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1Academic Journal
المؤلفون: Garcia-Pavia, Pablo, Oręziak, Artur, Masri, Ahmad, Barriales-Villa, Roberto, Abraham, Theodore, Owens, Anjali, Jensen, Morten, Wojakowski, Wojciech, Seidler, Tim, Hagege, Albert, Lakdawala, Neal, Wang, Andrew, Wheeler, Matthew, Choudhury, Lubna, Balaratnam, Ganesh, Shah, Ashish, Fox, Shawna, Hegde, Sheila, Olivotto, Iacopo
مصطلحات موضوعية: Efficacy, Long-term outcomes, MAVA-LTE (EXPLORER cohort), Mavacamten, Obstructive hypertrophic cardiomyopathy, Safety
وصف الملف: application/pdf
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2Academic Journal
المؤلفون: Mora-Ayestaran, Nerea, Dispenzieri, Angela, Kristen, Arnt, Maurer, Mathew, Diemberger, Igor, Drachman, Brian, Grogan, Martha, Gupta, Pritam, Glass, Oliver, Amass, Leslie, Garcia-Pavia, Pablo
المصدر: JACC: Advances. 3(8)
مصطلحات موضوعية: age, amyloid, cardiomyopathy, sex differences
وصف الملف: application/pdf
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3Academic Journal
المؤلفون: González-Moreno, Juan, Dispenzieri, Angela, Grogan, Martha, Coelho, Teresa, Tournev, Ivailo, Waddington-Cruz, Márcia, Wixner, Jonas, Diemberger, Igor, Garcia-Pavia, Pablo, Chapman, Doug, Gupta, Pritam, Glass, Oliver, Amass, Leslie
المصدر: Cardiology and Therapy. 13(1)
مصطلحات موضوعية: Amyloidosis, Cardiomyopathy, Mixed phenotype, Polyneuropathy, THAOS, Transthyretin
وصف الملف: application/pdf
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4
المؤلفون: Shah, Sanjiv J., Fine, Nowell, Garcia-Pavia, Pablo, Klein, Allan, Fernandes, Fabio, Weissman, Neil, Maurer, Mathew, Boman, Kurt, Gundapaneni, Balarama, Sultan, Marla, Elliott, Perry
المصدر: JAMA cardiology. 9(1):25-34
وصف الملف: electronic
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5Academic Journal
المساهمون: Instituto de Salud Carlos III, European Regional Development Fund, European Social Fund, MCIN, Pro-CNIC Foundation, Severo Ochoa, NIH
المصدر: European Heart Journal ; ISSN 0195-668X 1522-9645
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6
المؤلفون: Coelho, Teresa, Dispenzieri, Angela, Grogan, Martha, Conceição, Isabel, Waddington-Cruz, Márcia, Kristen, Arnt V., Wixner, Jonas, Diemberger, Igor, Gonzalez-Moreno, Juan, Maurer, Mathew S., Planté-Bordeneuve, Violaine, Garcia-Pavia, Pablo, Tournev, Ivailo, Gonzalez-Costello, Jose, Cariou, Eve, González-Duarte, Alejandra, Glass, Oliver, Chapman, Doug, Amass, Leslie
المصدر: Amyloid. 30(4):445-448
وصف الملف: electronic
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7
المؤلفون: Suhr, Ole B., Grogan, Martha, Silva, Ana Martins da, Karam, Chafic, Garcia-Pavia, Pablo, Drachman, Brian, Zago, Wagner, Tripuraneni, Radhika, Kinney, Gene G.
المصدر: Amyloid.
