المؤلفون: Caroline Le Guiner, Xiao Xiao, Thibaut Larcher, Aude Lafoux, Corinne Huchet, Gilles Toumaniantz, Oumeya Adjali, Ignacio Anegon, Séverine Remy, Josh Grieger, Juan Li, Vahid Farrokhi, Hendrik Neubert, Jane Owens, Maritza McIntyre, Philippe Moullier, R. Jude Samulski

المصدر: Molecular Therapy: Methods & Clinical Development, Vol 30, Iss , Pp 30-47 (2023)

مصطلحات موضوعية: Duchenne muscular dystrophy, gene therapy, recombinant adeno-associated virus, mini-dystrophin, DMDmdx rat, dose study, Genetics, QH426-470, Cytology, QH573-671

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050123000797; https://doaj.org/toc/2329-0501

URL الوصول: https://doaj.org/article/7a89e1515ecf4452944c4318d3851f25

المؤلفون: Mathieu Mével, Virginie Pichard, Mohammed Bouzelha, Dimitri Alvarez-Dorta, Pierre-Alban Lalys, Nathalie Provost, Marine Allais, Alexandra Mendes, Elodie Landagaray, Jean-Baptiste Ducloyer, Estelle Toublanc, Anne Galy, Nicole Brument, Gaëlle M. Lefevre, Sébastien G. Gouin, Carolina Isiegas, Guylène Le Meur, Thérèse Cronin, Caroline Le Guiner, Michel Weber, Philippe Moullier, Eduard Ayuso, David Deniaud, Oumeya Adjali

المصدر: Molecular Therapy: Methods & Clinical Development, Vol 32, Iss 1, Pp 101187- (2024)

مصطلحات موضوعية: adeno-associated virus, chemistry, bioconjugation, gene therapy, retina, Genetics, QH426-470, Cytology, QH573-671

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050124000032; https://doaj.org/toc/2329-0501

URL الوصول: https://doaj.org/article/1edecadd12924319b147b4cab1a426f8

المؤلفون: Gwladys Gernoux, Mickaël Guilbaud, Marie Devaux, Malo Journou, Virginie Pichard, Nicolas Jaulin, Adrien Léger, Johanne Le Duff, Jack-Yves Deschamps, Caroline Le Guiner, Philippe Moullier, Yan Cherel, Oumeya Adjali

المصدر: Molecular Therapy: Methods & Clinical Development, Vol 20, Iss , Pp 660-674 (2021)

مصطلحات موضوعية: AAV, gene transfer, locoregional delivery, immune response, tolerance, regulatory T cell, Genetics, QH426-470, Cytology, QH573-671

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050121000188; https://doaj.org/toc/2329-0501

URL الوصول: https://doaj.org/article/38d74ee6093e4b7fa86f324ccc982a8e

المؤلفون: Karim Bey, Johan Deniaud, Laurence Dubreil, Béatrice Joussemet, Joseph Cristini, Carine Ciron, Juliette Hordeaux, Morwenn Le Boulc’h, Kevin Marche, Maud Maquigneau, Michaël Guilbaud, Rosalie Moreau, Thibaut Larcher, Jack-Yves Deschamps, Marion Fusellier, Véronique Blouin, Caroline Sevin, Nathalie Cartier, Oumeya Adjali, Patrick Aubourg, Philippe Moullier, Marie-Anne Colle

المصدر: Molecular Therapy: Methods & Clinical Development, Vol 17, Iss , Pp 771-784 (2020)

مصطلحات موضوعية: nonhuman primate, AAV, gene therapy, central nervous system, intra-CSF, intrathecal delivery, Genetics, QH426-470, Cytology, QH573-671

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050120300619; https://doaj.org/toc/2329-0501

URL الوصول: https://doaj.org/article/a0aedb1aca064422b991e72f09f1cc8d

المؤلفون: Achille François, Mohammed Bouzelha, Emilie Lecomte, Frédéric Broucque, Magalie Penaud-Budloo, Oumeya Adjali, Philippe Moullier, Véronique Blouin, Eduard Ayuso

