-
1
المؤلفون: Shiangtung W. Jung, Li Jung Tai, Márcia Waddington-Cruz, William J. Litchy, Sotirios Tsimikas, Peter J. Dyck, Cecilia Monteiro, Gustavo Buchele, Julian D. Gillmore, Michela Brambatti, John L. Berk, Eugene Schneider, Yukio Ando, Teresa Coelho, Morie A. Gertz, Merrill D. Benson, Nicholas J. Viney, Louis O'Dea, Richard S. Geary, Brett P. Monia, Sami Khella, Laura Obici
المصدر: Neurology and therapy, vol 10, iss 1
Neurology and Therapyمصطلحات موضوعية: Oncology, endocrine system, medicine.medical_specialty, Neurology, Clinical Trials and Supportive Activities, Phases of clinical research, Neurodegenerative, Placebo, Study Protocol, 03 medical and health sciences, Rare Diseases, 0302 clinical medicine, Phase 3 clinical trial, Clinical Research, Internal medicine, medicine, Antisense oligonucleotide, 030212 general & internal medicine, Dosing, Peripheral Neuropathy, biology, business.industry, Amyloidosis, Clinical study design, Neurosciences, Evaluation of treatments and therapeutic interventions, nutritional and metabolic diseases, medicine.disease, Hereditary transthyretin-mediated amyloid polyneuropathy, AKCEA-TTR-L-rx, Clinical trial design, Transthyretin, Orphan Drug, AKCEA-TTR-Lrx, 6.1 Pharmaceuticals, biology.protein, Neurology (clinical), business, Polyneuropathy, 030217 neurology & neurosurgery
وصف الملف: application/pdf
-
2
المؤلفون: Louis O'Dea, Richard S. Geary, Eunju Hurh, Veronica J. Alexander, Kristin Balogh, Lynnetta Watts, Ewa Karwatowska-Prokopczuk, Sotirios Tsimikas
المصدر: Nucleic Acid Therapeutics. 30:198-206
مصطلحات موضوعية: 0301 basic medicine, medicine.medical_specialty, Messenger RNA, business.industry, Corrected qt, Affect (psychology), Biochemistry, QT interval, 03 medical and health sciences, 030104 developmental biology, 0302 clinical medicine, 030220 oncology & carcinogenesis, Internal medicine, Drug Discovery, Healthy volunteers, Antisense oligonucleotides, Genetics, Cardiology, Molecular Medicine, Medicine, business, Molecular Biology
-
3
المؤلفون: Linda C. Hemphill, Alberto Yataco, John P. Kane, Qingqing Yang, S.G. Hughes, Sotirios Tsimikas, Joseph L. Witztum, Robert A. Hegele, Manuel Castro-Cabezas, Robert Dufour, Steven Martin, Clinton Corder, Ulrich Julius, Seth J. Baum, Michel Krempf, James Powell, Mark Cervi, Steven Hamstead, Lawrence Galitz, Patrick M. Moriarty, Frank L.J. Visseren, Basil Issa, Traci Turner, Pankaj Vyas, Daniel Gaudet, Eunju Hurh, Erik S.G. Stroes, Peter P. Toth, Christie M. Ballantyne, Bruno Vergès, Cynthia Huffman, Jean Bergeron, Craig Thompson, Richard Shultzaberger, Ioanna Gouni-Berthold, Louis O'Dea, Cecil Murray Farrington, René Valéro, Eric Bruckert, Elisabeth Steinhagen-Thiessen, Abhay Agarwal, Letitia Thompson-Hargrave, Gordon A. Francis, Veronica J. Alexander, Richard Burdick
