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1Academic Journal
المؤلفون: Tahereh Mohammadian Gol, Guillermo Ureña-Bailén, Yujuan Hou, Ralph Sinn, Justin S. Antony, Rupert Handgretinger, Markus Mezger
المصدر: Frontiers in Genome Editing, Vol 4 (2023)
مصطلحات موضوعية: CRISPR/Cas, blood disorder, physical delivery, viral vectors, non-viral vectors, Biotechnology, TP248.13-248.65, Genetics, QH426-470
وصف الملف: electronic resource
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2Academic Journal
المؤلفون: Stefan Grote, Guillermo Ureña-Bailén, Kenneth Chun-Ho Chan, Caroline Baden, Markus Mezger, Rupert Handgretinger, Sabine Schleicher
المصدر: Cells, Vol 10, Iss 5, p 1020 (2021)
مصطلحات موضوعية: CD276, B7-H3, chimeric antigen receptor, NK-92, immune therapy, melanoma, Cytology, QH573-671
وصف الملف: electronic resource
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3Academic Journal
المؤلفون: Yujuan Hou, Guillermo Ureña-Bailén, Tahereh Mohammadian Gol, Paul Gerhard Gratz, Hans Peter Gratz, Alicia Roig-Merino, Justin S. Antony, Andrés Lamsfus-Calle, Alberto Daniel-Moreno, Rupert Handgretinger, Markus Mezger
المصدر: Genes; Volume 13; Issue 12; Pages: 2348
مصطلحات موضوعية: IL2RG, SCID, CRISPR/Cas9, ssODN, prime editing, somatic mosaicism
جغرافية الموضوع: agris
وصف الملف: application/pdf
Relation: Human Genomics and Genetic Diseases; https://dx.doi.org/10.3390/genes13122348
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4Academic JournalPreclinical Evaluation of CRISPR-Edited CAR-NK-92 Cells for Off-the-Shelf Treatment of AML and B-ALL
المؤلفون: Guillermo Ureña-Bailén, Jérôme-Maurice Dobrowolski, Yujuan Hou, Alicia Dirlam, Alicia Roig-Merino, Sabine Schleicher, Daniel Atar, Christian Seitz, Judith Feucht, Justin S. Antony, Tahereh Mohammadian Gol, Rupert Handgretinger, Markus Mezger
المصدر: International Journal of Molecular Sciences; Volume 23; Issue 21; Pages: 12828
مصطلحات موضوعية: NK-92, CD19-CAR, CD276-CAR, leukemia, AML, B-ALL, CRISPR-Cas9 knock-out, CBLB, NKG2A, TIGIT
جغرافية الموضوع: agris
وصف الملف: application/pdf
Relation: Molecular Biology; https://dx.doi.org/10.3390/ijms232112828
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5Academic JournalSomatic Reversion of a Novel IL2RG Mutation Resulting in Atypical X-Linked Combined Immunodeficiency
المؤلفون: Yujuan Hou, Hans Peter Gratz, Guillermo Ureña-Bailén, Paul G. Gratz, Karin Schilbach-Stückle, Tina Renno, Derya Güngör, Daniel A. Mader, Elke Malenke, Justin S. Antony, Rupert Handgretinger, Markus Mezger
المصدر: Genes; Volume 13; Issue 1; Pages: 35
مصطلحات موضوعية: atypical X-SCID, immunodeficiency, IL-2RG, γ C, somatic reversion, hypomorphic mutation
جغرافية الموضوع: agris
وصف الملف: application/pdf
Relation: Human Genomics and Genetic Diseases; https://dx.doi.org/10.3390/genes13010035
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6
المؤلفون: Guillermo Ureña-Bailén, Milena Block, Tommaso Grandi, Faidra Aivazidou, Jona Quednau, Dariusz Krenz, Alberto Daniel-Moreno, Andrés Lamsfus-Calle, Thomas Epting, Rupert Handgretinger, Stefan Wild, Markus Mezger
المصدر: CRISPR J
مصطلحات موضوعية: Genetics, Original Research, Biotechnology
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7Somatic Reversion of a Novel IL2RG Mutation Resulting in Atypical X-Linked Combined Immunodeficiency
المؤلفون: Yujuan Hou, Hans Peter Gratz, Guillermo Ureña-Bailén, Paul G. Gratz, Karin Schilbach-Stückle, Tina Renno, Derya Güngör, Daniel A. Mader, Elke Malenke, Justin S. Antony, Rupert Handgretinger, Markus Mezger
المصدر: Genes, Vol 13, Iss 35, p 35 (2022)
مصطلحات موضوعية: atypical X-SCID, Genetics, hypomorphic mutation, somatic reversion, IL-2RG, QH426-470, immunodeficiency, γC
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8
المؤلفون: Justin S. Antony, Markus Mezger, Alberto Daniel-Moreno, Praveen Baskaran, Rupert Handgretinger, Jennifer Rottenberger, Andrés Lamsfus-Calle, Sabina Marciano, Janani Raju, Thomas Epting, Lukas Heumos, Guillermo Ureña-Bailén