المصدر: Molecular Therapy: Methods & Clinical Development, Vol 10, Iss , Pp 223-236 (2018)

مصطلحات موضوعية: Genetics, QH426-470, Cytology, QH573-671

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050118300676; https://doaj.org/toc/2329-0501

URL الوصول: https://doaj.org/article/e86bc233d9c34383bc042649c09abbea

المؤلفون: Claire Domenger, Marine Allais, Virginie François, Adrien Léger, Emilie Lecomte, Marie Montus, Laurent Servais, Thomas Voit, Philippe Moullier, Yann Audic, Caroline Le Guiner

المصدر: Molecular Therapy: Nucleic Acids, Vol 10, Iss , Pp 277-291 (2018)

مصطلحات موضوعية: exon skipping, off-target, RNA sequencing, Duchenne, U7snRNA, Therapeutics. Pharmacology, RM1-950

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2162253117303074; https://doaj.org/toc/2162-2531

URL الوصول: https://doaj.org/article/b56772ff2df9496ca4c2cf486504309a

المؤلفون: Caroline Le Guiner, Laurent Servais, Marie Montus, Thibaut Larcher, Bodvaël Fraysse, Sophie Moullec, Marine Allais, Virginie François, Maeva Dutilleul, Alberto Malerba, Taeyoung Koo, Jean-Laurent Thibaut, Béatrice Matot, Marie Devaux, Johanne Le Duff, Jack-Yves Deschamps, Inès Barthelemy, Stéphane Blot, Isabelle Testault, Karim Wahbi, Stéphane Ederhy, Samia Martin, Philippe Veron, Christophe Georger, Takis Athanasopoulos, Carole Masurier, Federico Mingozzi, Pierre Carlier, Bernard Gjata, Jean-Yves Hogrel, Oumeya Adjali, Fulvio Mavilio, Thomas Voit, Philippe Moullier, George Dickson

المصدر: Nature Communications, Vol 8, Iss 1, Pp 1-15 (2017)

مصطلحات موضوعية: Science

وصف الملف: electronic resource

Relation: https://doaj.org/toc/2041-1723

URL الوصول: https://doaj.org/article/d425f7f6bf364aa99c6850ae61ecdd6b

المؤلفون: Céline Vandamme, Rebecca Xicluna, Leslie Hesnard, Marie Devaux, Nicolas Jaulin, Mickaël Guilbaud, Johanne Le Duff, Célia Couzinié, Philippe Moullier, Xavier Saulquin, Oumeya Adjali

المصدر: Frontiers in Immunology, Vol 10 (2020)

مصطلحات موضوعية: AAV, gene therapy, immune response, CD8+ T lymphocytes, tetramer-associated magnetic enrichment, Immunologic diseases. Allergy, RC581-607

وصف الملف: electronic resource

Relation: https://www.frontiersin.org/article/10.3389/fimmu.2019.03110/full; https://doaj.org/toc/1664-3224

URL الوصول: https://doaj.org/article/21c2793766ba4036b7fafebbf31d8574

المؤلفون: Audrey Bourdon, Virginie François, Liwen Zhang, Aude Lafoux, Bodvael Fraysse, Gilles Toumaniantz, Thibaut Larcher, Tiphaine Girard, Mireille Ledevin, Cyrielle Lebreton, Agnès Hivonnait, Anna Creismeas, Marine Allais, Basile Marie, Justine Guguin, Véronique Blouin, Séverine Remy, Ignacio Anegon, Corinne Huchet, Alberto Malerba, Betty Kao, Anita Le Heron, Philippe Moullier, George Dickson, Linda Popplewell, Oumeya Adjali, Federica Montanaro, Caroline Le Guiner

