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1Academic Journal
المؤلفون: Samantha L. Durfey, Sudhakar Pipavath, Anna Li, Anh T. Vo, Anina Ratjen, Suzanne Carter, Sarah J. Morgan, Matthew C. Radey, Brenda Grogan, Stephen J. Salipante, Michael J. Welsh, David A. Stoltz, Christopher H. Goss, Edward F. McKone, Pradeep K. Singh
المصدر: mBio, Vol 12, Iss 6 (2021)
مصطلحات موضوعية: CFTR modulator, cystic fibrosis, Pseudomonas aeruginosa, Staphylococcus aureus, lung infection, Microbiology, QR1-502
وصف الملف: electronic resource
Relation: https://doaj.org/toc/2150-7511
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2Academic Journal
المؤلفون: Sarah J. Morgan, Samantha L. Durfey, Sumedha Ravishankar, Peter Jorth, Wendy Ni, Duncan T. Skerrett, Moira L. Aitken, Edward F. McKone, Stephen J. Salipante, Matthew C. Radey, Pradeep K. Singh
المصدر: JCI Insight, Vol 6, Iss 24 (2021)
مصطلحات موضوعية: Infectious disease, Microbiology, Medicine
وصف الملف: electronic resource
Relation: https://doaj.org/toc/2379-3708
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3Academic Journal
المؤلفون: Andreas Jung, Annalisa Orenti, Fiona Dunlevy, Elina Aleksejeva, Egil Bakkeheim, Vladimir Bobrovnichy, Siobhán B. Carr, Carla Colombo, Harriet Corvol, Rebecca Cosgriff, Géraldine Daneau, Deniz Dogru, Pavel Drevinek, Andrea Dugac Vukic, Isabelle Fajac, Alice Fox, Stojka Fustik, Vincent Gulmans, Satenik Harutyunyan, Elpis Hatziagorou, Irena Kasmi, Hana Kayserová, Elena Kondratyeva, Uroš Krivec, Halyna Makukh, Kestutis Malakauskas, Edward F. McKone, Meir Mei-Zahav, Isabelle de Monestrol, Hanne Vebert Olesen, Rita Padoan, Tsitsino Parulava, Maria Dolores Pastor-Vivero, Luísa Pereira, Guergana Petrova, Andreas Pfleger, Liviu Pop, Jacqui G. van Rens, Milan Rodic´, Marc Schlesser, Valérie Storms, Oxana Turcu, Lukasz Woz´niacki, Panayiotis Yiallouros, Anna Zolin, Damian G. Downey, Lutz Naehrlich
المصدر: ERJ Open Research, Vol 7, Iss 4 (2021)
مصطلحات موضوعية: Medicine
وصف الملف: electronic resource
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4Academic Journal
المؤلفون: Katherine B. Hisert, Timothy P. Birkland, Kelly Q. Schoenfelt, Matthew E. Long, Brenda Grogan, Suzanne Carter, W. Conrad Liles, Edward F. McKone, Lev Becker, Anne M. Manicone, Sina A. Gharib
المصدر: Frontiers in Pharmacology, Vol 11 (2020)
مصطلحات موضوعية: cystic fibrosis, monocytes, ivacaftor, inflammation, transcriptome, Therapeutics. Pharmacology, RM1-950
وصف الملف: electronic resource
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5Academic Journal
المؤلفون: Katherine B. Hisert, Timothy P. Birkland, Kelly Q. Schoenfelt, Matthew E. Long, Brenda Grogan, Suzanne Carter, W. Conrad Liles, Edward F. McKone, Lev Becker, Anne M. Manicone
المصدر: ERJ Open Research, Vol 6, Iss 2 (2020)
مصطلحات موضوعية: Medicine
وصف الملف: electronic resource
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6Academic Journal
المؤلفون: Jennifer L. Taylor-Cousar, Marcus A. Mall, Bonnie W. Ramsey, Edward F. McKone, Elizabeth Tullis, Gautham Marigowda, Charlotte M. McKee, David Waltz, Samuel M. Moskowitz, Jessica Savage, Fengjuan Xuan, Steven M. Rowe
المصدر: ERJ Open Research, Vol 5, Iss 2 (2019)
مصطلحات موضوعية: Medicine
وصف الملف: electronic resource
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7
المؤلفون: Gregory S. Sawicki, Michael W. Konstan, Edward F. McKone, Richard B. Moss, Barry Lubarsky, Ellison Suthoff, Stefanie J. Millar, David J. Pasta, Nicole Mayer-Hamblett, Christopher H. Goss, Wayne J. Morgan, Margaret E. Duncan, Yoojung Yang
المصدر: Pulmonary Therapy. 8:385-395
مصطلحات موضوعية: Pulmonary and Respiratory Medicine, Respiratory Care
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8
