Dorothy P, Massi, Francesca, Landers, John E, Bosco, Daryl A
المساهمون: Biochemistry and Molecular Biotechnology, Brudnick Neuropsychiatric Research Institute, Genomics and Computational Biology, Horae Gene Therapy Center, Microbiology and Physiological Systems, Molecular, Cell and Cancer Biology, Morningside Graduate School of Biomedical Sciences, Neurobiology, Neurology, Pediatrics, Schafer Lab, Salome Funes, Michelle Mosqueda, Jonathan Jung, Matthew Unger
المصدر: Nature communications ; 15 ; 1 ; 2497 ; United States ; England
مصطلحات موضوعية: Amyotrophic lateral sclerosis, Microglia
Relation: This article is based on a previously available preprint in bioRxiv, https://doi.org/10.1101/2023.06.01.541136; Nature Communications; https://doi.org/10.1038/s41467-024-46695-w; Funes S, Jung J, Gadd DH, Mosqueda M, Zhong J, Shankaracharya, Unger M, Stallworth K, Cameron D, Rotunno MS, Dawes P, Fowler-Magaw M, Keagle PJ, McDonough JA, Boopathy S, Sena-Esteves M, Nickerson JA, Lutz C, Skarnes WC, Lim ET, Schafer DP, Massi F, Landers JE, Bosco DA. Expression of ALS-PFN1 impairs vesicular degradation in iPSC-derived microglia. Nat Commun. 2024 Mar 20;15(1):2497. doi:10.1038/s41467-024-46695-w. PMID: 38509062; PMCID: PMC10954694.; http://hdl.handle.net/20.500.14038/53350
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2Academic Journal
المؤلفون: Fang, Minggang, Deibler, Sara K, Krishnamurthy, Pranathi Meda, Wang, Feng, Rodriguez, Paola, Banday, Shahid, Virbasius, Ching-Man, Sena-Esteves, Miguel, Watts, Jonathan K, Green, Michael R
المساهمون: Molecular, Cell and Cancer Biology, Neurology, RNA Therapeutics Institute
المصدر: Frontiers in neuroscience ; 18 ; 1348478 ; United States ; Switzerland
مصطلحات موضوعية: ASO - antisense oligonucleotides, EZH2 (enhancer of zeste homolog 2), FMR1 reactivation, FMR1 silencing, FXS, neuron differentiation
Relation: Frontiers in Neuroscience; https://doi.org/10.3389/fnins.2024.1348478; Fang M, Deibler SK, Krishnamurthy PM, Wang F, Rodriguez P, Banday S, Virbasius CM, Sena-Esteves M, Watts JK, Green MR. EZH2 inhibition reactivates epigenetically silenced FMR1 and normalizes molecular and electrophysiological abnormalities in fragile X syndrome neurons. Front Neurosci. 2024 Feb 21;18:1348478. doi:10.3389/fnins.2024.1348478. PMID: 38449737; PMCID: PMC10915284.; http://hdl.handle.net/20.500.14038/53336
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3Report
المؤلفون: Maguire, Anne S, Ta, Linh, Gross, Amanda L, Osterhoudt, Devin E, Cannon, Jessica S, Hall, Paige I, Sandey, Maninder, Seyfried, Thomas N, Gray-Edwards, Heather L, Sena-Esteves, Miguel, Martin, Douglas R
المساهمون: Radiology, Horae Gene Therapy Center, Neurology
المصدر: bioRxiv : the preprint server for biology ; United States
مصطلحات موضوعية: Pathology, feline Sandhoff Disease, gene therapy
وصف الملف: application/pdf
Relation: bioRxiv; https://doi.org/10.1101/2024.11.15.623838; 2024.11.15.623838; https://repository.escholarship.umassmed.edu/handle/20.500.14038/53937
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4Academic Journal
المؤلفون: Benatti, Hector Ribeiro, Prestigiacomo, Rachel D, Taghian, Toloo, Miller, Rachael, King, Robert, Gounis, Matthew J, Celik, Ugur, Bertrand, Stephanie, Tuominen, Susan, Bierfeldt, Lindsey, Parsley, Elizabeth, Gallagher, Jillian, Hall, Erin F, McElroy, Abigail W, Sena-Esteves, Miguel, Khvorova, Anastasia, Aronin, Neil, Gray-Edwards, Heather L
المساهمون: Center for Clinical and Translational Science, Horae Gene Therapy Center, Medicine, Morningside Graduate School of Biomedical Sciences, Neurology, Radiology, RNA Therapeutics Institute, Animal Medicine, Rachael Miller, Jillian Gallagher
المصدر: Molecular therapy. Methods & clinical development ; 31 ; 101122 ; United States