المصدر: Gene Therapy. 29:520-535

مصطلحات موضوعية: Genetics, Molecular Medicine, Molecular Biology

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::3d9c1614fc49440d97af2761d82421d2
https://doi.org/10.1038/s41434-022-00317-6

المؤلفون: Mathieu Mével, Virginie Pichard, Mohammed Bouzelha, Dimitri Alvarez-Dorta, Pierre-Alban Lalys, Nathalie Provost, Marine Allais, Alexandra Mendes, Elodie Landagaray, Jean-Baptiste Ducloyer, Anne Galy, Nicole Brument, Gaëlle M. Lefevre, Sébastien G. Gouin, Carolina Isiegas, Guylène Le Meur, Thérèse Cronin, Caroline Le Guiner, Michel Weber, Philippe Moullier, Eduard Ayuso, David Deniaud, Oumeya Adjali

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_________::754177853388fd915b92c4ee4b3e16c7
https://doi.org/10.1101/2022.12.01.518481

المؤلفون: Iker Arriaga, Aitor Navarro, Amaia Etxabe, Cesar Trigueros, R. Jude Samulski, Philippe Moullier, Achille François, Nicola GA GA Abrescia

المصدر: Human Gene Therapy.

مصطلحات موضوعية: Capsid, Cryoelectron Microscopy, Virion, Genetics, Humans, Molecular Medicine, Capsid Proteins, Dependovirus, Serogroup, Molecular Biology, HeLa Cells

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::9a7193532118f808306e3dc1eeb6c2db
https://doi.org/10.1089/hum.2022.119

المؤلفون: Susan D'Costa, Veronique Blouin, Frederic Broucque, Magalie Penaud-Budloo, Achille Fçranois, Irene C Perez, Christine Le Bec, Philippe Moullier, Richard O Snyder, Eduard Ayuso

المصدر: Molecular Therapy: Methods & Clinical Development, Vol 3, Iss C (2016)

مصطلحات موضوعية: Genetics, QH426-470, Cytology, QH573-671

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050116301607; https://doaj.org/toc/2329-0501

URL الوصول: https://doaj.org/article/abdbfb21a81743f3b6a2cf91a09b3f39

المؤلفون: Emilie Lecomte, Benoît Tournaire, Benjamin Cogné, Jean-Baptiste Dupont, Pierre Lindenbaum, Mélanie Martin-Fontaine, Frédéric Broucque, Cécile Robin, Matthias Hebben, Otto-Wilhelm Merten, Véronique Blouin, Achille François, Richard Redon, Philippe Moullier, Adrien Léger

المصدر: Molecular Therapy: Nucleic Acids, Vol 4, Iss C (2015)

مصطلحات موضوعية: DNA contaminants, next generation sequencing, quality control, rAAV, Therapeutics. Pharmacology, RM1-950

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2162253116300452; https://doaj.org/toc/2162-2531

URL الوصول: https://doaj.org/article/741f46340a074fda945084019638521d

المؤلفون: Jean-Baptiste Dupont, Benoit Tournaire, Christophe Georger, Béatrice Marolleau, Laurence Jeanson-Leh, Mireille Ledevin, Pierre Lindenbaum, Emilie Lecomte, Benjamin Cogné, Laurence Dubreil, Thibaut Larcher, Bernard Gjata, Laetitia Van Wittenberghe, Caroline Le Guiner, Magalie Penaud-Budloo, Richard O Snyder, Philippe Moullier, Adrien Léger

المصدر: Molecular Therapy: Methods & Clinical Development, Vol 2, Iss , Pp - (2015)

مصطلحات موضوعية: Genetics, QH426-470, Cytology, QH573-671

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050116300225; https://doaj.org/toc/2329-0501

URL الوصول: https://doaj.org/article/846a902b7ddb4553bb393762ce9f0d6f

المؤلفون: Mickaël Guilbaud, Célia Couzinié, Gwladys Gernoux, Nicolas Jaulin, Johanne Le Duff, Marie Devaux, Alice Toromanoff, Philippe Moullier, Caroline Le Guiner, Céline Vandamme, Thibaut Larcher, Oumeya Adjali

