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1Academic Journal
المؤلفون: Magalie Penaud-Budloo, Emilie Lecomte, Quentin Lecomte, Simon Pacouret, Frédéric Broucque, Aurélien Guy-Duché, Jean-Baptiste Dupont, Laurence Jeanson-Leh, Cécile Robin, Véronique Blouin, Eduard Ayuso, Oumeya Adjali
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 32, Iss 3, Pp 101305- (2024)
مصطلحات موضوعية: gene therapy, AAV vectors, bioproduction, quality control, residual nucleic acids, microRNA, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
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2Academic Journal
المؤلفون: Anais Defois, Nina Bon, Mathieu Mével, David Deniaud, Yves Maugars, Jérôme Guicheux, Oumeya Adjali, Claire Vinatier
المصدر: Journal of Cartilage & Joint Preservation, Vol 4, Iss 2, Pp 100186- (2024)
مصطلحات موضوعية: Adeno-associated virus, Capsid engineering, Gene therapy, Osteoarthritis, Transgene optimization, Diseases of the musculoskeletal system, RC925-935, Other systems of medicine, RZ201-999, Sports medicine, RC1200-1245
وصف الملف: electronic resource
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3Academic Journal
المؤلفون: Caroline Le Guiner, Xiao Xiao, Thibaut Larcher, Aude Lafoux, Corinne Huchet, Gilles Toumaniantz, Oumeya Adjali, Ignacio Anegon, Séverine Remy, Josh Grieger, Juan Li, Vahid Farrokhi, Hendrik Neubert, Jane Owens, Maritza McIntyre, Philippe Moullier, R. Jude Samulski
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 30, Iss , Pp 30-47 (2023)
مصطلحات موضوعية: Duchenne muscular dystrophy, gene therapy, recombinant adeno-associated virus, mini-dystrophin, DMDmdx rat, dose study, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
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4Academic Journal
المؤلفون: Mathieu Mével, Virginie Pichard, Mohammed Bouzelha, Dimitri Alvarez-Dorta, Pierre-Alban Lalys, Nathalie Provost, Marine Allais, Alexandra Mendes, Elodie Landagaray, Jean-Baptiste Ducloyer, Estelle Toublanc, Anne Galy, Nicole Brument, Gaëlle M. Lefevre, Sébastien G. Gouin, Carolina Isiegas, Guylène Le Meur, Thérèse Cronin, Caroline Le Guiner, Michel Weber, Philippe Moullier, Eduard Ayuso, David Deniaud, Oumeya Adjali
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 32, Iss 1, Pp 101187- (2024)
مصطلحات موضوعية: adeno-associated virus, chemistry, bioconjugation, gene therapy, retina, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
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5Academic Journal
المؤلفون: Jean-Baptiste Ducloyer, Virginie Pichard, Mathieu Mevel, Anne Galy, Gaelle M. Lefevre, Nicole Brument, Dimitri Alvarez-Dorta, David Deniaud, Alexandra Mendes-Madeira, Lyse Libeau, Caroline Le Guiner, Therese Cronin, Oumeya Adjali, Michel Weber, Guylène Le Meur
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 28, Iss , Pp 387-393 (2023)
مصطلحات موضوعية: gene therapy, eye surgery, subretinal injection, air tamponade, fluid-air exchange, intravitreal, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
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6Academic Journal
المؤلفون: Anna Creisméas, Claire Gazaille, Audrey Bourdon, Marc-Antoine Lallemand, Virginie François, Marine Allais, Mireille Ledevin, Thibaut Larcher, Gilles Toumaniantz, Aude Lafoux, Corinne Huchet, Ignacio Anegon, Oumeya Adjali, Caroline Le Guiner, Bodvaël Fraysse
المصدر: Journal of Translational Medicine, Vol 19, Iss 1, Pp 1-17 (2021)
مصطلحات موضوعية: DMD, Calcium, TRPC1, TRPC3, DMD mdx rat, Gene therapy, Medicine
وصف الملف: electronic resource
Relation: https://doaj.org/toc/1479-5876
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7Academic Journal
المؤلفون: Gwladys Gernoux, Mickaël Guilbaud, Marie Devaux, Malo Journou, Virginie Pichard, Nicolas Jaulin, Adrien Léger, Johanne Le Duff, Jack-Yves Deschamps, Caroline Le Guiner, Philippe Moullier, Yan Cherel, Oumeya Adjali
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 20, Iss , Pp 660-674 (2021)
مصطلحات موضوعية: AAV, gene transfer, locoregional delivery, immune response, tolerance, regulatory T cell, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
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8Academic Journal