المؤلفون: Suzanne C. Carter, Alessandro N. Franciosi, Kate M. O’Shea, Orla M. O’Carroll, Ashutosh Sharma, Aoife Bell, Brian Keogan, Paul O’Reilly, Suzie Coughlan, Sheonagh M. Law, Robert D. Gray, Katherine B. Hisert, Pradeep K. Singh, Gordon Cooke, Brenda Grogan, Cillian F. De Gascun, Charles G. Gallagher, Trevor T. Nicholson, Bradley S. Quon, Edward F. McKone
المصدر: Annals of the American Thoracic Society. 19:1818-1826
مصطلحات موضوعية: Inflammation, Pulmonary and Respiratory Medicine, C-Reactive Protein, Phenotype, Cystic Fibrosis, Disease Progression, Humans, Lung, Biomarkers, Anti-Bacterial Agents
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9
المؤلفون: Ahmet Z Uluer, Gordon MacGregor, Pilar Azevedo, Veronica Indihar, Claire Keating, Marcus A Mall, Edward F McKone, Bonnie W Ramsey, Steven M Rowe, Ronald C Rubenstein, Jennifer L Taylor-Cousar, Elizabeth Tullis, Lael M Yonker, Chenghao Chu, Anna P Lam, Nitin Nair, Patrick R Sosnay, Simon Tian, Fredrick Van Goor, Lakshmi Viswanathan, David Waltz, Linda T Wang, Yingmei Xi, Joanne Billings, Alexander Horsley, Edward F. Nash, Marleen Bakker, Renske van der Meer, Petrus Merkus, Christof Majoor, Karen McCoy, Krishna Pancham, James Tolle, Bryon Quick, Ahmet Uluer, Emily DiMango, Adupa Rao, Santiago Reyes, Ross Klingsberg, Celeste Barreto, Victor Ortega, Donna Willey-Courand, Carsten Schwarz, Sivagurunathan Sutharsan, Rainald Fischer, Jane Davies, Jamie Duckers, Simon Doe, Harry Heijerman, George M. Solomon, Christian Merlo, Jennifer Griffonnet, Joseph Pilewski, Jordan Dunitz, Saba Sheikh, Ronald C. Rubenstein, Daniel B. Rosenbluth, Theodore Liou, Maria Indihar, Lael Yonker, Samya Nasr, Cynthia D. Brown, Gregory S. Sawicki, Jennifer Ruddy, Bryan Garcia, Andrew Braun, Alex H. Gifford, Nighat Mehdi, Maria Tupayachi Ortiz, Raksha Jain, Francisco J. Calimano, Jimmy Johannes, Cori L. Daines, Jason Fullmer, Joel Mermis, Christopher Barrios, Ngoc Ly, Brian P. Casserly, Stephan Eisenmann, Helge Hebestreit, Alexander Kiefer, Daniel Peckham, Martin Ledson, Eva Van Braeckel, Noel Gerard McElvaney, Edward McKone, Barry Plant, Lucy Burr, Daniel J. Smith, Peter Middleton, John Wilson
المساهمون: VU University medical center
المصدر: The Lancet Respiratory Medicine, 11(6), 550-562. Elsevier Limited
VX18-121-101 & VX18-561-101 Study Groups 2023, ' Safety and efficacy of vanzacaftor–tezacaftor–deutivacaftor in adults with cystic fibrosis : randomised, double-blind, controlled, phase 2 trials ', The Lancet Respiratory Medicine, vol. 11, no. 6, pp. 550-562 . https://doi.org/10.1016/S2213-2600(22)00504-5
LANCET RESPIRATORY MEDICINEمصطلحات موضوعية: Pulmonary and Respiratory Medicine, Medicine and Health Sciences
وصف الملف: application/pdf
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المصدر: Journal of Cystic Fibrosis. 21:562-573
مصطلحات موضوعية: Pulmonary and Respiratory Medicine, Spirometry, medicine.medical_specialty, Cystic Fibrosis, biology, medicine.diagnostic_test, business.industry, C-reactive protein, MEDLINE, Odds ratio, medicine.disease, Cystic fibrosis, Anti-Bacterial Agents, Clinical trial, Systematic review, Forced Expiratory Volume, Internal medicine, Pediatrics, Perinatology and Child Health, biology.protein, Humans, Medicine, Administration, Intravenous, Observational study, business
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11
المؤلفون: Edward F. McKone, Chenghao Chu, Claire E. Wainwright, Neil Ahluwalia, Samuel M. Moskowitz, Paul McNally, Edith T. Zemanick, Ronald L. Gibson, Jane Davies, Fengjuan Xuan, Steven M. Rowe, Tanya G. Weinstock, Bonnie W. Ramsey, Elizabeth Tullis, Susanna A McColley, David Waltz, S. Tian, Thang Ho, Jonathan H. Rayment, Sabrina Noel, Marcus A. Mall, Jennifer L. Taylor-Cousar
المصدر: American Journal of Respiratory and Critical Care Medicine. 203:1522-1532