مصطلحات موضوعية: CNS drug administration, CSF drug delivery, Ommaya reservoir, i.c.v. catheter, i.c.v. injection, large animal model, oligonucleotide safety assessment, siRNA
Relation: Molecular Therapy – Methods & Clinical Development; https://doi.org/10.1016/j.omtm.2023.101122; Benatti HR, Prestigiacomo RD, Taghian T, Miller R, King R, Gounis MJ, Celik U, Bertrand S, Tuominen S, Bierfeldt L, Parsley E, Gallagher J, Hall EF, McElroy AW, Sena-Esteves M, Khvorova A, Aronin N, Gray-Edwards HL. Awake intracerebroventricular delivery and safety assessment of oligonucleotides in a large animal model. Mol Ther Methods Clin Dev. 2023 Sep 26;31:101122. doi:10.1016/j.omtm.2023.101122. PMID: 37920238; PMCID: PMC10618110.; http://hdl.handle.net/20.500.14038/52769; Molecular therapy. Methods & clinical development
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5Academic Journal
المؤلفون: Kell, Pamela, Sidhu, Rohini, Qian, Mingxing, Mishra, Sonali, Nicoli, Elena-Raluca, D'Souza, Precilla, Tifft, Cynthia J, Gross, Amanda L, Gray-Edwards, Heather L, Martin, Douglas R, Sena-Esteves, Miguel, Dietzen, Dennis J, Singh, Manmilan, Luo, Jingqin, Schaffer, Jean E, Ory, Daniel S, Jiang, Xuntian
المساهمون: Horae Gene Therapy Center, Neurology, Radiology
المصدر: EBioMedicine ; 92 ; 104627 ; Netherlands
مصطلحات موضوعية: GM1 gangliosidosis, Gene therapy, Pentasaccharide, Pharmacodynamic biomarker
Relation: EBioMedicine; https://doi.org/10.1016/j.ebiom.2023.104627; Kell P, Sidhu R, Qian M, Mishra S, Nicoli ER, D'Souza P, Tifft CJ, Gross AL, Gray-Edwards HL, Martin DR, Sena-Esteves M, Dietzen DJ, Singh M, Luo J, Schaffer JE, Ory DS, Jiang X. A pentasaccharide for monitoring pharmacodynamic response to gene therapy in GM1 gangliosidosis. EBioMedicine. 2023 Jun;92:104627. doi:10.1016/j.ebiom.2023.104627. Epub 2023 May 31. PMID: 37267847; PMCID: PMC10277919.; http://hdl.handle.net/20.500.14038/52243
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6Academic Journal
المؤلفون: Kumar, Meenakshi Sundaram, Fowler-Magaw, Megan E, Kulick, Daniel, Boopathy, Sivakumar, Gadd, Del Hayden, Rotunno, Melissa, Douthwright, Catherine, Golebiowski, Diane, Yusuf, Issa, Xu, Zuoshang, Brown, Robert H, Sena-Esteves, Miguel, O'Neil, Alison L, Bosco, Daryl A
المساهمون: Biochemistry and Molecular Biotechnology, Horae Gene Therapy Center, Morningside Graduate School of Biomedical Sciences, Neurology
المصدر: International journal of molecular sciences ; 23 ; 24 ; Switzerland
مصطلحات موضوعية: amyotrophic lateral sclerosis (ALS) (Lou Gehrig disease), antibody engineering, neurite outgrowth, protein misfolding, superoxide dismutase (SOD), UMCCTS funding
Relation: International Journal of Molecular Sciences; https://doi.org/10.3390/ijms232416013; Kumar MS, Fowler-Magaw ME, Kulick D, Boopathy S, Gadd DH, Rotunno M, Douthwright C, Golebiowski D, Yusuf I, Xu Z, Brown RH Jr, Sena-Esteves M, O'Neil AL, Bosco DA. Anti-SOD1 Nanobodies That Stabilize Misfolded SOD1 Proteins Also Promote Neurite Outgrowth in Mutant SOD1 Human Neurons. Int J Mol Sci. 2022 Dec 16;23(24):16013. doi:10.3390/ijms232416013. PMID: 36555655; PMCID: PMC9784173.; http://hdl.handle.net/20.500.14038/51735
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7Academic Journal
المؤلفون: Hocquemiller, Michaël, Giersch, Laura, Mei, Xin, Gross, Amanda L, Randle, Ashley N, Gray-Edwards, Heather L, Hudson, Judith A, Todeasa, Sophia, Stoica, Lorelei, Martin, Douglas R, Sena-Esteves, Miguel, Aiach, Karen, Laufer, Ralph
المساهمون: Horae Gene Therapy Center, Neurology, Radiology
المصدر: Molecular therapy. Methods & clinical development ; 27 ; 281 ; 292 ; United States
مصطلحات موضوعية: AAV, GM1, gangliosidosis, gene therapy, lysosomal storage disease