المصدر: Human Gene Therapy. 30:802-813

مصطلحات موضوعية: Time Factors, Transgene, Genetic Vectors, Gene Expression, Genome, Viral, Biology, Antibodies, Viral, medicine.disease_cause, Virus, 03 medical and health sciences, Transactivation, 0302 clinical medicine, Immune system, Immunity, Gene expression, Genetics, medicine, Animals, Transgenes, Muscle, Skeletal, Molecular Biology, Adeno-associated virus, Research Articles, 030304 developmental biology, 0303 health sciences, Immunogenicity, Gene Transfer Techniques, Dependovirus, Virology, Macaca fascicularis, 030220 oncology & carcinogenesis, Cytokines, Molecular Medicine, Follow-Up Studies

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::f060ff6554ac6c488f069cf53a064b2a
https://doi.org/10.1089/hum.2018.234

المؤلفون: Mirja Hommel, Dimitri Alvarez-Dorta, Oumeya Adjali, Aurélien Leray, Eduard Ayuso, Gloria González-Aseguinolaza, Simon Pacouret, Mickaël Guilbaud, Mohammed Bouzelha, Philippe Moullier, Sébastien G. Gouin, Laurence Dubreil, Mathieu Mével, Véronique Blouin, Jean Philippe Combal, David Deniaud, Magalie Penaud-Budloo

المساهمون: INSERM, UMR 1089, Centre hospitalier universitaire de Nantes (CHU Nantes), Chimie Et Interdisciplinarité : Synthèse, Analyse, Modélisation (CEISAM), Université de Nantes - UFR des Sciences et des Techniques (UN UFR ST), Université de Nantes (UN)-Université de Nantes (UN)-Centre National de la Recherche Scientifique (CNRS)-Institut de Chimie du CNRS (INC), Physiopathologie Animale et bioThérapie du muscle et du système nerveux (PAnTher), Ecole Nationale Vétérinaire, Agroalimentaire et de l'alimentation Nantes-Atlantique (ONIRIS)-Institut National de Recherche pour l’Agriculture, l’Alimentation et l’Environnement (INRAE), Expertise en Anatomie Pathologique (APEX), Ecole Nationale Vétérinaire, Agroalimentaire et de l'alimentation Nantes-Atlantique (ONIRIS)-Institut National de Recherche pour l’Agriculture, l’Alimentation et l’Environnement (INRAE)-Ecole Nationale Vétérinaire, Agroalimentaire et de l'alimentation Nantes-Atlantique (ONIRIS)-Institut National de Recherche pour l’Agriculture, l’Alimentation et l’Environnement (INRAE), Vivet Therapeutics SAS, Universidad de Navarra [Pamplona] (UNAV), Université de Nantes (UN)-Université de Nantes (UN)-Institut de Chimie du CNRS (INC)-Centre National de la Recherche Scientifique (CNRS), École nationale vétérinaire, agroalimentaire et de l'alimentation Nantes-Atlantique (ONIRIS)-Institut National de Recherche pour l’Agriculture, l’Alimentation et l’Environnement (INRAE), École nationale vétérinaire, agroalimentaire et de l'alimentation Nantes-Atlantique (ONIRIS)-Institut National de Recherche pour l’Agriculture, l’Alimentation et l’Environnement (INRAE)-École nationale vétérinaire, agroalimentaire et de l'alimentation Nantes-Atlantique (ONIRIS)-Institut National de Recherche pour l’Agriculture, l’Alimentation et l’Environnement (INRAE), JAULIN, Nicolas

المصدر: Chemical Science
Chemical Science, The Royal Society of Chemistry, 2020, 11 (4), pp.1122-1131. ⟨10.1039/C9SC04189C⟩
Chemical Science, 2020, 11 (4), pp.1122-1131. ⟨10.1039/C9SC04189C⟩