المساهمون: Experimental Vascular Medicine, Vascular Medicine, ACS - Atherosclerosis & ischemic syndromes, Unité de Recherche sur les Maladies Cardiovasculaires, du Métabolisme et de la Nutrition = Research Unit on Cardiovascular and Metabolic Diseases (ICAN), Assistance publique - Hôpitaux de Paris (AP-HP) (AP-HP)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Sorbonne Université (SU)-Institut de Cardiométabolisme et Nutrition = Institute of Cardiometabolism and Nutrition [CHU Pitié Salpêtrière] (IHU ICAN), CHU Pitié-Salpêtrière [AP-HP], Assistance publique - Hôpitaux de Paris (AP-HP) (AP-HP)-Sorbonne Université (SU)-Assistance publique - Hôpitaux de Paris (AP-HP) (AP-HP)-Sorbonne Université (SU)-CHU Pitié-Salpêtrière [AP-HP], Assistance publique - Hôpitaux de Paris (AP-HP) (AP-HP)-Sorbonne Université (SU), Centre recherche en CardioVasculaire et Nutrition = Center for CardioVascular and Nutrition research (C2VN), Aix Marseille Université (AMU)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Institut National de Recherche pour l’Agriculture, l’Alimentation et l’Environnement (INRAE)
المصدر: The Lancet Diabetes and Endocrinology, 9(5), 264-275. Elsevier BV
The Lancet. Diabetes & Endocrinology
The Lancet. Diabetes & Endocrinology, 2021, 9 (5), pp.264-275. ⟨10.1016/S2213-8587(21)00046-2⟩مصطلحات موضوعية: Adult, Male, medicine.medical_specialty, Internationality, Endocrinology, Diabetes and Metabolism, [SDV]Life Sciences [q-bio], Oligonucleotides, Phases of clinical research, 030209 endocrinology & metabolism, Placebo, law.invention, 03 medical and health sciences, chemistry.chemical_compound, Young Adult, 0302 clinical medicine, Endocrinology, Randomized controlled trial, Double-Blind Method, law, Internal medicine, Internal Medicine, medicine, Humans, 030212 general & internal medicine, Dosing, ComputingMilieux_MISCELLANEOUS, Aged, Triglyceride, business.industry, Middle Aged, Oligonucleotides, Antisense, medicine.disease, Clinical trial, Causality, Clinical research, Treatment Outcome, chemistry, Acute pancreatitis, Female, Hyperlipoproteinemia Type I, business, Follow-Up Studies
URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::0f0bbc0c3b73435049e18dbae3f86ae1
https://pure.amc.nl/en/publications/efficacy-and-safety-of-volanesorsen-in-patients-with-multifactorial-chylomicronaemia-compass-a-multicentre-doubleblind-randomised-placebocontrolled-phase-3-trial(2a99109c-0aba-417c-98a2-6f552441ac78).html -
4
المؤلفون: Hartmut Schmidt, Eunju Hurh, Louis O'Dea, Brant Hubbard, Elif Arioglu Oral, Anatoly Tiulpakov, Joseph Tami, Veronica J. Alexander, Ann Mertens, A. Garg, Lynnetta Watts
المصدر: Endocrine Abstracts.
مصطلحات موضوعية: Pediatrics, medicine.medical_specialty, business.industry, Medicine, In patient, business, Familial partial lipodystrophy, medicine.disease
-
5
المؤلفون: Anatoly Tiulpakov, Elif Arioglu Oral, Eunju Hurh, Hartmut Schmidt, Lynnetta Watts, Louis O'Dea, Brant Hubbard, Joseph Tami, A. Garg, Ann Mertens, Veronica J. Alexander
المصدر: Endocrine Abstracts.
