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1Academic Journal
المؤلفون: Andrews, Jinsy A., Meng, Lisa, Kulke, Sarah F., Rudnicki, Stacy A., Wolff, Andrew A., Bozik, Michael E., Malik, Fady I., Shefner, Jeremy M.
Thesis Advisors: Univ Arizona, Barrow Neurol Inst, Cytokinetics, Inc, South San Francisco, California, Knopp Biosciences, Pittsburgh, Pennsylvania, Barrow Neurological Institute, The University of Arizona, Phoenix
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2Academic Journal
المؤلفون: Rudnicki, Stacy A, Andrews, Jinsy A, Duong, Tina, Cockroft, Bettina M, Malik, Fady I, Meng, Lisa, Wei, Jenny, Wolff, Andrew A, Genge, Angela, Johnson, Nicholas E, Tesi-Rocha, Carolina, Connolly, Anne M, Darras, Basil T, Felice, Kevin, Finkel, Richard S, Shieh, Perry B, Mah, Jean K, Statland, Jeffrey, Campbell, Craig, Habib, Ali A, Kuntz, Nancy L, Oskoui, Maryam, Day, John W
المصدر: Neurotherapeutics : the journal of the American Society for Experimental NeuroTherapeutics. 18(2)
مصطلحات موضوعية: Muscle, Skeletal, Humans, Muscular Atrophy, Spinal, Pyridines, Pyrimidines, Pyrroles, Troponin I, Drugs, Investigational, Cohort Studies, Double-Blind Method, Adolescent, Adult, Aged, Middle Aged, Child, Female, Male, Young Adult, Walk Test, Reldesemtiv, pharmacodynamics, pharmacokinetics, six-minute walk test, spinal muscular atrophy clinical trial, Rare Diseases, Clinical Trials and Supportive Activities, Clinical Research, 6.1 Pharmaceuticals, Evaluation of treatments and therapeutic interventions, Neurosciences, Pharmacology and Pharmaceutical Sciences, Public Health and Health Services, Neurology & Neurosurgery
وصف الملف: application/pdf
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3Academic Journal
المؤلفون: Simkins, Tyrell J., Kupfer, Stuart, Malik, Fady I., Meng, Lisa, Rudnicki, Stacy A., Wei, Jenny, Shefner, Jeremy M., Bowser, Robert
المصدر: Amyotrophic Lateral Sclerosis & Frontotemporal Degeneration; Feb2025, Vol. 26 Issue 1/2, p103-112, 10p
مصطلحات موضوعية: AMYOTROPHIC lateral sclerosis, PEARSON correlation (Statistics), VITAL capacity (Respiration), CYTOPLASMIC filaments, DISEASE progression
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4Academic Journal
المؤلفون: Shefner, Jeremy M, Al-Chalabi, Ammar, Andrews, Jinsy A, Chio, Adriano, De Carvalho, Mamede, Cockroft, Bettina M, Corcia, Philippe, Couratier, Philippe, Cudkowicz, Merit E, Genge, Angela, Hardiman, Orla, Heiman-Patterson, Terry, Henderson, Robert D, Ingre, Caroline, Jackson, Carlayne E, Johnston, Wendy, Lechtzin, Noah, Ludolph, Albert, Maragakis, Nicholas J, Miller, Timothy M, Mora Pardina, Jesus S, Petri, Susanne, Simmons, Zachary, Van Den Berg, Leonard H, Zinman, Lorne, Kupfer, Stuart, Malik, Fady I, Meng, Lisa, Simkins, Tyrell J, Wei, Jenny, Wolff, Andrew A, Rudnicki, Stacy A
المساهمون: Neurologen, Projectafdeling ALS, Brain, Regenerative Medicine and Stem Cells
مصطلحات موضوعية: ALSFRS-R, Amyotrophic lateral sclerosis, randomized clinical trial, reldesemtiv, Clinical Neurology, Neurology, Journal Article
وصف الملف: application/pdf
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5Academic Journal
المؤلفون: Shefner, Jeremy M., Al-Chalabi, Ammar, Andrews, Jinsy A., Chio, Adriano, De Carvalho, Mamede, Cockroft, Bettina M., Corcia, Philippe, Couratier, Philippe, Cudkowicz, Merit E., Genge, Angela, Hardiman, Orla, Heiman-Patterson, Terry, Henderson, Robert D., Ingre, Caroline, Jackson, Carlayne E., Johnston, Wendy, Lechtzin, Noah, Ludolph, Albert, Maragakis, Nicholas J., Miller, Timothy M., Mora Pardina, Jesus S., Petri, Susanne, Simmons, Zachary, Van Den Berg, Leonard H., Zinman, Lorne, Kupfer, Stuart, Malik, Fady I., Meng, Lisa, Simkins, Tyrell J., Wei, Jenny, Wolff, Andrew A., Rudnicki, Stacy A.