مصطلحات موضوعية: Amyloidosis, ATTR, cardiomyopathy, monoclonal antibody, phase 1
وصف الملف: electronic
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8Academic Journal
المؤلفون: Van Linthout, Sophie, Stellos, Konstantinos, Giacca, Mauro, Bertero, Edoardo, Cannata, Antonio, Carrier, Lucie, Garcia-Pavia, Pablo, Ghigo, Alessandra, González, Arantxa, Haugaa, Kristina H, Imazio, Massimo, Lopes, Luis R, Most, Patrick, Pollesello, Piero, Schunkert, Heribert, Streckfuss-Bömeke, Katrin, Thum, Thomas, Tocchetti, Carlo Gabriele, Tschöpe, Carsten, van der Meer, Peter, van Rooij, Eva, Metra, Marco, Rosano, Giuseppe M C, Heymans, Stephane
المساهمون: Van Linthout, Sophie, Stellos, Konstantino, Giacca, Mauro, Bertero, Edoardo, Cannata, Antonio, Carrier, Lucie, Garcia-Pavia, Pablo, Ghigo, Alessandra, González, Arantxa, Haugaa, Kristina H, Imazio, Massimo, Lopes, Luis R, Most, Patrick, Pollesello, Piero, Schunkert, Heribert, Streckfuss-Bömeke, Katrin, Thum, Thoma, Tocchetti, Carlo Gabriele, Tschöpe, Carsten, van der Meer, Peter, van Rooij, Eva, Metra, Marco, Rosano, Giuseppe M C, Heymans, Stephane
مصطلحات موضوعية: Adeno‐associated viral vector, Gene editing, Gene replacement, Gene silencing, Gene therapy, Heart failure
Relation: journal:EUROPEAN JOURNAL OF HEART FAILURE; https://hdl.handle.net/11588/988377
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9Academic Journal
المؤلفون: Rader, Florian, Oręziak, Artur, Choudhury, Lubna, Saberi, Sara, Fermin, David, Wheeler, Matthew T., Abraham, Theodore P., Garcia-Pavia, Pablo, Zwas, Donna R., Masri, Ahmad, Olivotto, Iacopo
المساهمون: Rader, Florian, Oręziak, Artur, Choudhury, Lubna, Saberi, Sara, Fermin, David, Wheeler, Matthew T., Abraham, Theodore P., Garcia-Pavia, Pablo, Zwas, Donna R., Masri, Ahmad, Olivotto, Iacopo
Relation: https://resolver.sub.uni-goettingen.de/purl?gro-2/140329; S221317792300687X
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10Academic Journal
المؤلفون: Lee, Matthew M.Y., Masri, Ahmad, Nassif, Michael E., Barriales-Villa, Roberto, Abraham, Theodore P., Claggett, Brian L., Coats, Caroline J., Gimeno, Juan Ramón, Kulac, Ian J., Landsteiner, Isabela, Ma, Changsheng, Maron, Martin S., Olivotto, Iacopo, Owens, Anjali T., Solomon, Scott D., Veselka, Josef, Jacoby, Daniel L., Heitner, Stephen B., Kupfer, Stuart, Malik, Fady I., Meng, Lisa, Wohltman, Amy, Lewis, Gregory D., Wang, Andrew, Sherrid, Mark V, Kelly, Jacob P, Marian, Ali J, Owens, Anjali Tiku, Wever-Pinzon, Omar, Owens, David, Wheeler, Matthew T, Nagueh, Sherif F, Rader, Florian, McGrew, Frank A, Wong, Timothy, O'Neill, Thomas, Bach, Richard G, Martinez, Matthew, Lakdawala, Neal K, Collado, Elias, Turer, Aslan, Desai Y, Milind, Hussain, Zainal, Tower-Rader, Albree F, Hannawi, Bashar, Geske, Jeffrey, Saberi, Sara, Phelan, Dermot, Kramer, Christopher, Sarswat, Nitasha, Ahmad, Ferhaan, Choudhury, Lubna, Markowitz, Jeremy S, Sen, Sounok, Bering, Patrick, Maron, Martin S, Jani, Sandeep, Brinkley, Douglas, Naidu, Srihari, Maurer, Mathew S, Moss, Noah, Bilen, Ozlem, Silva Enciso, Jorge, Fraser, Robert, Akinboboye, Olakunle, Asher, Craig, Emani, Sitaramesh, Sharma, Abhinav, Fermin, David, Lyle, Melissa, Raymer, David, Darlington, Andrew, Resnic, Frederic, Nielsen, Christopher