-
1Dissertation/ Thesis
المؤلفون: Malaiwong, Nawaphat
المساهمون: University/Department: Universitat Politècnica de Catalunya. Institut de Ciències Fotòniques
Thesis Advisors: Krieg, Michael
المصدر: TDX (Tesis Doctorals en Xarxa)
مصطلحات موضوعية: Mechanosensation, Proprioception, C. elegans, Gene editing, Mecanosensació, Propriocepció, Edició de gens, Àrees temàtiques de la UPC::Enginyeria biomèdica
وصف الملف: application/pdf
URL الوصول: http://hdl.handle.net/10803/690281
-
2Dissertation/ Thesis
المؤلفون: Santo Domingo Martínez, Miguel
Thesis Advisors: Garcia Mas, Jordi, Pujol Abajo, Marta
المصدر: TDX (Tesis Doctorals en Xarxa)
مصطلحات موضوعية: Maduració, Maduración, Fruit ripening, Meló, Melón, Melon, Edició gènica, Edición génica, Gene editing, Ciències Experimentals
وصف الملف: application/pdf
URL الوصول: http://hdl.handle.net/10803/688042
-
3Academic Journal
المؤلفون: Stevens, Christian, Carmichael, Jillian, Watkinson, Ruth, Kowdle, Shreyas, Reis, Rebecca, Hamane, Kory, Jang, Jason, Park, Arnold, Pernet, Olivier, Khamaikawin, Wannisa, Hong, Patrick, Thibault, Patricia, Gowlikar, Aditya, An, Dong, Lee, Benhur
المصدر: Journal of Virology. 98(12)
مصطلحات موضوعية: CCR5, CRISPR/Cas9, HIV, Paramyxoviridae, Sendai virus, gene editing, hematopoietic stem and progenitor cells, monocytes, viral vector, Gene Editing, Humans, Sendai virus, Receptors, CCR5, Hematopoietic Stem Cells, Genetic Vectors, CRISPR-Cas Systems, Temperature, HIV-1, Transduction, Genetic, HIV Infections, Monocytes
وصف الملف: application/pdf
-
4Academic Journal
المؤلفون: Ngo, Wayne, Peukes, Julia, Baldwin, Alisha, Xue, Zhiwei, Hwang, Sidney, Stickels, Robert, Lin, Zhi, Satpathy, Ansuman, Wells, James, Schekman, Randy, Nogales De La Morena, Evangelina, Doudna, Jennifer
المصدر: Proceedings of the National Academy of Sciences. 122(1)
مصطلحات موضوعية: delivery, genome editing, viral-like particles, Gene Editing, Humans, CRISPR-Cas Systems, Lentivirus, Ribonucleoproteins, HEK293 Cells, CRISPR-Associated Protein 9, Genetic Vectors
وصف الملف: application/pdf
-
5Academic Journal
المؤلفون: Rallabandi, Harikrishna, Singh, Manish, Looger, Loren, Nath, Swapan
المصدر: International Journal of Molecular Sciences. 26(1)
مصطلحات موضوعية: CLEC16A, autophagy, enhancer, lupus, post-GWAS, Lectins, C-Type, Humans, Lupus Erythematosus, Systemic, Genetic Predisposition to Disease, Monosaccharide Transport Proteins, Polymorphism, Single Nucleotide, Alleles, Autophagy, Genome-Wide Association Study, Gene Editing, STAT3 Transcription Factor, CRISPR-Cas Systems, B-Lymphocytes, Chromosomes, Human, Pair 16
وصف الملف: application/pdf
-
6Academic Journal
المؤلفون: Luthers, Christopher, Ha, Sung-Min, Mittelhauser, Annika, Morselli, Marco, Long, Joseph, Kuo, Caroline, Romero, Zulema, Kohn, Donald
المصدر: Molecular Therapy: Methods & Clinical Development. 32(4)
مصطلحات موضوعية: CD40LG, CRISPR-Cas9, HBB, adeno-associated virus 6, gene editing, hematopoietic stem cells, homologous recombination, non-homologous end joining, sickle cell disease
وصف الملف: application/pdf
-
7Academic Journal