المؤلفون: Denis Horgan, Andres Metspalu, Marie-Christine Ouillade, Dimitrios Athanasiou, John Pasi, Oumeya Adjali, Patrick Harrison, Cedric Hermans, Giovanni Codacci-Pisanelli, Jasmina Koeva, Thomas Szucs, Viorica Cursaru, Ivica Belina, Chiara Bernini, Suijie Zhuang, Stephen McMahon, Draga Toncheva, Thomas Thum
المصدر: Biomedicine Hub, Vol 5, Iss 3, Pp 1-23 (2020)
مصطلحات موضوعية: european union, gene therapy, gene transfer, personalised healthcare, personalised medicine, policy, quality of life, tissue engineering, vector design, virus, Medicine (General), R5-920
وصف الملف: electronic resource
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9Academic Journal
المؤلفون: Pauline F. Schmit, Simon Pacouret, Eric Zinn, Elizabeth Telford, Fotini Nicolaou, Frédéric Broucque, Eva Andres-Mateos, Ru Xiao, Magalie Penaud-Budloo, Mohammed Bouzelha, Nicolas Jaulin, Oumeya Adjali, Eduard Ayuso, Luk H. Vandenberghe
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 17, Iss , Pp 107-121 (2020)
مصطلحات موضوعية: capsid mosaics, adeno-associated virus, aav, library, cross-packaging, mosaic, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
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10Academic Journal
المؤلفون: Karim Bey, Johan Deniaud, Laurence Dubreil, Béatrice Joussemet, Joseph Cristini, Carine Ciron, Juliette Hordeaux, Morwenn Le Boulc’h, Kevin Marche, Maud Maquigneau, Michaël Guilbaud, Rosalie Moreau, Thibaut Larcher, Jack-Yves Deschamps, Marion Fusellier, Véronique Blouin, Caroline Sevin, Nathalie Cartier, Oumeya Adjali, Patrick Aubourg, Philippe Moullier, Marie-Anne Colle
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 17, Iss , Pp 771-784 (2020)
مصطلحات موضوعية: nonhuman primate, AAV, gene therapy, central nervous system, intra-CSF, intrathecal delivery, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
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11Academic Journal
المؤلفون: Achille François, Mohammed Bouzelha, Emilie Lecomte, Frédéric Broucque, Magalie Penaud-Budloo, Oumeya Adjali, Philippe Moullier, Véronique Blouin, Eduard Ayuso
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 10, Iss , Pp 223-236 (2018)
وصف الملف: electronic resource
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12Academic JournalLong-term microdystrophin gene therapy is effective in a canine model of Duchenne muscular dystrophy
المؤلفون: Caroline Le Guiner, Laurent Servais, Marie Montus, Thibaut Larcher, Bodvaël Fraysse, Sophie Moullec, Marine Allais, Virginie François, Maeva Dutilleul, Alberto Malerba, Taeyoung Koo, Jean-Laurent Thibaut, Béatrice Matot, Marie Devaux, Johanne Le Duff, Jack-Yves Deschamps, Inès Barthelemy, Stéphane Blot, Isabelle Testault, Karim Wahbi, Stéphane Ederhy, Samia Martin, Philippe Veron, Christophe Georger, Takis Athanasopoulos, Carole Masurier, Federico Mingozzi, Pierre Carlier, Bernard Gjata, Jean-Yves Hogrel, Oumeya Adjali, Fulvio Mavilio, Thomas Voit, Philippe Moullier, George Dickson
المصدر: Nature Communications, Vol 8, Iss 1, Pp 1-15 (2017)
مصطلحات موضوعية: Science
وصف الملف: electronic resource
Relation: https://doaj.org/toc/2041-1723
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13Academic Journal
المؤلفون: Céline Vandamme, Rebecca Xicluna, Leslie Hesnard, Marie Devaux, Nicolas Jaulin, Mickaël Guilbaud, Johanne Le Duff, Célia Couzinié, Philippe Moullier, Xavier Saulquin, Oumeya Adjali
المصدر: Frontiers in Immunology, Vol 10 (2020)
مصطلحات موضوعية: AAV, gene therapy, immune response, CD8+ T lymphocytes, tetramer-associated magnetic enrichment, Immunologic diseases. Allergy, RC581-607
وصف الملف: electronic resource
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14Academic Journal
المؤلفون: Judith Lorant, Thibaut Larcher, Nicolas Jaulin, Benoît Hedan, Aurélie Lardenois, Isabelle Leroux, Laurence Dubreil, Mireille Ledevin, Hélicia Goubin, Sophie Moullec, Jack-Yves Deschamps, Chantal Thorin, Catherine André, Oumeya Adjali, Karl Rouger
المصدر: Cell Transplantation, Vol 27 (2018)
مصطلحات موضوعية: Medicine
وصف الملف: electronic resource
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15Academic Journal