مصطلحات موضوعية: Pediatrics, medicine.medical_specialty, business.industry, Medicine, Baseline data, business, Familial partial lipodystrophy, medicine.disease
-
6
المؤلفون: Joyce Kingsbury, Amparo L Figueroa, Joseph L. Witztum, Walter Singleton, Louis O'Dea, Daniel Gaudet, Philip Piscitelli, Ewa Karwatowska-Prokopczuk, Sotirios Tsimikas, Seth J. Baum, Vupanorsen Study Investigators, Eunju Hurh, Richard S. Geary, Victoria J Bartlett
المصدر: European heart journal. 41(40)
مصطلحات موضوعية: medicine.medical_specialty, Apolipoprotein B, Lipoproteins, Galactosamine, Type 2 diabetes, 030204 cardiovascular system & hematology, 03 medical and health sciences, chemistry.chemical_compound, 0302 clinical medicine, Double-Blind Method, Internal medicine, Diabetes mellitus, Medicine, Humans, RNA, Messenger, Triglycerides, 030304 developmental biology, Angiopoietin-Like Protein 3, Hypertriglyceridemia, 0303 health sciences, biology, business.industry, Cholesterol, Fatty liver, medicine.disease, Endocrinology, Angiopoietin-like Proteins, chemistry, Diabetes Mellitus, Type 2, Pharmaceutical Preparations, biology.protein, Steatosis, Cardiology and Cardiovascular Medicine, business, Lipoprotein
-
7
المؤلفون: Lynnetta M, Watts, Ewa, Karwatowska-Prokopczuk, Eunju, Hurh, Veronica J, Alexander, Kristin, Balogh, Louis, O'Dea, Richard S, Geary, Sotirios, Tsimikas
المصدر: Nucleic Acid Therapeutics
مصطلحات موضوعية: Adult, Hypertriglyceridemia, Male, antisense oligonucleotide, Apolipoprotein C-III, Dose-Response Relationship, Drug, Drug-Related Side Effects and Adverse Reactions, Moxifloxacin, Oligonucleotides, QTc interval, subcutaneous (SC) therapeutic dose, Oligonucleotides, Antisense, Placebo Effect, Original Papers, Healthy Volunteers, Electrocardiography, Double-Blind Method, Humans, Female, volanesorsen, RNA, Messenger, Triglycerides, supratherapeutic dose
-
8
المؤلفون: Michael Stevenson, Louis O'Dea, Handrean Soran, Marcello Arca, Paul D. Rosenblit, Andrew Hsieh
المصدر: Expert Review of Cardiovascular Therapy. 16:537-546
مصطلحات موضوعية: Adult, Male, Burden of disease, Pediatrics, medicine.medical_specialty, hypertriglyceridemia, Oligonucleotides, 030204 cardiovascular system & hematology, type 1 hyperlipoproteinemia, 03 medical and health sciences, 0302 clinical medicine, Quality of life, Internal Medicine, medicine, Humans, survey, volanesorsen, In patient, 030212 general & internal medicine, Aged, Retrospective Studies, Apolipoprotein C-III, business.industry, Hypertriglyceridemia, familial chylomicronemia syndrome, quality of life, General Medicine, Middle Aged, Familial Chylomicronemia, medicine.disease, Clinical trial, Female, Hyperlipoproteinemia Type I, lipids (amino acids, peptides, and proteins), Cardiology and Cardiovascular Medicine, business
-
9
المؤلفون: Cecilia Monteiro, Qingqing Yang, Nick Viney, Arnt V. Kristen, Merrill D. Benson, Rodney H. Falk, Louis O'Dea, Brett P. Monia, Li Tai, Eugene Schneider, Mathew S. Maurer, Gustavo Buchele, Sotirios Tsimikas, Brambatti Michela, Richard S. Geary
المصدر: Heart & Lung. 50:565-566
مصطلحات موضوعية: Pulmonary and Respiratory Medicine, Tafamidis, medicine.medical_specialty, biology, business.industry, Phases of clinical research, Critical Care and Intensive Care Medicine, Placebo, Gastroenterology, Clinical trial, chemistry.chemical_compound, Regimen, Transthyretin, chemistry, Tolerability, Internal medicine, biology.protein, Medicine, Cardiology and Cardiovascular Medicine, business, Amyloid cardiomyopathy