المؤلفون: Arantes, Pablo, Chen, Xiaoyu, Sinha, Souvik, Saha, Aakash, Patel, Amun, Sample, Matthew, Nierzwicki, Łukasz, Lapinaite, Audrone, Palermo, Giulia
المصدر: Nucleic Acids Research. 52(22)
مصطلحات موضوعية: Gene Editing, CRISPR-Cas Systems, CRISPR-Associated Protein 9, DNA, Protein Multimerization, Humans, Adenosine Deaminase, Protein Domains, Deamination, Molecular Dynamics Simulation, Adenine
وصف الملف: application/pdf
-
8Academic Journal
المؤلفون: Wu, Yiqian, Huang, Ziliang, Liu, Yahan, He, Peixiang, Wang, Yuxuan, Yan, Liyanran, Wang, Xinhui, Gao, Shanzi, Zhou, Xintao, Yoon, Chi, Sun, Kun, Situ, Yinglin, Ho, Phuong, Zeng, Yushun, Yuan, Zhou, Zhu, Linshan, Zhou, Qifa, Zhao, Yunde, Liu, Thomas, Kwong, Gabriel, Chien, Shu, Liu, Longwei, Wang, Yingxiao
المصدر: Nature Communications. 15(1)
مصطلحات موضوعية: Humans, Neoplasms, Animals, CRISPR-Cas Systems, Receptors, Chimeric Antigen, Mice, Cell Line, Tumor, Gene Editing, Clustered Regularly Interspaced Short Palindromic Repeats, Immunotherapy, Adoptive, Dependovirus, Immunotherapy, Genomics, Ultrasonic Waves
وصف الملف: application/pdf
-
9Academic Journal
المؤلفون: Gao, Kewa, Han, Hesong, Cranick, Matileen G, Zhao, Sheng, Xu, Shanxiu, Yin, Boyan, Song, Hengyue, Hu, Yibo, Clarke, Maria T, Wang, David, Wong, Jessica M, Zhao, Zehua, Burgstone, Benjamin W, Farmer, Diana L, Murthy, Niren, Wang, Aijun
المصدر: ACS Nano. 18(44)
مصطلحات موضوعية: Medical Biotechnology, Biomedical and Clinical Sciences, Neurosciences, Intellectual and Developmental Disabilities (IDD), Pediatric, Bioengineering, Nanotechnology, Biotechnology, Gene Therapy, Stem Cell Research, Mental Health, Brain Disorders, Genetics, Perinatal Period - Conditions Originating in Perinatal Period, 2.1 Biological and endogenous factors, 5.1 Pharmaceuticals, 5.2 Cellular and gene therapies, Reproductive health and childbirth, Neurological, Animals, Mice, Brain, RNA, Messenger, Nanoparticles, Female, Lipids, Gene Editing, Pregnancy, Polyethylene Glycols, Liposomes, in utero, gene editing, mRNA delivery, nanoparticles, CRISPR/Cas9, CNS disorder, Nanoscience & Nanotechnology
وصف الملف: application/pdf
-
10Academic Journal
المؤلفون: Chen, An-Ping, Gao, Peng, Lin, Liang, Ashok, Preeti, He, Hongzhi, Ma, Chao, Zou, David, Allain, Vincent, Boyne, Alex, Juillerat, Alexandre, Duchateau, Philippe, Rath, Armin, Teper, Daniel, Arulanandam, Antonio, Chang, Hao-Ming, Eyquem, Justin, Li, Wei
المصدر: Cell Reports: Methods. 4(9)
مصطلحات موضوعية: B2M, CP: cancer biology, GUIDE-seq, TALEN, TGFβR2, anti-tumor, beta-2-microglobulin, gene editing, human induced pluripotent stem cells, iPSC-derived cell therapies, iPSCs, interleukin-15, natural killer cells, Induced Pluripotent Stem Cells, Killer Cells, Natural, Interleukin-15, Humans, Receptor, Transforming Growth Factor-beta Type II, Cell Differentiation, Transcription Activator-Like Effector Nucleases, Gene Editing
وصف الملف: application/pdf
-
11Academic Journal
المؤلفون: Ruan, Weimin, Xu, Sen, An, Yang, Cui, Yingxue, Liu, Yang, Wang, Yibin, Ismail, Muhammad, Liu, Yong, Zheng, Meng
المصدر: Advanced Science. 11(33)