D, Metra, Marco, Musumeci, Beatrice, Emdin, Michele, Targetti, Mattia, Canepa, Marco, Michels, Michelle, Knackstedt, Christian, Amin, Ahmad S., Barriales Villa, Roberto, Garcia Pavia, Pablo, Gimeno Blanes, Juan Ramon, Hidalgo Urbano, Rafael Jesus, Rincon Diaz, Luis Miguel, Ripoll Vera, Tomas Vicente V, Garcia Alvarez, Ana, Zemanek, David, Jensen, MortenK, Mogensen, Jens, Thune, Jens J, Bundgaard, Henning, Charron, Philippe, Trochu, Jean-Noel, Habib, Gilbert, Lhermusier, Thibault, Reant, Patricia, Hagege, Albert A, Logeart, Damien, Mitrovic, Veselin, Edelmann, Frank, Seidler, Tim, Meder, Benjamin, Schulze, Paul Christian, Stoerk, Stefan, Bekfani, Tarek, Rassaf, Tienush, Merkely, Bela, Arad, Michael, Halabi, Majdi, Zwas, Donna, Piltz, Xavier, Paz, Offir, Habib, Manhal, Dudek, Dariusz, Oreziak, Artur, Wojakowski, Wojciech, Toste Batista, Alexandra M, Mesquita Bastos, Jose Adelino, Elliott, Perry M, Mahmod, Masliza, Coats, Caroline, Cooper, Robert, Bradlow, William, Pantazis, Antonios, Tome Esteban, Maria Teresa, McGinnis, Shaina, Campain, Joseph, Cocca-Spofford, Diane, Giverts, Ilya, Griskowitz, Catherine, Newlands, Chloe, Moreno, Fabely Moreno
وصف الملف: text
Relation: https://eprints.gla.ac.uk/342146/1/342146.pdf; Lee, M. M.Y. et al. (2024) Aficamten and cardiopulmonary exercise test performance: a substudy of the SEQUOIA-HCM randomized clinical trial. JAMA Cardiology , 9(11), pp. 990-1000. (doi:10.1001/jamacardio.2024.2781 ) (PMID:39230885)
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11Academic Journal
المؤلفون: Maron, Martin S., Masri, Ahmad, Nassif, Michael E., Barriales-Villa, Roberto, Abraham, Theodore P., Arad, Michael, Cardim, Nuno, Choudhury, Lubna, Claggett, Brian, Coats, Caroline J., Düngen, Hans-Dirk, Garcia-Pavia, Pablo, Hagège, Albert A., Januzzi, James L., Kulac, Ian, Lee, Matthew M.Y., Lewis, Gregory D., Ma, Chang-Sheng, Michels, Michelle, Oreziak, Artur, Owens, Anjali T., Spertus, John A., Solomon, Scott D., Tfelt-Hansen, Jacob, van Sinttruije, Marion, Veselka, Josef, Watkins, Hugh C., Jacoby, Daniel L., Heitner, Stephen B., Kupfer, Stuart, Malik, Fady I., Meng, Lisa, Wohltman, Amy, Olivotto, Iacopo
وصف الملف: text
Relation: https://eprints.gla.ac.uk/340385/1/340385.pdf; Maron, M. S. et al. (2024) Impact of aficamten on disease and symptom burden in obstructive hypertrophic cardiomyopathy results from SEQUOIA-HCM. Journal of the American College of Cardiology , 84(19), pp. 1821-1831. (doi:10.1016/j.jacc.2024.09.003 ) (PMID:39352339)
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12Academic Journal
المؤلفون: de Frutos, Fernando, Ochoa, Juan Pablo, Webster, Gregory, Jansen, Mark, Remior, Paloma, Rasmussen, Torsten B, Sabater-Molina, Maria, Barriales-Villa, Roberto, Girolami, Francesca, Cesar, Sergi, Fuentes-Canamero, M. Eugenia, Garcia-Roves, Reyes Alvarez, Wahbi, Karim, Limeres, Javier, Kubanek, Milos, Slieker, Martijn G, Sarquella-Brugada, Georgia, Abrams, Dominic J, Dooijes, Dennis, Dominguez, Fernando, Garcia-Pavia, Pablo
