المؤلفون: Scott A. Peslak, Selami Demirci, Vemika Chandra, Byoung Ryu, Saurabh K. Bhardwaj, Jing Jiang, Jeremy W. Rupon, Robert E. Throm, Naoya Uchida, Alexis Leonard, Khaled Essawi, Aylin C. Bonifacino, Allen E. Krouse, Nathaniel S. Linde, Robert E. Donahue, Francesca Ferrara, Matthew Wielgosz, Osheiza Abdulmalik, Nicole Hamagami, Paula Germino-Watnick, Anh Le, Rebecca Chu, Malikiya Hinds, Mitchell J. Weiss, Wei Tong, John F. Tisdale, Gerd A. Blobel

المصدر: Molecular Therapy: Nucleic Acids, Vol 31, Iss , Pp 452-465 (2023)

مصطلحات موضوعية: MT: Oligonucleotides, Therapies and Applications, enhancer-promoter interactions, forced chromatin looping, sickle cell disease, hemoglobin switching, Therapeutics. Pharmacology, RM1-950

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2162253123000197; https://doaj.org/toc/2162-2531

URL الوصول: https://doaj.org/article/32788d42c8a3431085e1147f913baa4b

المؤلفون: Swati Singh, Iram Khan, Socheath Khim, Brenda Seymour, Karen Sommer, Matthew Wielgosz, Zachary Norgaard, Hans-Peter Kiem, Jennifer Adair, Denny Liggitt, Arthur Nienhuis, David J. Rawlings

المصدر: Molecular Therapy: Methods & Clinical Development, Vol 4, Iss C, Pp 1-16 (2017)

مصطلحات موضوعية: Wiskott-Aldrich Syndrome, gene therapy, insulated lentivirus, Genetics, QH426-470, Cytology, QH573-671

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050116301292; https://doaj.org/toc/2329-0501

URL الوصول: https://doaj.org/article/75b0053448c6480ca7c60f6f8b5d2a01

المؤلفون: Jun Zhan, Irudayam Maria Johnson, Matthew Wielgosz, Arthur W Nienhuis

المصدر: Molecular Therapy: Methods & Clinical Development, Vol 3, Iss C (2016)

مصطلحات موضوعية: Genetics, QH426-470, Cytology, QH573-671

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2329050116302017; https://doaj.org/toc/2329-0501

URL الوصول: https://doaj.org/article/a529b7f6d29c4eb3a98ee9fe12b605ea

المؤلفون: Naoya, Uchida, Francesca, Ferrara, Claire M, Drysdale, Morgan, Yapundich, Jackson, Gamer, Tina, Nassehi, Julia, DiNicola, Yoshitaka, Shibata, Matthew, Wielgosz, Yoon-Sang, Kim, Matthew, Bauler, Robert E, Throm, Juan J, Haro-Mora, Selami, Demirci, Aylin C, Bonifacino, Allen E, Krouse, N Seth, Linde, Robert E, Donahue, Byoung, Ryu, John F, Tisdale

المصدر: Science translational medicine. 13(591)

مصطلحات موضوعية: Repressor Proteins, Mice, Erythroid Cells, Receptors, Erythropoietin, Animals, Macaca mulatta, Fetal Hemoglobin

URL الوصول: https://explore.openaire.eu/search/publication?articleId=pmid________::f7d4c09f92cfc16e828243b01c520df5
https://pubmed.ncbi.nlm.nih.gov/33910976

المؤلفون: Yoon-Sang, Kim, Matthew, Wielgosz, Byoung, Ryu

المصدر: Methods in molecular biology (Clifton, N.J.). 2005

مصطلحات موضوعية: Mice, Transduction, Genetic, Genetic Vectors, Lentivirus, Hematopoietic Stem Cell Transplantation, Animals, Heterografts, Humans, Hematopoietic Stem Cells

URL الوصول: https://explore.openaire.eu/search/publication?articleId=pmid________::afbc47a7b9b0b9ca575e14664c778bed
https://pubmed.ncbi.nlm.nih.gov/31175648