-
10
المؤلفون: Joseph L. Witztum, Richard S. Geary, Veronica J. Alexander, Eunju Hurh, Louis O'Dea, Steven G. Hughes, Sotirios Tsimikas, Shuting Xia
المصدر: European heart journal, vol 40, iss 33
مصطلحات موضوعية: Male, Apolipoprotein B, Messenger, Oligonucleotides, 030204 cardiovascular system & hematology, Cardiorespiratory Medicine and Haematology, Cardiovascular, chemistry.chemical_compound, 0302 clinical medicine, Hypertriglyceridaemia, Protein biosynthesis, Medicine, media_common, Hypertriglyceridemia, 0303 health sciences, biology, Middle Aged, Cardiovascular disease, Cholesterol, Treatment Outcome, Heart Disease, 6.1 Pharmaceuticals, Female, Cardiology and Cardiovascular Medicine, Drug, Adult, medicine.medical_specialty, Adolescent, media_common.quotation_subject, Clinical Trials and Supportive Activities, Clinical Sciences, Drug Administration Schedule, 03 medical and health sciences, Young Adult, Double-Blind Method, Clinical Research, Internal medicine, Humans, Antisense, APOC3 Gene, 030304 developmental biology, Apolipoproteins B, Aged, Messenger RNA, Apolipoprotein C-III, business.industry, Evaluation of treatments and therapeutic interventions, medicine.disease, Atherosclerosis, Endocrinology, chemistry, Cardiovascular System & Hematology, Galactosamine, biology.protein, RNA, business
وصف الملف: application/pdf
-
11
المؤلفون: Rob Halter, Brant Hubbard, Elif Oral, Louis O'Dea, Michael Stevenson, Nandini Hadker, Caroline Crowson
المصدر: Journal of Clinical Lipidology. 14:590
مصطلحات موضوعية: Gerontology, Nutrition and Dietetics, Quality of life (healthcare), business.industry, Endocrinology, Diabetes and Metabolism, Perspective (graphical), Internal Medicine, Medicine, Cardiology and Cardiovascular Medicine, business, Familial partial lipodystrophy, medicine.disease
-
12
المؤلفون: James MacDougall, Handrean Soran, Patrick M. Moriarty, Daniel Gaudet, Brant Hubbard, John J.P. Kastelein, Veronica J. Alexander, Robert A. Hegele, Joseph L. Witztum, Andres Digenio, Marcello Arca, Louis O'Dea, Eric Bruckert
المساهمون: Vascular Medicine, ACS - Atherosclerosis & ischemic syndromes, ACS - Pulmonary hypertension & thrombosis
المصدر: Journal of the Endocrine Society, 3(12), 2397-2410. Endocrine Society
Journal of the Endocrine Societyمصطلحات موضوعية: medicine.medical_specialty, Endocrinology, Diabetes and Metabolism, severe hypertriglyceridemia, pancreatitis, 030209 endocrinology & metabolism, Context (language use), 030204 cardiovascular system & hematology, Logistic regression, BMI, 03 medical and health sciences, 0302 clinical medicine, Internal medicine, medicine, Medical history, clinical variables, familial chylomicronemia syndrome, Clinical Research Articles, Genetic testing, medicine.diagnostic_test, Receiver operating characteristic, business.industry, Lipids and Cardiovascular, Metabolic disorder, medicine.disease, Cohort, lipids (amino acids, peptides, and proteins), business, Body mass index
-
13
