-
1Academic Journal
المؤلفون: Majhail, Navneet S., Miller, Beckley, Dean, Rebecca, Manghani, Rocio, Shin, Heayoung, Sivaraman, Smitha, Maziarz, Richard T.
المصدر: Transplantation and Cellular Therapy ; volume 29, issue 12, page 749.e1-749.e5 ; ISSN 2666-6367
-
2Academic Journal
المؤلفون: Bean, Karen, Jones, Simon A., Chakrapani, Anupam, Vijay, Suresh, Wu, Teresa, Church, Heather, Chanson, Charlotte, Olaye, Andrew, Miller, Beckley, Jensen, Ivar, Pang, Francis
المصدر: International Journal of Neonatal Screening (IJNS); Sep2024, Vol. 10 Issue 3, p45, 21p
-
3Academic Journal
المؤلفون: Majhail, Navneet S., Miller, Beckley, Dean, Rebecca, Manghani, Rocio, Galamidi-Cohen, Einat, Sivaraman, Smitha, Maziarz, Richard T
المصدر: Transplantation and Cellular Therapy ; volume 28, issue 3, page S326 ; ISSN 2666-6367
-
4Academic Journal
المؤلفون: Pang, Francis, Dean, Rebecca, Jensen, Ivar, Bean, Karen, Fields, Christopher, Miller, Beckley
المصدر: Molecular Genetics and Metabolism ; volume 138, issue 2, page 107258 ; ISSN 1096-7192
-
5Academic Journal
المؤلفون: Dean, Rebecca, Jensen, Ivar, Cyr, Phil, Miller, Beckley, Maru, Benit, Sproule, Douglas M., Feltner, Douglas E., Wiesner, Thomas, Malone, Daniel C., Bischof, Matthias, Toro, Walter, Dabbous, Omar
المصدر: Journal of Market Access & Health Policy; Dec 2021, Vol. 9 Issue 1, p1-12, 12p
مصطلحات موضوعية: SPINAL muscular atrophy, QUALITY-adjusted life years, COST effectiveness, DIRECT costing, GENE therapy
-
6Academic Journal
المؤلفون: Malone, Daniel C., Dean, Rebecca, Arjunji, Ramesh, Jensen, Ivar, Cyr, Phil, Miller, Beckley, Maru, Benit, Sproule, Douglas M., Feltner, Douglas E., Dabbous, Omar
المصدر: Journal of Market Access & Health Policy; Dec2019, Vol. 7 Issue 1, p1-4, 4p
مصطلحات موضوعية: SPINAL muscular atrophy, MARKOV processes, NATURAL history, COST effectiveness, GENETIC disorders
مصطلحات جغرافية: UNITED States
-
7Periodical
المؤلفون: Majhail, Navneet S., Miller, Beckley, Dean, Rebecca, Manghani, Rocio, Sivaraman, Smitha, Galamidi-Cohen, Einat, Maziarz, Richard T.
المصدر: Blood; November 2021, Vol. 138 Issue: 1, Number 1 Supplement 1 p4036-4036, 1p