المؤلفون: Aurélie Moreau, Céline Vandamme, Mercedes Segovia, Marie Devaux, Mickaël Guilbaud, Gaëlle Tilly, Nicolas Jaulin, Johanne Le Duff, Yan Cherel, Jack-Yves Deschamps, Ignacio Anegon, Philippe Moullier, Maria Cristina Cuturi, Oumeya Adjali
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 1, Iss C (2014)
وصف الملف: electronic resource
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16Academic Journal
المؤلفون: Caroline Le Guiner, Knut Stieger, Alice Toromanoff, Mickaël Guilbaud, Alexandra Mendes-Madeira, Marie Devaux, Lydie Guigand, Yan Cherel, Philippe Moullier, Fabienne Rolling, Oumeya Adjali
المصدر: PLoS ONE, Vol 9, Iss 9, p e102538 (2014)
وصف الملف: electronic resource
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17Academic Journal
المؤلفون: Aurélien Leray, Pierre-Alban Lalys, Juliette Varin, Mohammed Bouzelha, Audrey Bourdon, Dimitri Alvarez-Dorta, Karine Pavageau, Sébastien Depienne, Maia Marchand, Anthony Mellet, Joanna Demilly, Jean-Baptiste Ducloyer, Tiphaine Girard, Bodvaël Fraysse, Mireille Ledevin, Mickaël Guilbaud, Sébastien G. Gouin, Eduard Ayuso, Oumeya Adjali, Thibaut Larcher, Thérèse Cronin, Caroline Le Guiner, David Deniaud, Mathieu Mével
المصدر: Biomedicine & Pharmacotherapy, Vol 171, Iss , Pp 116148- (2024)
مصطلحات موضوعية: Adeno-associated virus, Bioconjugation, Tyrosine, Targeting, Liver, Retina, Therapeutics. Pharmacology, RM1-950
Relation: http://www.sciencedirect.com/science/article/pii/S0753332224000295; https://doaj.org/toc/0753-3322; https://doaj.org/article/1ed978775aad41fbbbc3787da57c93b5
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18Academic Journal
المؤلفون: Samer Masri, Laure Carré, Nicolas Jaulin, Céline Vandamme, Célia Couzinié, Aurélien Guy-Duché, Jean-Baptiste Dupont, Allwyn Pereira, Eric Charpentier, Laurent David, Gwladys Gernoux, Mickaël Guilbaud, Oumeya Adjali
المصدر: International Journal of Molecular Sciences, Vol 24, Iss 13, p 10447 (2023)
مصطلحات موضوعية: cell–virus interaction, AAV, innate immunity, gene therapy, human-monocyte-derived dendritic cells, transcriptomic analysis, Biology (General), QH301-705.5, Chemistry, QD1-999
Relation: https://www.mdpi.com/1422-0067/24/13/10447; https://doaj.org/toc/1661-6596; https://doaj.org/toc/1422-0067; https://doaj.org/article/fe3eaffab875485da755793c0229386f
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19Academic Journal
المؤلفون: Juliette Varin, Clément Morival, Noémien Maillard, Oumeya Adjali, Therese Cronin
المصدر: International Journal of Molecular Sciences; Volume 22; Issue 23; Pages: 12818
مصطلحات موضوعية: immunogenicity, inflammation, gene therapy, AAV
جغرافية الموضوع: agris
وصف الملف: application/pdf
Relation: Molecular Pathology, Diagnostics, and Therapeutics; https://dx.doi.org/10.3390/ijms222312818
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20
المؤلفون: Sylvie Saleun, Caroline Mas, Aline Le Roy, Magalie Penaud-Budloo, Oumeya Adjali, Véronique Blouin, Christine Ebel
المساهمون: Laboratoire de Thérapie Génique Translationnelle des Maladies Génétiques / Translational Research in Gene Therapy - UMR_S 1089 (TARGET), Institut National de la Santé et de la Recherche Médicale (INSERM)-Nantes Université - UFR de Médecine et des Techniques Médicales (Nantes Univ - UFR MEDECINE), Nantes Université - pôle Santé, Nantes Université (Nantes Univ)-Nantes Université (Nantes Univ)-Nantes Université - pôle Santé, Nantes Université (Nantes Univ)-Nantes Université (Nantes Univ), Institut de biologie structurale (IBS - UMR 5075), Centre National de la Recherche Scientifique (CNRS)-Institut de Recherche Interdisciplinaire de Grenoble (IRIG), Direction de Recherche Fondamentale (CEA) (DRF (CEA)), Commissariat à l'énergie atomique et aux énergies alternatives (CEA)-Commissariat à l'énergie atomique et aux énergies alternatives (CEA)-Direction de Recherche Fondamentale (CEA) (DRF (CEA)), Commissariat à l'énergie atomique et aux énergies alternatives (CEA)-Commissariat à l'énergie atomique et aux énergies alternatives (CEA)-Université Grenoble Alpes (UGA)
المصدر: European Biophysics Journal
European Biophysics Journal, 2023, ⟨10.1007/s00249-023-01650-3⟩مصطلحات موضوعية: AAV vector, AUC, Adeno-associated virus, [SDV]Life Sciences [q-bio], Sedimentation velocity, Analytical ultracentrifugation, Biophysics, Quality control, General Medicine