المصدر: Journal of the American Heart Association [online], 13(21), art. no. e036208, (2024-01-01)
مصطلحات موضوعية: dilated cardiomyopathy, genetics, MYH7, pediatric
Relation: https://pubmed.ncbi.nlm.nih.gov/39494569; https://doi.org/10.1161/JAHA.124.036208; https://zenodo.org/communities/ikem; https://zenodo.org/communities/cardia; oai:zenodo.org:14192403
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13Academic Journal
المؤلفون: Ochoa, Juan Pablo, Espinosa, M. Ángeles, Gayán-Ordas, Jara, Fernández-Valledor, Andrea, Gallego-Delgado, María, Tirón, Coloma, Lozano-Ibañez, Adrián, García Pinilla, José Manuel, Rodríguez-Palomares, José F., Larrañaga-Moreira, José María, Llamas-Gómez, Helena, Ripoll-Vera, Tomas, Braza-Boïls, Aitana, Vilches, Silvia, Méndez, Irene, Bascompte-Claret, Ramón, García-Álvarez, Ana, Villacorta, Eduardo, Fernandez-Lozano, Ignacio, Lara-Pezzi, Enrique, Garcia-Pavia, Pablo
مصطلحات موضوعية: Cardiac conduction disorders, Cardiomyopathy, Genetics, Pacemaker, Sudden cardiac death
Relation: Reproducció del document publicat a: https://doi.org/10.1016/j.jacep.2024.05.008; JACC: Clinical Electrophysiology, 2024, vol. 10, núm. 10, p. 2250-2260; https://doi.org/10.1016/j.jacep.2024.05.008; https://repositori.udl.cat/handle/10459.1/467042
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14Academic Journal
المؤلفون: Remior-Pérez, Paloma, Gómez-Molina, Miriam, García-Rodríguez, Daniel, Gallego-Delgado, María, Mohamed-Salem, Laroussi, de Haro-del Moral, Javier, Hernández-Terciado, Fernando, de Castro, Daniel, Eiros-Bachiller, Rocio, Dominguez, Fernando, Gonzalez-Lopez, Esther, Villacorta, Eduardo, Pascual-Figal, Domingo A., Garcia-Pavia, Pablo
المساهمون: Pfizer
المصدر: Canadian Journal of Cardiology ; ISSN 0828-282X
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15Academic JournalHypertrophic cardiomyopathy due to truncating variants in myosin binding protein C: a Spanish cohort
المؤلفون: Melendo-Viu, Maria, Salguero-Bodes, Rafael, Valverde-Gómez, María, Larrañaga-Moreira, Jose María, Barriales, Roberto, Díez-Lopez, Carles, Limeres Freire, Javier, Peña-Peña, Maria Luisa, Garcia Pavia, Pablo, Ripoll, Tomas, Climent-Payá, Vicente, Gallego Delgado, Maria, Zorio, Esther, Bermudez Jimenez, Francisco José, García-Pinilla, José Manuel, Méndez Fernández, Irene, Sabater-Molina, Maria, Perez Asensio, Ana, Marchán-Lopez, Álvaro, Arribas Ynsaurriaga, Fernando, Bueno, Hector, Palomino Doza, Julián A
المصدر: Open Heart ; volume 11, issue 2, page e002891 ; ISSN 2053-3624
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16Academic Journal
المؤلفون: de Frutos, Fernando, Saturi, Giulia, Gonzalez-Lopez, Esther, Sguazzotti, Maurizio, Dominguez, Fernando, Ponziani, Alberto, Cabrera-Romero, Eva, Caponetti, Angelo Giuseppe, Lozano, Sara, Massa, Paolo, Peiro-Aventin, Belen, Accietto, Antonella, Mora-Ayestarán, Nerea, Giovannetti, Alessandro, Castro-Urda, Victor, Gagliardi, Christian, Cobo-Marcos, Marta, Rios-Tamayo, Rafael, Biagini, Elena, Gomez-Bueno, Manuel, Galiè, Nazzareno, Segovia-Cubero, Javier, Longhi, Simone, Garcia-Pavia, Pablo