المساهمون: Cytokinetics
المصدر: Amyotrophic Lateral Sclerosis and Frontotemporal Degeneration ; volume 24, issue 5-6, page 523-534 ; ISSN 2167-8421 2167-9223
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6Academic Journal
المؤلفون: Gebrehiwet, Paulos, Brekke, Johan, Rudnicki, Stacy A., Mellor, Jennifer, Wright, Jack, Earl, Lucy, Ball, Nathan, Iqbal, Halima, Thomas, Owen, Castellano, Giorgio
المصدر: Amyotrophic Lateral Sclerosis and Frontotemporal Degeneration ; volume 25, issue 3-4, page 345-357 ; ISSN 2167-8421 2167-9223
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7Academic Journal
المؤلفون: Gebrehiwet, Paulos, Meng, Lisa, Rudnicki, Stacy A., Sarocco, Phil, Wei, Jenny, Wolff, Andrew A., Butzner, Michael, Chiò, Adriano, Andrews, Jinsy A., Genge, Angela, Hughes, Dyfrig A., Jackson, Carlayne E., Lechtzin, Noah, Miller, Timothy M., Shefner, Jeremy M.
المساهمون: Cytokinetics
المصدر: Journal of Medical Economics ; volume 26, issue 1, page 488-493 ; ISSN 1369-6998 1941-837X
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8Academic Journal
المؤلفون: Gebrehiwet, Paulos, Meng, Lisa, Rudnicki, Stacy A., Sarocco, Phil, Wei, Jenny, Wolff, Andrew A., Chiò, Adriano, Andrews, Jinsy A., Genge, Angela, Jackson, Carlayne E., Lechtzin, Noah, Miller, Timothy M., Shefner, Jeremy M.
المساهمون: Cytokinetics, Astellas Pharma Inc
المصدر: Amyotrophic Lateral Sclerosis and Frontotemporal Degeneration ; volume 24, issue 3-4, page 304-310 ; ISSN 2167-8421 2167-9223
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9Academic Journal
المؤلفون: Rudnicki, Stacy A., Andrews, Jinsy A., Bian, Amy, Cockroft, Bettina M., Cudkowicz, Merit E., Hardiman, Orla, Malik, Fady I., Meng, Lisa, Wolff, Andrew A., Shefner, Jeremy M.
المساهمون: Cytokinetics, Incorporated, Error! Hyperlink reference not valid.
المصدر: Amyotrophic Lateral Sclerosis and Frontotemporal Degeneration ; volume 22, issue 7-8, page 486-494 ; ISSN 2167-8421 2167-9223
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10Academic Journal
المؤلفون: Rudnicki, Stacy A., Andrews, Jinsy A., Genge, Angela, Jackson, Carlayne, Lechtzin, Noah, Miller, Timothy M., Cockroft, Bettina M., Malik, Fady I., Meng, Lisa, Wei, Jenny, Wolff, Andrew A., Shefner, Jeremy M.
المساهمون: Astellas Pharma Inc., Cytokinetics, Incorporated, Astellas Pharma Inc
المصدر: Amyotrophic Lateral Sclerosis and Frontotemporal Degeneration ; volume 23, issue 3-4, page 263-270 ; ISSN 2167-8421 2167-9223
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11Academic Journal
المؤلفون: Rudnicki, Stacy A.
المصدر: Amyotrophic Lateral Sclerosis and Frontotemporal Degeneration ; volume 22, issue sup1, page 2-4 ; ISSN 2167-8421 2167-9223
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12Academic Journal
المؤلفون: Rudnicki, Stacy A., Andrews, Jinsy A., Duong, Tina, Cockroft, Bettina M., Malik, Fady I., Meng, Lisa, Wei, Jenny, Wolff, Andrew A., Genge, Angela, Johnson, Nicholas E., Tesi-Rocha, Carolina, Connolly, Anne M., Darras, Basil T., Felice, Kevin, Finkel, Richard S., Shieh, Perry B., Mah, Jean K., Statland, Jeffrey, Campbell, Craig, Habib, Ali A., Kuntz, Nancy L., Oskoui, Maryam, Day, John W.