المؤلفون: Louis O'Dea, Sotirios Tsimikas, Qingqing Yang, Erik S.G. Stroes, Daniel Gaudet, Fernando Civeira, Handrean Soran, Dirk J. Blom, Linda C. Hemphill, Steven D. Freedman, Jean Bergeron, Joseph L. Witztum, Steven Hughes, Richard S. Geary, Eric Bruckert, Andres Digenio, Veronica J. Alexander, Marcello Arca, Karren R Williams
المساهمون: University of California [San Diego] (UC San Diego), University of California, Université de Montréal (UdeM), Beth Israel Deaconess Medical Center [Boston] (BIDMC), Harvard Medical School [Boston] (HMS), Università degli Studi di Roma 'La Sapienza' = Sapienza University [Rome], Université Laval [Québec] (ULaval), Manchester University NHS Foundation Trust (MFT), University of Zaragoza - Universidad de Zaragoza [Zaragoza], Massachusetts General Hospital [Boston], University of Cape Town, CHU Pitié-Salpêtrière [AP-HP], Sorbonne Université (SU)-Assistance publique - Hôpitaux de Paris (AP-HP) (AP-HP), Vascular Medicine, ACS - Atherosclerosis & ischemic syndromes
المصدر: Zaguán: Repositorio Digital de la Universidad de Zaragoza
Universidad de Zaragoza
New England Journal of Medicine
New England Journal of Medicine, Massachusetts Medical Society, 2019, 381 (6), pp.531-542. ⟨10.1056/NEJMoa1715944⟩
Zaguán. Repositorio Digital de la Universidad de Zaragoza
instname
New England journal of medicine, 381(6), 531-542. Massachussetts Medical Societyمصطلحات موضوعية: Adult, Male, medicine.medical_specialty, [SDV]Life Sciences [q-bio], Injections, Subcutaneous/adverse effects, 030204 cardiovascular system & hematology, Triglycerides blood, Hyperlipoproteinemia Type I/blood, familial chylomicronemia, volanesorsen, triglycerides, therapy, apoCIII, familial chylomicronemia, Injections, Oligonucleotides/administration & dosage, Young Adult, 03 medical and health sciences, chemistry.chemical_compound, 0302 clinical medicine, Double-Blind Method, apoCIII, Internal medicine, Humans, Medicine, volanesorsen, 030212 general & internal medicine, triglycerides, Aged, RNA, Messenger/antagonists & inhibitors, therapy, Analysis of Variance, Triglyceride, Platelet Count, Thrombocytopenia/chemically induced, business.industry, Genetic disorder, General Medicine, Middle Aged, Familial Chylomicronemia, medicine.disease, 3. Good health, Triglycerides/blood, Endocrinology, Multicenter study, chemistry, RNA, Female, Subcutaneous/adverse effects, Apolipoprotein C-III/antagonists & inhibitors, business, Lipoprotein lipase activity, Messenger/antagonists & inhibitors
وصف الملف: application/pdf
-
14
المؤلفون: Linda C. Hemphill, Raul D. Santos, Dirk J. Blom, Seth J. Baum, Andres Digenio, Ewa Karwatowska-Prokopczuk, Joseph L. Witztum, Ovidio Muñiz-Grijalvo, Louis O'Dea, Karren R Williams, Veronica J. Alexander
المصدر: Repositório Institucional da USP (Biblioteca Digital da Produção Intelectual)
Universidade de São Paulo (USP)
instacron:USPمصطلحات موضوعية: 0301 basic medicine, Adult, Male, Chylomicronemia, medicine.medical_specialty, Endocrinology, Diabetes and Metabolism, Natural history, Oligonucleotides, Hyperlipoproteinemia, 030204 cardiovascular system & hematology, Cohort Studies, 03 medical and health sciences, Lipoprotein lipase deficiency, Young Adult, 0302 clinical medicine, Internal medicine, Internal Medicine, medicine, Humans, Young adult, Hypertriglyceridemia, Nutrition and Dietetics, business.industry, Extremely restrictive low-fat diet, Metabolic disorder, Middle Aged, medicine.disease, Acute pancreatitis, 030104 developmental biology, Treatment Outcome, Population study, Pancreatitis, lipids (amino acids, peptides, and proteins), Female, Hyperlipoproteinemia Type I, Familial Chylomicronemia Syndrome, DIETA COM RESTRIÇÃO DE GORDURAS, Cardiology and Cardiovascular Medicine, business, Body mass index
