-
1Academic Journal
المؤلفون: Laurent Servais, Paul Strijbos, Margaux Poleur, Andrada Mirea, Nina Butoianu, Valeria A. Sansone, Carole Vuillerot, Ulrike Schara-Schmidt, Mariacristina Scoto, Andreea M. Seferian, Stefano C. Previtali, Már Tulinius, Andrés Nascimento, Pat Furlong, Teji Singh, Roxana Donisa Dreghici, Nathalie Goemans, Eugenio Mercuri, Volker Straub, Maitea Guridi Ormazabal, Jessica Braid, Francesco Muntoni, Alexis Tricot, Mélanie Annoussamy, Damien Eggenspieler
المصدر: Scientific Reports, Vol 14, Iss 1, Pp 1-12 (2024)
مصطلحات موضوعية: Stride Velocity 95th Centile, Digital endpoints, Wearables, Duchenne muscular dystrophy, Regulatory qualification, V3 framework, Medicine, Science
وصف الملف: electronic resource
Relation: https://doaj.org/toc/2045-2322
-
2
المؤلفون: Jessica F, Boehler, Kristy J, Brown, Margaret, Beatka, J Patrick, Gonzalez, Roxana, Donisa Dreghici, Meghan, Soustek-Kramer, Sharon, McGonigle, Annie, Ganot, Timothy, Palmer, Caitlin, Lowie, Jeffrey S, Chamberlain, Michael W, Lawlor, Carl A, Morris
المصدر: Neuromuscular Disorders. 33:40-49
مصطلحات موضوعية: Neurology, Pediatrics, Perinatology and Child Health, Neurology (clinical), Genetics (clinical)
-
3
المؤلفون: Carl A. Morris, Roxana Donisa Dreghici, J. Patrick Gonzalez
المصدر: Cell and Gene Therapy Insights. :129-140
مصطلحات موضوعية: General Economics, Econometrics and Finance