المصدر: Neurotherapeutics ; volume 18, issue 3, page 2130 ; ISSN 1878-7479
الاتاحة: https://doi.org/10.1007/s13311-021-01120-8
https://link.springer.com/content/pdf/10.1007/s13311-021-01120-8.pdf
https://link.springer.com/article/10.1007/s13311-021-01120-8/fulltext.html
https://api.elsevier.com/content/article/PII:S1878747923007973?httpAccept=text/xml
https://api.elsevier.com/content/article/PII:S1878747923007973?httpAccept=text/plain -
13Academic Journal
المؤلفون: Gebrehiwet, Paulos, Brekke, Johan, Rudnicki, Stacy A., Mellor, Jennifer, Wright, Jack, Earl, Lucy, Ball, Nathan, Iqbal, Halima, Thomas, Owen, Castellano, Giorgio
المصدر: Amyotrophic Lateral Sclerosis & Frontotemporal Degeneration; May2024, Vol. 25 Issue 3/4, p345-357, 13p
مصطلحات موضوعية: AMYOTROPHIC lateral sclerosis, DATA analysis, BODY mass index, SYMPTOMS, EMPLOYMENT changes
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14Electronic Resource
المؤلفون: Neurologen, Projectafdeling ALS, Brain, Regenerative Medicine and Stem Cells, Shefner, Jeremy M, Al-Chalabi, Ammar, Andrews, Jinsy A, Chio, Adriano, De Carvalho, Mamede, Cockroft, Bettina M, Corcia, Philippe, Couratier, Philippe, Cudkowicz, Merit E, Genge, Angela, Hardiman, Orla, Heiman-Patterson, Terry, Henderson, Robert D, Ingre, Caroline, Jackson, Carlayne E, Johnston, Wendy, Lechtzin, Noah, Ludolph, Albert, Maragakis, Nicholas J, Miller, Timothy M, Mora Pardina, Jesus S, Petri, Susanne, Simmons, Zachary, Van Den Berg, Leonard H, Zinman, Lorne, Kupfer, Stuart, Malik, Fady I, Meng, Lisa, Simkins, Tyrell J, Wei, Jenny, Wolff, Andrew A, Rudnicki, Stacy A
URL:
https://doi.org/10.1080/21678421.2023.2216223 http://hdl.handle.net/1874/449379 http://www.scopus.com/inward/record.url?scp=85161386139&partnerID=8YFLogxK
2167-8421
Amyotrophic Lateral Sclerosis & Frontotemporal Degeneration
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15Academic Journal
المؤلفون: Shefner, Jeremy M., Jacobsen, Bill, Kupfer, Stuart, Malik, Fady I., Meng, Lisa, Wei, Jenny, Wolff, Andrew A, Rudnicki, Stacy A.
المصدر: Amyotrophic Lateral Sclerosis & Frontotemporal Degeneration; Feb2024, Vol. 25 Issue 1/2, p162-169, 8p
مصطلحات موضوعية: AMYOTROPHIC lateral sclerosis, FUNCTIONAL status, GRIP strength, MUSCLE strength, VITAL capacity (Respiration)
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16Academic Journal
المؤلفون: Shefner, Jeremy M., Camu, William, Cudkowicz, Merit E., Hardiman, Orla, Cockroft, Bettina M., Lee, Jacqueline H., Malik, Fady I., Meng, Lisa, Rudnicki, Stacy A., Wolff, Andrew A., Andrews, Jinsy A.
المساهمون: Centre Hospitalier Régional Universitaire Montpellier (CHRU Montpellier), Trinity College Dublin
المصدر: ISSN: 2167-8421 ; Amyotrophic Lateral Sclerosis and Frontotemporal Degeneration ; https://hal.umontpellier.fr/hal-02862303 ; Amyotrophic Lateral Sclerosis and Frontotemporal Degeneration, Taylor & Francis, 2019, 20 (7-8), pp.584-594. ⟨10.1080/21678421.2019.1612922⟩.
