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1Dissertation/ Thesis
المؤلفون: Ollington, Bethany
المساهمون: Murdoch, Craig, Colley, Helen
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2Academic JournalEffective AAV-mediated gene replacement therapy in retinal organoids modelling AIPL1-associated LCA4
المؤلفون: Sai, Hali, Ollington, Bethany, Rezek, Farah O, Chai, Niuzheng, Lane, Amelia, Georgiadis, Tassos, Bainbridge, James, Michaelides, Michel, Sacristan-Reviriego, Almudena, Perdigão, Pedro RL, Leung, Amy, van der Spuy, Jacqueline
المصدر: Molecular Therapy - Nucleic Acids , 35 (1) , Article 102148. (2024)
مصطلحات موضوعية: MT: Delivery strategies, Leber congenital amaurosis, retinal organoid, aryl hydrocarbon receptor, interacting protein-like 1adeno-associated virus, inherited retinal degeneration, gene therapy, induced pluripotent stem cells
وصف الملف: application/pdf
Relation: https://discovery.ucl.ac.uk/id/eprint/10188446/1/OMTN102148_proof.pdf; https://discovery.ucl.ac.uk/id/eprint/10188446/
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3Academic Journal
المؤلفون: Perdigão, Pedro RL, Ollington, Bethany, Sai, Hali, Leung, Amy, Sacristan-Reviriego, Almudena, van der Spuy, Jacqueline
المصدر: International Journal of Molecular Sciences , 24 (6) , Article 5912. (2023)
مصطلحات موضوعية: AIPL1, CRISPR/Cas9 gene editing, Leber congenital amaurosis, inherited retinal dystrophy, retinal organoid, Child, Preschool, Humans, Carrier Proteins, Adaptor Proteins, Signal Transducing, CRISPR-Cas Systems, Cell Line, Organoids, Eye Proteins
وصف الملف: text
Relation: https://discovery.ucl.ac.uk/id/eprint/10168444/1/van%20der%20Spuy_ijms-24-05912.pdf; https://discovery.ucl.ac.uk/id/eprint/10168444/
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4Academic JournalElectrospun patch delivery of anti-TNFα F(ab) for the treatment of inflammatory oral mucosal disease
المؤلفون: Edmans, Jake G., Ollington, Bethany, Colley, Helen E., Santocildes-Romero, Martin E., Siim Madsen, Lars, Hatton, Paul V., Spain, Sebastian G., Murdoch, Craig
المصدر: Journal of Controlled Release ; volume 350, page 146-157 ; ISSN 0168-3659
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5Academic Journal
المؤلفون: Ollington, Bethany, Colley, Helen E., Murdoch, Craig
المصدر: Tissue Engineering Part C: Methods ; volume 27, issue 8, page 462-471 ; ISSN 1937-3384 1937-3392
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6Academic Journal
المؤلفون: Al-Sahaf, Sarmad, Hendawi, Naeima B., Ollington, Bethany, Bolt, Robert, Ottewell, Penelope D., Hunter, Keith D., Murdoch, Craig
المساهمون: Medical Research Council
المصدر: Frontiers in Oral Health ; volume 2 ; ISSN 2673-4842