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1Academic Journal
المؤلفون: Bornert, Olivier, Peking, Patricia, Bremer, Jeroen, Koller, Ulrich, van den Akker, Peter C., Aartsma-Rus, Annemieke, Pasmooij, Anna M. G., Murauer, Eva M., Nystroem, Alexander
المصدر: Bornert , O , Peking , P , Bremer , J , Koller , U , van den Akker , P C , Aartsma-Rus , A , Pasmooij , A M G , Murauer , E M & Nystroem , A 2017 , ' RNA-based therapies for genodermatoses ' , Experimental dermatology , vol. 26 , no. 1 , pp. 3-10 . https://doi.org/10.1111/exd.13141
مصطلحات موضوعية: antisense oligonucleotides, in vitro-transcribed mRNA, RNA trans-splicing, siRNA, skin, DYSTROPHIC EPIDERMOLYSIS-BULLOSA, DUCHENNE MUSCULAR-DYSTROPHY, PREMATURE TERMINATION CODONS, DERMAL-EPIDERMAL JUNCTION, SKIN ADHESION DISORDERS, MODIFIED MESSENGER-RNA, VII COLLAGEN, GENE-THERAPY, MOUSE MODEL
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المؤلفون: Eva M. Murauer, Olivier Bornert, Anna M.G. Pasmooij, Peter C. van den Akker, Alexander Nyström, Annemieke Aartsma-Rus, Patricia Peking, Jeroen Bremer, Ulrich Koller
المصدر: Experimental Dermatology, 26(1), 3-10
مصطلحات موضوعية: 0301 basic medicine, RNA trans-splicing, SKIN ADHESION DISORDERS, VII COLLAGEN, Small interfering RNA, skin, in vitro-transcribed mRNA, Trans-splicing, PREMATURE TERMINATION CODONS, Dermatology, Computational biology, Biology, Biochemistry, Trans-Splicing, DUCHENNE MUSCULAR-DYSTROPHY, 03 medical and health sciences, 0302 clinical medicine, Genome editing, Gene Knockdown Techniques, medicine, Animals, Humans, RNA, Messenger, Molecular Biology, Genetics, Gene knockdown, MODIFIED MESSENGER-RNA, GENE-THERAPY, Genodermatosis, Skin Diseases, Genetic, RNA, Genetic Therapy, MOUSE MODEL, Oligonucleotides, Antisense, medicine.disease, 030104 developmental biology, 030220 oncology & carcinogenesis, siRNA, RNA splicing, DYSTROPHIC EPIDERMOLYSIS-BULLOSA, antisense oligonucleotides, DERMAL-EPIDERMAL JUNCTION