المساهمون: Instituto de Salud Carlos III, European Regional Development Fund/European Social Fund "A way to make Europe"/"Investing in your future", ISCIII, MCIN, the Pro‐CNIC Foundation, Severo Ochoa
المصدر: Amyloid ; volume 31, issue 4, page 334-338 ; ISSN 1350-6129 1744-2818
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17Academic Journal
المؤلفون: Coats, Caroline J., Maron, Martin S., Abraham, Theodore P., Olivotto, Iacopo, Lee, Matthew M.Y., Arad, Michael, Cardim, Nuno, Ma, Chang-Sheng, Choudhury, Lubna, Düngen, Hans-Dirk, Garcia-Pavia, Pablo, Hagège, Albert A., Lewis, Gregory D., Michels, Michelle, Oreziak, Artur, Owens, Anjali T., Tfelt-Hansen, Jacob, Veselka, Josef, Watkins, Hugh C., Heitner, Stephen B., Jacoby, Daniel L, Kupfer, Stuart, Malik, Fady I., Meng, Lisa, Wohltman, Amy, Masri, Ahmad, SEQUOIA-HCM Investigators
وصف الملف: text
Relation: https://eprints.gla.ac.uk/337079/1/337079.pdf; Coats, C. J. et al. (2024) Exercise capacity in patients with obstructive hypertrophic cardiomyopathy: SEQUOIA-HCM baseline characteristics and study design. JACC: Heart Failure , 12(1), pp. 199-215. (doi:10.1016/j.jchf.2023.10.004 ) (PMID:38032573)
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18Academic Journal
المؤلفون: Coats, Caroline J., Masri, Ahmad, Nassif, Michael E., Barriales‐Villa, Roberto, Arad, Michael, Cardim, Nuno, Choudhury, Lubna, Claggett, Brian, Düngen, Hans‐Dirk, Garcia‐Pavia, Pablo, Hagège, Albert A., Januzzi, James L., Lee, Matthew M. Y., Lewis, Gregory D., Ma, Chang‐Sheng, Maron, Martin S., Michael Miao, Zi, Michels, Michelle, Olivotto, Iacopo, Oreziak, Artur, Owens, Anjali T., Spertus, John A., Solomon, Scott D., Tfelt‐Hansen, Jacob, van Sinttruije, Marion, Veselka, Josef, Watkins, Hugh, Jacoby, Daniel L., German, Polina, Heitner, Stephen B., Kupfer, Stuart, Lutz, Justin D., Malik, Fady I., Meng, Lisa, Wohltman, Amy, Abraham, Theodore P., Zhang, Yuhui, Yang, Haibo, Shao, Chunli, Yuan, Zuyi, Zeng, Qingchun, Li, Xiaodong, Wang, Yushi, Shu, Yan, Chen, Mulei, Tao, Ling, Li, Xinli, Wang, Jingfeng, Yu, Zaixin, Cheng, Xiang, Hong, Kui, Zemanek, David, Bundgaard, Henning, Thune, Jens, Jensen, Morten, Mogensen, Jens, Habib, Gilbert, Charron, Philippe, Lhermusier, Thibault, Trochu, Jean‐Noël, Reant, Patricia, Logeart, Damien, Mitrovic, Veselin, Bekfani, Tarek, Edelmann, Frank, Seidler, Tim, Meder, Benjamin, Christian Schulze, Paul, Stoerk, Stephan, Rassaf, Tienush, Merkely, Bela, Zfat‐Zwas, Donna, Halabi, Majdi, Paz, Offir, Piltz, Xavier, Metra, Marco, Canepa, Marco, Musumeci, Beatrice, Emdin, Michele, Amin, Ahmad, Knackstedt, Christian, Wojakowski, Wojciech, Dudek, Dariusz, Toste, Alexandra, Mesquita Bastos, José, Ramón Gimeno Blanes, Juan, Jesus Hidalgo Urbano, Rafael, Garcia Alvarez, Ana, Miguel Rincón Diaz, Luis, Vicente Ripoll Vera, Tomas, Elliott, Perry, Greater Glasgow, NHS., Cooper, Rob, Heart, Liverpool, Mahmod, Masliza, Pantazis, Antonis, Teresa Tome