المصدر: The CRISPR Journal. 4:207-222
مصطلحات موضوعية: Gene Editing, Transgene, beta-Thalassemia, KLF1, Genetic Therapy, beta-Globins, Dependovirus, Biology, Hematopoietic Stem Cells, medicine.disease_cause, Hemoglobinopathies, Insertional mutagenesis, Homology directed repair, Fetal hemoglobin, Genetics, medicine, Cancer research, Humans, Clustered Regularly Interspaced Short Palindromic Repeats, CRISPR-Cas Systems, Enhancer, Adeno-associated virus, Gene, Fetal Hemoglobin, Biotechnology
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9
المؤلفون: Guillermo Ureña-Bailén, Justin S. Antony, Yujuan Hou, Janani Raju, Andres Lamsfus-Calle, Alberto Daniel-Moreno, Rupert Handgretinger, Markus Mezger
المصدر: CRISPR-/Cas9 Based Genome Editing for Treating Genetic Disorders and Diseases ISBN: 9781003088516
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10
المؤلفون: Justin S. Antony, Alberto Daniel-Moreno, Andrés Lamsfus-Calle, Janani Raju, Merve Kaftancioglu, Guillermo Ureña-Bailén, Jennifer Rottenberger, Yujuan Hou, Vidiyaah Santhanakumaran, Jun-Hoe Lee, Lukas Heumos, Judith Böhringer, Ingeborg Krägeloh-Mann, Rupert Handgretinger, Markus Mezger
المصدر: The CRISPR journal. 5(1)
مصطلحات موضوعية: Gene Editing, Mutation, Genetics, Humans, Genetic Therapy, Leukodystrophy, Metachromatic, Prospective Studies, CRISPR-Cas Systems, Hematopoietic Stem Cells, Biotechnology
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11
المؤلفون: Christian Seitz, Daniel Atar, Justin S. Antony, Patrick Schlegel, Alberto Daniel-Moreno, Markus Mezger, Rupert Handgretinger, Guillermo Ureña-Bailén, Andrés Lamsfus-Calle, Janani Raju
المصدر: Briefings in Functional Genomics. 19:191-200
مصطلحات موضوعية: Gene Editing, 0303 health sciences, medicine.medical_treatment, Cell, Cancer, Computational biology, Immunotherapy, Biology, medicine.disease, Chimeric antigen receptor, Clinical trial, 03 medical and health sciences, 0302 clinical medicine, medicine.anatomical_structure, Genome editing, 030220 oncology & carcinogenesis, medicine, Humans, CRISPR, CRISPR-Cas Systems, Car t cells, 030304 developmental biology
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12
المؤلفون: Kenneth Chun-Ho Chan, Rupert Handgretinger, Sabine Schleicher, Caroline Baden, Guillermo Ureña-Bailén, Stefan Grote, Markus Mezger
المصدر: Cells
Volume 10
Issue 5
Cells, Vol 10, Iss 1020, p 1020 (2021)مصطلحات موضوعية: Cytotoxicity, Immunologic, B7 Antigens, Skin Neoplasms, QH301-705.5, medicine.medical_treatment, In Vitro Techniques, Immunotherapy, Adoptive, Article, Immune system, NK-92, Antigen, Antigens, Neoplasm, Cell Movement, Cell Line, Tumor, immune therapy, medicine, Tumor Microenvironment, melanoma, Cytotoxic T cell, Humans, Neoplasm Invasiveness, Lactic Acid, CD276, Biology (General), Hypoxia, CRISPR/Cas9, Immunosuppression Therapy, Tumor microenvironment, Receptors, Chimeric Antigen, chimeric antigen receptor, business.industry, Melanoma, Lentivirus, General Medicine, Immunotherapy, Fibroblasts, Hydrogen-Ion Concentration, medicine.disease, Chimeric antigen receptor, Gene Expression Regulation, Neoplastic, Killer Cells, Natural, B7-H3, Immune System, Cancer research, CRISPR-Cas Systems, business, Immunosuppressive Agents
وصف الملف: application/pdf
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13
المؤلفون: Andrés Lamsfus-Calle, Rupert Handgretinger, Alberto Daniel-Moreno, Markus Mezger, Guillermo Ureña-Bailén, Janani Raju, Justin S. Antony
المصدر: Blood reviews. 40
مصطلحات موضوعية: Gene Editing, biology, Cas9, Genetic enhancement, medicine.medical_treatment, Lentivirus, Hematopoietic Stem Cell Transplantation, Hematopoietic stem cell, Hematology, Hematopoietic stem cell transplantation, Computational biology, Genetic Therapy, biology.organism_classification, Hematopoietic Stem Cells, Hematologic Diseases, medicine.anatomical_structure, Oncology, Genome editing, Immune System Diseases, medicine, CRISPR, Humans, Autografts, Gene