مصطلحات موضوعية: CRISPR, Cas12a, gene‐editing, glioblastoma, nanocapsule, Glioblastoma, Animals, Mice, Nanocapsules, Gene Editing, Brain Neoplasms, CRISPR-Cas Systems, Humans, Polo-Like Kinase 1, Disease Models, Animal, Cell Line, Tumor, Protein Serine-Threonine Kinases, Proto-Oncogene Proteins, ErbB Receptors, Cell Cycle Proteins, Mice, Nude, CRISPR-Associated Proteins, Bacterial Proteins, Endodeoxyribonucleases
وصف الملف: application/pdf
-
12Academic Journal
المؤلفون: Hołubowicz, Rafał, Du, Samuel W, Felgner, Jiin, Smidak, Roman, Choi, Elliot H, Palczewska, Grazyna, Menezes, Carolline Rodrigues, Dong, Zhiqian, Gao, Fangyuan, Medani, Omar, Yan, Alexander L, Hołubowicz, Maria W, Chen, Paul Z, Bassetto, Marco, Risaliti, Eleonora, Salom, David, Workman, J Noah, Kiser, Philip D, Foik, Andrzej T, Lyon, David C, Newby, Gregory A, Liu, David R, Felgner, Philip L, Palczewski, Krzysztof
المصدر: Nature Biomedical Engineering. 9(1)
مصطلحات موضوعية: Engineering, Biomedical Engineering, Bioengineering, Genetics, Gene Therapy, Nanotechnology, Biotechnology, Generic health relevance, Animals, Humans, Mice, Lipids, Ribonucleoproteins, Nanoparticles, Cell-Penetrating Peptides, Gene Editing, Biomedical engineering
وصف الملف: application/pdf
-
13Academic Journal
المؤلفون: Du, Samuel W, Newby, Gregory A, Salom, David, Gao, Fangyuan, Menezes, Carolline Rodrigues, Suh, Susie, Choi, Elliot H, Chen, Paul Z, Liu, David R, Palczewski, Krzysztof
المصدر: Proceedings of the National Academy of Sciences of the United States of America. 121(48)
مصطلحات موضوعية: Biomedical and Clinical Sciences, Ophthalmology and Optometry, Eye Disease and Disorders of Vision, Neurodegenerative, Biotechnology, Neurosciences, Orphan Drug, Genetics, Rare Diseases, 2.1 Biological and endogenous factors, 5.2 Cellular and gene therapies, Eye, Animals, Rhodopsin, Retinitis Pigmentosa, Mice, Gene Editing, Disease Models, Animal, CRISPR-Cas Systems, Retinal Rod Photoreceptor Cells, Mutation, rhodopsin, base editing, prime editing, retinitis pigmentosa
وصف الملف: application/pdf
-
14Academic Journal
المؤلفون: He, Yawen, Chen, Juhong
المصدر: Analytical Chemistry. 96(45)
مصطلحات موضوعية: CRISPR-Cas Systems, Gene Editing, Bacteriophage T4, Escherichia coli, Microbial Sensitivity Tests, Anti-Bacterial Agents, Humans, Colorimetry, High-Throughput Screening Assays, beta-Galactosidase
وصف الملف: application/pdf
-
15Academic Journal
المؤلفون: Hamilton, Jennifer R, Chen, Evelyn, Perez, Barbara S, Sandoval Espinoza, Cindy R, Kang, Min Hyung, Trinidad, Marena, Ngo, Wayne, Doudna, Jennifer A
المصدر: Nature Biotechnology. 42(11)
مصطلحات موضوعية: Medical Biotechnology, Biomedical and Clinical Sciences, Immunology, Biotechnology, Genetics, Gene Therapy, Bioengineering, 1.1 Normal biological development and functioning, 5.2 Cellular and gene therapies, Generic health relevance, Humans, Animals, Mice, Gene Editing, T-Lymphocytes, CRISPR-Cas Systems, Cell Engineering, Genetic Vectors, Gene Transfer Techniques
وصف الملف: application/pdf
-
16Academic Journal