مصطلحات موضوعية: Randomized clinical trial, amyotrophic lateral sclerosis, tirasemtiv, [SDV]Life Sciences [q-bio], [SDV.NEU.NB]Life Sciences [q-bio]/Neurons and Cognition [q-bio.NC]/Neurobiology, [SDV.SP.PHARMA]Life Sciences [q-bio]/Pharmaceutical sciences/Pharmacology
Relation: hal-02862303; https://hal.umontpellier.fr/hal-02862303; https://hal.umontpellier.fr/hal-02862303/document; https://hal.umontpellier.fr/hal-02862303/file/A%20phase%20III%20trial%20of%20tirasemtiv%20as%20a%20potential%20treatment%20for%20amyotrophic%20lateral%20sclerosis.pdf
الاتاحة: https://hal.umontpellier.fr/hal-02862303
https://hal.umontpellier.fr/hal-02862303/document
https://hal.umontpellier.fr/hal-02862303/file/A%20phase%20III%20trial%20of%20tirasemtiv%20as%20a%20potential%20treatment%20for%20amyotrophic%20lateral%20sclerosis.pdf
https://doi.org/10.1080/21678421.2019.1612922 -
17Academic Journal
المؤلفون: Gebrehiwet, Paulos, Meng, Lisa, Rudnicki, Stacy A., Sarocco, Phil, Wei, Jenny, Wolff, Andrew A., Chiò, Adriano, Andrews, Jinsy A., Genge, Angela, Jackson, Carlayne E., Lechtzin, Noah, Miller, Timothy M., Shefner, Jeremy M.
المصدر: Amyotrophic Lateral Sclerosis & Frontotemporal Degeneration; May2023, Vol. 24 Issue 3/4, p304-310, 7p
مصطلحات موضوعية: AMYOTROPHIC lateral sclerosis, RETROSPECTIVE studies
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18
المؤلفون: Rudnicki, Stacy A., Andrews, Jinsy A., Duong, Tina, Cockroft, Bettina M., Malik, Fady I., Meng, Lisa, Wei, Jenny, Wolff, Andrew A., Adelantado, Angela, Damm, Peter, Mathiesen, Elizabeth Reinhardt, Jensen, Dorte Moeller, Anderson, Lise Lotte T., Lapolla, Annunziata, Dalfrà, Maria G., Bertolotto, Alessandra, Wender-Ozegowska, Ewa, Zawiejska, Agnieszka, Hill, David J., Snoek, Frank J.
المصدر: Paediatrics Publications
وصف الملف: application/pdf
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19Academic Journal
المؤلفون: Shefner, Jeremy M., Andrews, Jinsy A., Genge, Angela, Jackson, Carlayne, Lechtzin, Noah, Miller, Timothy M., Cockroft, Bettina M., Meng, Lisa, Wei, Jenny, Wolff, Andrew A., Malik, Fady I., Bodkin, Cynthia, Brooks, Benjamin R., Caress, James, Dionne, Annie, Fee, Dominic, Goutman, Stephen A., Goyal, Namita A., Hardiman, Orla, Hayat, Ghazala, Heiman-Patterson, Terry, Heitzman, Daragh, Henderson, Robert D., Johnston, Wendy, Karam, Chafic, Kiernan, Matthew C., Kolb, Stephen J., Korngut, Lawrence, Ladha, Shafeeq, Matte, Genevieve, Mora, Jesus S., Needham, Merrilee, Oskarsson, Bjorn, Pattee, Gary L., Pioro, Erik P., Pulley, Michael, Quan, Dianna, Rezania, Kourosh, Schellenberg, Kerri L., Schultz, David, Shoesmith, Christen, Simmons, Zachary, Statland, Jeffrey, Sultan, Shumaila, Swenson, Andrea, Van Den Berg, Leonard H., Vu, Tuan, Vucic, Steve, Weiss, Michael, Whyte-Rayson, Ashley, Wymer, James, Zinman, Lorne, Rudnicki, Stacy A.
المساهمون: Neurology, School of Medicine
المصدر: PMC
مصطلحات موضوعية: Amyotrophic lateral sclerosis, Randomized clinical trial, Reldesemtiv
وصف الملف: application/pdf
Relation: Amyotrophic Lateral Sclerosis and Frontotemporal Degeneration; Shefner JM, Andrews JA, Genge A, et al. A Phase 2, Double-Blind, Randomized, Dose-Ranging Trial Of Reldesemtiv In Patients With ALS. Amyotroph Lateral Scler Frontotemporal Degener. 2021;22(3-4):287-299. doi:10.1080/21678421.2020.1822410; https://hdl.handle.net/1805/30538
الاتاحة: https://hdl.handle.net/1805/30538
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20Academic Journal
المؤلفون: Bozik, Michael E., Mitsumoto, Hiroshi, Brooks, Benjamin R., Rudnicki, Stacy A., Moore, Dan H., Zhang, Bing, Ludolph, Albert, Cudkowicz, Merit E., van den Berg, Leonard H., Mather, James, Petzinger, Thomas, Archibald, Donald
المصدر: Amyotrophic Lateral Sclerosis and Frontotemporal Degeneration ; volume 15, issue 5-6, page 406-413 ; ISSN 2167-8421 2167-9223