-
15
المؤلفون: Morie A. Gertz, Eugene Schneider, Qingqing Yang, Gustavo Buchele, Rodney H. Falk, Michela Brambatti, Ewa Karwatowska-Prokopczuk, Nicholas J. Viney, Sotirios Tsimikas, Cecilia Monteiro, Richard S. Geary, Merrill D. Benson, Brett P. Monia, Li-Jung Tai, Louis O'Dea
المصدر: Blood. 134:5764-5764
مصطلحات موضوعية: Tafamidis, medicine.medical_specialty, business.industry, Surrogate endpoint, Immunology, Disease progression, Phases of clinical research, Cell Biology, Hematology, Placebo, Biochemistry, chemistry.chemical_compound, chemistry, Family medicine, Medicine, Data monitoring committee, In patient, business, Amyloid cardiomyopathy
-
16
المؤلفون: Paul Saenger, Ora H. Pescovitz, Barry B. Bercu, Frederick T. Murray, Hal Landy, Jim Brentzel, Louis O'Dea, B. Hanson, Campbell Howard, Sadeghi-Nejad Abdollah, Edward O. Reiter, Geref International Study Group
المصدر: Endocrine. 15:S51-S56
مصطلحات موضوعية: Endocrinology, Endocrinology, Diabetes and Metabolism
-
17
المؤلفون: Ernest Loumaye, Louis O’Dea, Colin M. Howles, Patrick Engrand
المصدر: Fertility and Sterility. 67:889-899
مصطلحات موضوعية: Adult, medicine.medical_specialty, medicine.drug_class, medicine.medical_treatment, media_common.quotation_subject, Fertilization in Vitro, Biology, Chorionic Gonadotropin, Follicle-stimulating hormone, Pregnancy, Internal medicine, Follicular phase, medicine, Humans, Prospective Studies, Ovulation, Retrospective Studies, media_common, In vitro fertilisation, Estradiol, Obstetrics and Gynecology, Luteinizing Hormone, Embryo Transfer, Embryo transfer, Pregnancy rate, Treatment Outcome, Endocrinology, Reproductive Medicine, Oocytes, Female, Follicle Stimulating Hormone, Gonadotropin, Luteinizing hormone
-
18
المؤلفون: Susan Ince, Genevieve Decosterd, Angela Piazzi, Louis O’Dea, Isabelle Martineau, K. Van Loon, Ernest Loumaye, A. Galazka, Colin M. Howles
المصدر: Human reproduction (Oxford, England). 11
مصطلحات موضوعية: endocrine system, medicine.medical_specialty, medicine.drug_class, media_common.quotation_subject, Drug Evaluation, Preclinical, CHO Cells, Biology, Chorionic Gonadotropin, law.invention, Anovulation, Follicle-stimulating hormone, law, Internal medicine, Cricetinae, Follicular phase, medicine, Animals, Humans, Ovulation, media_common, Randomized Controlled Trials as Topic, Chinese hamster ovary cell, Rehabilitation, Obstetrics and Gynecology, Luteinizing Hormone, medicine.disease, Recombinant Proteins, Endocrinology, Reproductive Medicine, Recombinant DNA, Female, Gonadotropin, Follicle Stimulating Hormone, Luteinizing hormone, Genetic Engineering, hormones, hormone substitutes, and hormone antagonists
-
19Academic Journal
المؤلفون: Louis O'Dea1, Fanny O'Brien2, Karen Currie3, George Hemsey4
المصدر: Current Medical Research & Opinion. Oct2008, Vol. 24 Issue 10, p2785-2793. 9p.
مصطلحات موضوعية: *AMENORRHEA treatment, *LUTEINIZING hormone, *FOLLICLE-stimulating hormone, *ESTRADIOL, *DOSE-effect relationship in pharmacology, *ACADEMIC medical centers