Relation: Molecular Therapy – Methods & Clinical Development; https://doi.org/10.1016/j.omtm.2022.10.004; Hocquemiller M, Giersch L, Mei X, Gross AL, Randle AN, Gray-Edwards HL, Hudson JA, Todeasa S, Stoica L, Martin DR, Sena-Esteves M, Aiach K, Laufer R. AAVrh10 vector corrects pathology in animal models of GM1 gangliosidosis and achieves widespread distribution in the CNS of nonhuman primates. Mol Ther Methods Clin Dev. 2022 Oct 7;27:281-292. doi:10.1016/j.omtm.2022.10.004. PMID: 36320411; PMCID: PMC9594110.; http://hdl.handle.net/20.500.14038/51580; Molecular therapy. Methods & clinical development
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8Academic Journal
المؤلفون: Wentworth, Simon, Batista, Ana Rita, Alterman, Julia, Khvorova, Anastasia, Sena-Esteves, Miguel
المصدر: Neuro-Oncology ; volume 25, issue Supplement_1, page i16-i16 ; ISSN 1522-8517 1523-5866
مصطلحات موضوعية: Cancer Research, Neurology (clinical), Oncology
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9Book
المؤلفون: Aronin, Neil, Sena-Esteves, Miguel, Khvorova, Anastasia, DiFiglia, Marian, Brodsky, Michael
المصدر: Huntington's Disease ; page 523-549 ; ISBN 9780323956727
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10Academic Journal
المؤلفون: Choudhury, Sourav Roy, Harris, Anne F., Cabral, Damien J., Keeler, Allison M, Ferreira, Jennifer, Su, Qin, Stoica, Lorelei, Aronin, Neil, Gao, Guangping, Sena-Esteves, Miguel
المساهمون: Department of Medicine, Department of Microbiology and Physiological Systems, Gene Therapy Center, Department of Neurology, RNA Therapeutics Institute
المصدر: Molecular therapy : the journal of the American Society of Gene Therapy ; 24 ; 4 ; 726-35
مصطلحات موضوعية: Biochemistry, Biophysics, and Structural Biology, Cell and Developmental Biology, Genetics and Genomics, Neuroscience and Neurobiology, Therapeutics
Relation: Link to Article in PubMed; https://doi.org/10.1038/mt.2015.231; Mol Ther. 2016 Apr;24(4):726-35. doi:10.1038/mt.2015.231. Epub 2015 Dec 28. Link to article on publisher's site; 1525-0016 (Linking); http://hdl.handle.net/20.500.14038/48807; https://escholarship.umassmed.edu/cgi/viewcontent.cgi?article=1017&context=rti_pubs&unstamped=1; https://escholarship.umassmed.edu/rti_pubs/18; rti_pubs/18
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11Academic Journal
المؤلفون: Taghian, Toloo, Batista, Ana Rita, Rodriguez, Paola, Mesa, Katerina, Zheng, Shaokuan, King, Robert M., Gounis, Matthew J., Todeasa, Sophia H., Sena-Esteves, Miguel, Meade, Thomas J., Gray-Edwards, Heather L
المساهمون: Department of Neurology, Department of Radiology, Horae Gene Therapy Center
المصدر: Molecular therapy. Methods and clinical development ; 23 ; 128-134
مصطلحات موضوعية: AAV gene therapy, GM1 gangliosidosis, MR tracking of enzyme expression, enzyme-activated contrast agent probes, magnetic resonance imaging, Amino Acids, Peptides, and Proteins, Analytical, Diagnostic and Therapeutic Techniques and Equipment, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Enzymes and Coenzymes, Genetics and Genomics, Radiology
Relation: Link to Article in PubMed; Taghian T, Batista AR, Kamper S, Caldwell M, Lilley L, Li H, Rodriguez P, Mesa K, Zheng S, King RM, Gounis MJ, Todeasa S, Maguire A, Martin DR, Sena-Esteves M, Meade TJ, Gray-Edwards HL. Real-time MR tracking of AAV gene therapy with βgal-responsive MR probe in a murine model of GM1-gangliosidosis. Mol Ther Methods Clin Dev. 2021 Aug 26;23:128-134. doi:10.1016/j.omtm.2021.08.003. PMID: 34703836; PMCID: PMC8517204. Link to article on publisher's site; 2329-0501 (Linking); http://hdl.handle.net/20.500.14038/48564; https://escholarship.umassmed.edu/cgi/viewcontent.cgi?article=1679&context=radiology_pubs&unstamped=1; https://escholarship.umassmed.edu/radiology_pubs/662; radiology_pubs/662