مصطلحات موضوعية: 0303 health sciences, biology, Chemistry, [SDV]Life Sciences [q-bio], viruses, Asialoglycoprotein, General Chemistry, Gene delivery, medicine.disease_cause, Genome, Virus, 3. Good health, Cell biology, [SDV] Life Sciences [q-bio], 03 medical and health sciences, Transduction (genetics), 0302 clinical medicine, Capsid, 030220 oncology & carcinogenesis, medicine, biology.protein, Antibody, Adeno-associated virus, 030304 developmental biology

وصف الملف: application/pdf

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::87a9713574e18c368d03437b10a2f8f6
https://pubmed.ncbi.nlm.nih.gov/34084369

المؤلفون: Audrey, Bourdon, Virginie, François, Liwen, Zhang, Aude, Lafoux, Bodvael, Fraysse, Gilles, Toumaniantz, Thibaut, Larcher, Tiphaine, Girard, Mireille, Ledevin, Cyrielle, Lebreton, Agnès, Hivonnait, Anna, Creismeas, Marine, Allais, Basile, Marie, Justine, Guguin, Véronique, Blouin, Séverine, Remy, Ignacio, Anegon, Corinne, Huchet, Alberto, Malerba, Betty, Kao, Anita, Le Heron, Philippe, Moullier, George, Dickson, Linda, Popplewell, Oumeya, Adjali, Federica, Montanaro, Caroline, Le Guiner

المصدر: Gene therapy. 29(9)

مصطلحات موضوعية: Dystrophin, Muscular Dystrophy, Duchenne, Tandem Mass Spectrometry, Animals, Genetic Therapy, Muscle, Skeletal, Chromatography, Liquid, Dystrophin-Associated Protein Complex, Rats

URL الوصول: https://explore.openaire.eu/search/publication?articleId=pmid________::932d0ee578a32dab628daaac46e8bb2b
https://pubmed.ncbi.nlm.nih.gov/35449294

المؤلفون: Jerome Denard, Christine Jenny, Véronique Blouin, Philippe Moullier, Fedor Svinartchouk

المصدر: Molecular Therapy: Methods & Clinical Development, Vol 1, Iss C (2014)

مصطلحات موضوعية: Genetics, QH426-470, Cytology, QH573-671

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050116300985; https://doaj.org/toc/2329-0501

URL الوصول: https://doaj.org/article/571489f5df1c4a6fb1aa395317632f9e

المؤلفون: Aurélie Moreau, Céline Vandamme, Mercedes Segovia, Marie Devaux, Mickaël Guilbaud, Gaëlle Tilly, Nicolas Jaulin, Johanne Le Duff, Yan Cherel, Jack-Yves Deschamps, Ignacio Anegon, Philippe Moullier, Maria Cristina Cuturi, Oumeya Adjali

المصدر: Molecular Therapy: Methods & Clinical Development, Vol 1, Iss C (2014)

مصطلحات موضوعية: Genetics, QH426-470, Cytology, QH573-671

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050116300948; https://doaj.org/toc/2329-0501

URL الوصول: https://doaj.org/article/6a2fa6a406d94ab892a87a5739bb4b38

المؤلفون: Caroline Le Guiner, Knut Stieger, Alice Toromanoff, Mickaël Guilbaud, Alexandra Mendes-Madeira, Marie Devaux, Lydie Guigand, Yan Cherel, Philippe Moullier, Fabienne Rolling, Oumeya Adjali

المصدر: PLoS ONE, Vol 9, Iss 9, p e102538 (2014)

مصطلحات موضوعية: Medicine, Science

وصف الملف: electronic resource

Relation: http://europepmc.org/articles/PMC4172479?pdf=render; https://doaj.org/toc/1932-6203

URL الوصول: https://doaj.org/article/ffab1b8d1e2d44658e04053f53d319fa