المؤلفون: Lessard, Samuel, Rimmelé, Pauline, Ling, Hui, Moran, Kevin, Vieira, Benjamin, Lin, Yi-Dong, Rajani, Gaurav, Hong, Vu, Reik, Andreas, Boismenu, Richard, Hsu, Ben, Chen, Michael, Cockroft, Bettina, Uchida, Naoya, Tisdale, John, Alavi, Asif, Krishnamurti, Lakshmanan, Abedi, Mehrdad, Galeon, Isobelle, Reiner, David, Wang, Lin, Ramezi, Anne, Rendo, Pablo, Walters, Mark, Levasseur, Dana, Peters, Robert, Harris, Timothy, Hicks, Alexandra
المصدر: Scientific Reports. 14(1)
مصطلحات موضوعية: Anemia, Sickle Cell, Fetal Hemoglobin, Humans, Gene Editing, Hematopoietic Stem Cells, Zinc Finger Nucleases, Female, Male, Adult, Hematopoietic Stem Cell Transplantation, Animals, Mice, Repressor Proteins
وصف الملف: application/pdf
-
17Academic Journal
المؤلفون: An, Meirui, Raguram, Aditya, Du, Samuel W, Banskota, Samagya, Davis, Jessie R, Newby, Gregory A, Chen, Paul Z, Palczewski, Krzysztof, Liu, David R
المصدر: Nature Biotechnology. 42(10)
مصطلحات موضوعية: Medical Biotechnology, Biomedical and Clinical Sciences, Gene Therapy, Genetics, Biotechnology, Ribonucleoproteins, Animals, Mice, Humans, Gene Editing, Virion, RNA, Guide, CRISPR-Cas Systems
وصف الملف: application/pdf
-
18Academic Journal
المؤلفون: Ligunas, Gloria D, Paniagua, German F, LaBelle, Jesselynn, Ramos-Martinez, Adela, Shen, Kyle, Gerlt, Emma H, Aguilar, Kaddy, Nguyen, Ngoc, Materna, Stefan C, Woo, Stephanie
مصطلحات موضوعية: Biochemistry and Cell Biology, Biological Sciences, Genetics, 1.1 Normal biological development and functioning, Generic health relevance, Zebrafish, Animals, Zebrafish Proteins, CRISPR-Cas Systems, Animals, Genetically Modified, Luminescent Proteins, Organ Specificity, Green Fluorescent Proteins, Gene Editing, Promoter Regions, Genetic, Tubulin, CRISPR-Cas, Protein tagging, Split fluorescent protein, Medical and Health Sciences, Developmental Biology, Biological sciences, Biomedical and clinical sciences, Health sciences
وصف الملف: application/pdf
-
19Academic Journal
المؤلفون: Karageorgiou, Charikleia, Gokcumen, Omer, Dennis, Megan Y
مصطلحات موضوعية: Biological Sciences, Bioinformatics and Computational Biology, Genetics, Human Genome, 1.1 Normal biological development and functioning, Generic health relevance, Humans, Animals, Evolution, Molecular, Genome, Human, Genomics, Genomic Structural Variation, Phenotype, Hominidae, Biological Evolution, Gene Editing, Developmental Biology, Biochemistry and cell biology
وصف الملف: application/pdf
-
20Academic Journal
المؤلفون: Mudde, Anne CA, Kuo, Caroline Y, Kohn, Donald B, Booth, Claire
المصدر: The Journal of Allergy and Clinical Immunology In Practice. 12(5)
مصطلحات موضوعية: Medical Biotechnology, Biomedical and Clinical Sciences, Pediatric, Genetics, Stem Cell Research, Biotechnology, Regenerative Medicine, Gene Therapy, Development of treatments and therapeutic interventions, 5.2 Cellular and gene therapies, Inflammatory and immune system, Humans, Gene Editing, Genetic Therapy, Animals, CRISPR-Cas Systems, Agammaglobulinemia, Severe Combined Immunodeficiency, Hematopoietic Stem Cell Transplantation, Gene editing, Inborn errors of immunity, CRISPR/Cas, Prime editing, Base editing, Immunology
وصف الملف: application/pdf