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12Academic Journal
المؤلفون: Gray-Edwards, Heather L, Jiang, Xuntian, Randle, Ashley N., Taylor, Amanda R., Voss, Taylor L., Johnson, Aime K., McCurdy, Victoria J., Sena-Esteves, Miguel, Ory, Daniel S., Martin, Douglas R.
المساهمون: Department of Neurology
المصدر: Molecular therapy. Methods and clinical development ; 6 ; 135-142
مصطلحات موضوعية: AAV, GM1 gangliosidosis, adeno-associated virus, biomarkers, feline, gene therapy, lipidomics, neurologic disease, Animal Sciences, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetics and Genomics, Nervous System Diseases, Nutritional and Metabolic Diseases
Relation: Link to Article in PubMed; Mol Ther Methods Clin Dev. 2017 Jul 26;6:135-142. doi:10.1016/j.omtm.2017.07.005. eCollection 2017 Sep 15. Link to article on publisher's site; 2329-0501 (Linking); http://hdl.handle.net/20.500.14038/40391; https://escholarship.umassmed.edu/cgi/viewcontent.cgi?article=4206&context=oapubs&unstamped=1; https://escholarship.umassmed.edu/oapubs/3198; oapubs/3198
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13Academic Journal
المؤلفون: Brekk, Oeystein R., Korecka, Joanna A., Crapart, Cecile C., Huebecker, Mylene, MacBain, Zachary K., Rosenthal, Sara Ann, Sena-Esteves, Miguel, Priestman, David A., Platt, Frances M., Isacson, Ole, Hallett, Penelope J.
المساهمون: Department of Neurology
المصدر: Acta neuropathologica communications ; 8 ; 1 ; 127
مصطلحات موضوعية: Lipid binding, Neuroprotection, Parkinson’s disease, Sandhoff disease, α-Synuclein, β-Hexosaminidase, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Lipids, Nervous System, Nervous System Diseases, Neurology, Neuroscience and Neurobiology, Nutritional and Metabolic Diseases
Relation: Link to Article in PubMed; Brekk OR, Korecka JA, Crapart CC, Huebecker M, MacBain ZK, Rosenthal SA, Sena-Esteves M, Priestman DA, Platt FM, Isacson O, Hallett PJ. Upregulating β-hexosaminidase activity in rodents prevents α-synuclein lipid associations and protects dopaminergic neurons from α-synuclein-mediated neurotoxicity. Acta Neuropathol Commun. 2020 Aug 6;8(1):127. doi:10.1186/s40478-020-01004-6. PMID: 32762772; PMCID: PMC7409708. Link to article on publisher's site; 2051-5960 (Linking); http://hdl.handle.net/20.500.14038/41522; https://escholarship.umassmed.edu/cgi/viewcontent.cgi?article=5329&context=oapubs&unstamped=1; https://escholarship.umassmed.edu/oapubs/4303; oapubs/4303
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14Academic Journal
المساهمون: Department of Neurology
المصدر: Molecular therapy. Methods and clinical development ; 15 ; 320-332
مصطلحات موضوعية: AAV capsid library, AAV vector, adeno-associated virus vector, central nervous system, gene delivery, gene therapy, transduction efficiency, Genetics and Genomics, Molecular, Cellular, and Tissue Engineering, Nervous System, Therapeutics, Viruses
Relation: Link to Article in PubMed; Mol Ther Methods Clin Dev. 2019 Oct 23;15:320-332. doi:10.1016/j.omtm.2019.10.007. eCollection 2019 Dec 13. Link to article on publisher's site; 2329-0501 (Linking); http://hdl.handle.net/20.500.14038/41316; https://escholarship.umassmed.edu/cgi/viewcontent.cgi?article=5120&context=oapubs&unstamped=1; https://escholarship.umassmed.edu/oapubs/4101; oapubs/4101
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15Academic Journal
المؤلفون: Prabhakar, Shilpa, Cheah, Pike See, Zhang, Xuan, Zinter, Max, Gianatasio, Maria, Hudry, Eloise, Bronson, Roderick T., Kwiatkowski, David J., Stemmer-Rachamimov, Anat, Maguire, Casey A., Sena-Esteves, Miguel, Tannous, Bakhos A., Breakefield, Xandra O.