Esteban, Maria, Health, Oregon, Marian, Ali, Owens, David, McGrew, Frank, Bach, Richard, Wever‐Pinzon, Omar, Collado, Elias, Turer, Aslan, Hannawi, Bashar, Geske, Jeffrey, Heart, Penn, Symanski, John, Heart, Sanger, Kramer, Christopher, Sarswat, Nitasha, Ahmad, Ferhaan, Markowitz, Jeremy, Lakdawala, Neal, Jani, Sandeep, Brinkley, Marshall, Bilen, Ozlem, Asher, Craig, Emani, Sitaramesh, Sharma, Abhinav, Fermin, David, Lyle, Melissa, Raymer, David, Darlington, Andrew, Nielsen, Christopher, Wang, Andrew, Nagueh, Sherif, Martinez, Matthew, Desai, Milind, Tower‐Rader, Albree, Kelly, Jacob, Heart, Alaska, Rader, Florian, Sen, Sounok, Bering, Patrick, Maurer, Mathew, Mitter, Sumeet, Sherrid, Mark, Wong, Timothy, Hussain, Zainal, Saberi, Sara, Naidu, Srihari, Silva Enciso, Jorge
وصف الملف: text
Relation: https://eprints.gla.ac.uk/337074/1/337074.pdf; Coats, C. J. et al. (2024) Dosing and safety profile of aficamten in symptomatic obstructive hypertrophic cardiomyopathy: results from from SEQUOIA‐HCM. Journal of the American Heart Association , 13(5), e035993. (doi:10.1161/JAHA.124.035993 ) (PMID:39056349)
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19Academic Journal
المؤلفون: Maron, Martin S., Masri, Ahmad, Nassif, Michael E., Barriales-Villa, Roberto, Abraham, Theodore P., Arad, Michael, Cardim, Nuno, Choudhury, Lubna, Claggett, Brian, Coats, Caroline J., Düngen, Hans Dirk, Garcia-Pavia, Pablo, Hagège, Albert A., Januzzi, James L., Kulac, Ian, Lee, Matthew M.Y., Lewis, Gregory D., Ma, Chang Sheng, Michels, Michelle, Oreziak, Artur, Owens, Anjali T., Spertus, John A., Solomon, Scott D., Tfelt-Hansen, Jacob, van Sinttruije, Marion, Veselka, Josef, Watkins, Hugh C., Jacoby, Daniel L., Heitner, Stephen B., Kupfer, Stuart, Malik, Fady I., Meng, Lisa, Wohltman, Amy, Olivotto, Iacopo
المصدر: Maron , M S , Masri , A , SEQUOIA‐HCM Investigators , Nassif , M E , Barriales-Villa , R , Abraham , T P , Arad , M , Cardim , N , Choudhury , L , Claggett , B , Coats , C J , Düngen , H D , Garcia-Pavia , P , Hagège , A A , Januzzi , J L , Kulac , I , Lee , M M Y , Lewis , G D , Ma , C S , Michels , M , Oreziak , A , Owens , A T , ....
وصف الملف: application/pdf
الاتاحة: https://pure.eur.nl/en/publications/95cbd5a2-f101-4229-af26-810da8baefd0
https://doi.org/10.1016/j.jacc.2024.09.003
https://pure.eur.nl/ws/files/171393041/Impact_of_Aficamten_on_Disease_and_Symptom_Burden_in_Obstructive_Hypertrophic_Cardiomyopathy.pdf
http://www.scopus.com/inward/record.url?scp=85206685901&partnerID=8YFLogxK -
20Academic Journal
المؤلفون: Fontana, Marianna, Berk, John L, Gillmore, Julian JD, Witteles, Ronald M, Grogan, Martha, Drachman, Brian, Damy, Thibaud, Garcia-Pavia, Pablo, Taubel, Jorg, Solomon, Scott D, Sheikh, Farooq FH, Tahara, Nobuhiro, González-Costello, José, Tsujita, Kenichi, Morbach, Caroline, Pozsonyi, Zoltán, Petrie, Mark C, Delgado, Diego, Van der Meer, Peter, Jabbour, Andrew, Bondue, Antoine, Kim, Darae, Azevedo, Olga, Hvitfeldt Poulsen, Steen, Yilmaz, Ali, Jankowska, Ewa A, Algalarrondo, Vincent, Slugg, Andrew, Garg, Pushkal P, Boyle, Katherine L, Yureneva, Elena, Silliman, Nancy, Yang, Lilli, Chen, Jihong, Eraly, Satish SA, Vest, John, Maurer, Mathew S, HELIOS-B Trial Investigators
المصدر: The New England journal of medicine
مصطلحات موضوعية: Cardiologie et circulation, Médecine interne
وصف الملف: 1 full-text file(s): application/pdf
Relation: uri/info:doi/10.1056/NEJMoa2409134; uri/info:pmid/39213194