-
1Academic Journal
المؤلفون: Seemin S. Ahmed, Hillard Rubin, Minglun Wang, Deiby Faulkner, Arnold Sengooba, Serena N. Dollive, Nancy Avila, Jeff L. Ellsworth, Diana Lamppu, Maria Lobikin, Jason Lotterhand, Laura Adamson-Small, Teresa Wright, Albert Seymour, Omar L. Francone
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 17, Iss , Pp 568-580 (2020)
وصف الملف: electronic resource
-
2Academic Journal
المؤلفون: Gibran Nasir, Rajiv Chopra, Fiona Elwood, Seemin S. Ahmed
المصدر: Frontiers in Medicine, Vol 8 (2021)
مصطلحات موضوعية: Krabbe disease (globoid cell leukodystrophy), leukodystrophies, adeno-associated virus, gene therapy, galactocerebrosidase, psychosine, Medicine (General), R5-920
وصف الملف: electronic resource
-
3
المصدر: Human Gene Therapy. 33:221-222
مصطلحات موضوعية: Genetics, Molecular Medicine, Molecular Biology