المساهمون: Horae Gene Therapy Center, Department of Neurology
المصدر: Molecular therapy. Methods and clinical development ; 15 ; 18-26
مصطلحات موضوعية: brain, gene therapy, neurology, tumor suppressor, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetics and Genomics, Molecular Biology, Nervous System Diseases, Therapeutics
Relation: Link to Article in PubMed; Mol Ther Methods Clin Dev. 2019 Aug 16;15:18-26. doi:10.1016/j.omtm.2019.08.003. eCollection 2019 Dec 13. Link to article on publisher's site; 2329-0501 (Linking); http://hdl.handle.net/20.500.14038/41208; https://escholarship.umassmed.edu/cgi/viewcontent.cgi?article=5012&context=oapubs&unstamped=1; https://escholarship.umassmed.edu/oapubs/3995; oapubs/3995
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16Academic Journal
المؤلفون: Latour, Yvonne L., Yoon, Robin, Thomas, Sarah E., Grant, Christina, Li, Cuiling, Sena-Esteves, Miguel, Allende, Maria L., Proia, Richard L., Tifft, Cynthia J.
المساهمون: Gene Therapy Center, Department of Neurology
المصدر: Molecular genetics and metabolism reports ; 21 ; 100513
مصطلحات موضوعية: 4MU, 4-methylumbelliferyl, AAV, adeno-associated virus, AAV9, AAV serotype 9, BSA, bovine serum albumin, CNS, central nervous system, CPB, citrate phosphate buffer, EB, embryoid body, GFP, green fluorescent protein, HPTLC, high-performance thin-layer chromatography, PBS, phosphate-buffered saline, RT-qPCR, real-time quantitative polymerase chain reaction, SD, standard deviation, X-gal, 5-bromo-4-chloro-3-indolyl-β-D-galactopyranoside, hiPSC, human induced pluripotent stem cells, iPS, induced pluripotent stem
Relation: Link to Article in PubMed; Mol Genet Metab Rep. 2019 Sep 11;21:100513. doi:10.1016/j.ymgmr.2019.100513. eCollection 2019 Dec. Link to article on publisher's site; 2214-4269 (Linking); http://hdl.handle.net/20.500.14038/41206; https://escholarship.umassmed.edu/cgi/viewcontent.cgi?article=5010&context=oapubs&unstamped=1; https://escholarship.umassmed.edu/oapubs/3993; oapubs/3993
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17Academic Journal
المؤلفون: Wang, Dan, Zhong, Li, Li, Mengxin, Li, Jia, Tran, Karen, Ren, Lingzhi, He, Ran, Xie, Jun, Moser, Richard P., Fraser, Cara, Kuchel, Tim, Sena-Esteves, Miguel, Flotte, Terence R., Aronin, Neil, Gao, Guangping
المساهمون: Department of Medicine, Department of Pediatrics, Department of Neurosurgery, Viral Vector Core, Department of Microbiology and Physiological Systems, Li Weibo Institute for Rare Diseases Research, Horae Gene Therapy Center
المصدر: Molecular Therapy. Methods and Clinical Development ; 11 ; 65-72
مصطلحات موضوعية: CNS gene transfer, adeno-associated virus, gene therapy, large animals, neutralizing antibody, Genetics and Genomics, Immunoprophylaxis and Therapy, Molecular Biology, Therapeutics
Relation: Link to article in PubMed; Mol Ther Methods Clin Dev. 2018 Oct 4;11:65-72. doi:10.1016/j.omtm.2018.09.003. eCollection 2018 Dec 14. Link to article on publisher's site; http://hdl.handle.net/20.500.14038/40785; https://escholarship.umassmed.edu/cgi/viewcontent.cgi?article=4606&context=oapubs&unstamped=1; https://escholarship.umassmed.edu/oapubs/3594; oapubs/3594
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18Academic Journal
المؤلفون: Allende, Maria L., Cook, Emily K., Larman, Bridget C., Nugent, Adrienne, Brady, Jacqueline M., Golebiowski, Diane, Sena-Esteves, Miguel, Tifft, Cynthia J., Proia, Richard L.
المساهمون: Horae Gene Therapy Center, Department of Neurology
المصدر: Journal of lipid research ; 59 ; 3 ; 550-563
مصطلحات موضوعية: Clustered Regularly Interspaced Short Palindromic Repeats/Cas9, GM2 gangliosidosis, Tay-Sachs disease, brain development, brain lipids, gangliosides, patient-derived induced pluripotent stem cells, sphingolipids, storage diseases, Cell Biology, Cells, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Developmental Biology, Genetic Phenomena, Lipids, Nervous System Diseases, Neuroscience and Neurobiology, Nutritional and Metabolic Diseases
Relation: Link to Article in PubMed; J Lipid Res. 2018 Mar;59(3):550-563. doi:10.1194/jlr.M081323. Epub 2018 Jan 22. Link to article on publisher's site; 0022-2275 (Linking); http://hdl.handle.net/20.500.14038/40546; https://escholarship.umassmed.edu/cgi/viewcontent.cgi?article=4363&context=oapubs&unstamped=1; https://escholarship.umassmed.edu/oapubs/3352; oapubs/3352
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19Academic Journal
المساهمون: Department of Microbiology and Physiological Systems, Department of Neurology, Horae Gene Therapy Center
المصدر: Molecular oncology ; 11 ; 2 ; 180-193
مصطلحات موضوعية: adeno-associated virus, glioblastoma, interferon-beta, intracranial, syngeneic, xenograft, Cancer Biology, Genetics and Genomics, Neoplasms, Oncology, Therapeutics
Relation: Link to Article in PubMed; Mol Oncol. 2017 Feb;11(2):180-193. Epub 2017 Jan 18. Link to article on publisher's site; 1574-7891 (Linking); http://hdl.handle.net/20.500.14038/40262; https://escholarship.umassmed.edu/cgi/viewcontent.cgi?article=4062&context=oapubs&unstamped=1; https://escholarship.umassmed.edu/oapubs/3057; oapubs/3057
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20Academic Journal
المؤلفون: Vodicka, Petr, Chase, Kathryn O., Iuliano, Maria, Tousley, Adelaide, Valentine, Dana T., Sapp, Ellen, Kegel-Gleason, Kimberly B., Sena-Esteves, Miguel, Aronin, Neil, DiFiglia, Marian
المساهمون: Horae Gene Therapy Center, Department of Medicine, Division of Endocrinology and Metabolism, Department of Neurology
المصدر: Journal of Huntington's disease ; 5 ; 3 ; 249-260
مصطلحات موضوعية: Adeno associated virus, GRP78/BiP, Huntington’s disease, LC3, TFEB, autophagy, huntingtin, neurodegeneration, striatum, Cell Biology, Genetics and Genomics, Nervous System Diseases, Neurology
Relation: Link to Article in PubMed; J Huntingtons Dis. 2016 Oct 1;5(3):249-260. Link to article on publisher's site; 1879-6397 (Linking); http://hdl.handle.net/20.500.14038/40139; https://escholarship.umassmed.edu/cgi/viewcontent.cgi?article=3944&context=oapubs&unstamped=1; https://escholarship.umassmed.edu/oapubs/2939; 9532581; oapubs/2939
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