مصطلحات موضوعية: Pulmonary and Respiratory Medicine, congenital, hereditary, and neonatal diseases and abnormalities, medicine.medical_specialty, business.industry, Critical Care and Intensive Care Medicine, medicine.disease, Cystic fibrosis, Gastroenterology, Ivacaftor, Open label study, Internal medicine, medicine, Tezacaftor, In patient, Allele, business, medicine.drug
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12
المؤلفون: Elizabeth Tullis, Sivagurunathan Sutharsan, Daniel Campbell, Neil Ahluwalia, Mark Higgins, Tara Lynn Barto, Emily DiMango, Caroline A. Owen, Edward F. McKone
المصدر: Journal of Cystic Fibrosis. 20:234-242
مصطلحات موضوعية: Adult, Male, Pulmonary and Respiratory Medicine, Heterozygote, medicine.medical_specialty, Indoles, Adolescent, Cystic Fibrosis, Medizin, Cystic Fibrosis Transmembrane Conductance Regulator, Phases of clinical research, Quinolones, Aminophenols, Cystic fibrosis, Gastroenterology, Ivacaftor, Double-Blind Method, Pharmacokinetics, Internal medicine, medicine, Clinical endpoint, Humans, Benzodioxoles, Chloride Channel Agonists, biology, business.industry, medicine.disease, Cystic fibrosis transmembrane conductance regulator, Respiratory Function Tests, Clinical trial, Drug Combinations, Regimen, Mutation, Pediatrics, Perinatology and Child Health, biology.protein, Female, sense organs, business, Ion Channel Gating, medicine.drug
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13
المؤلفون: Matthias Griese, Deepika Polineni, Jennifer L. Taylor-Cousar, Edward F. McKone, Samuel M. Moskowitz, Stefano Costa, Cori L. Daines, Felix C. Ringshausen, Marcus A. Mall, Nicholas J. Withers, Rachel W. Linnemann, Bradley S. Quon
المصدر: American Journal of Respiratory and Critical Care Medicine
مصطلحات موضوعية: Pulmonary and Respiratory Medicine, medicine.medical_specialty, business.industry, Phases of clinical research, Critical Care and Intensive Care Medicine, medicine.disease, Cystic fibrosis, law.invention, Ivacaftor, Clinical trial, Pharmacotherapy, Randomized controlled trial, law, Interim, Internal medicine, Correspondence, medicine, Young adult, business, medicine.drug
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14
المؤلفون: Holly Davage, Barry Linnane, Hilary Cassidy, Anne Trappe, Seamas C. Donnelly, Sarah L. Doyle, Edward F. McKone, Judith A. Coppinger, Eugene T. Dillon, Rebecca Reilly, Zivile Useckaite, Jenny Lennon, David Matallanas, Kiva Brennan, Paul McNally, S. Carter, Mark Ward
المصدر: Thorax
مصطلحات موضوعية: Adult, Male, Pulmonary and Respiratory Medicine, Adolescent, Cystic Fibrosis, Neutrophils, Regulator, Cystic Fibrosis Transmembrane Conductance Regulator, Nanoparticle tracking analysis, Pilot Projects, Inflammation, Transfection, Cystic fibrosis, Mass Spectrometry, Cell Line, Extracellular Vesicles, 03 medical and health sciences, 0302 clinical medicine, Cell Movement, medicine, Humans, Child, Gene, Cells, Cultured, 030304 developmental biology, 0303 health sciences, medicine.diagnostic_test, business.industry, Chemotaxis, Age Factors, Infant, neutrophil biology, medicine.disease, Molecular biology, Transmembrane protein, Bronchoalveolar lavage, Signalling, Child, Preschool, Nanoparticles, Female, medicine.symptom, paediatric lung disaese, business, Bronchoalveolar Lavage Fluid, Signal Transduction, 030215 immunology
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15
المؤلفون: Sivagurunathan Sutharsan, Edward F McKone, Damian G Downey, Jamie Duckers, Gordon MacGregor, Elizabeth Tullis, Eva Van Braeckel, Claire E Wainwright, Danie Watson, Neil Ahluwalia, Bote G Bruinsma, Christopher Harris, Anna P Lam, Yiyue Lou, Samuel M Moskowitz, Simon Tian, Jason Yuan, David Waltz, Marcus A Mall, Paul Aurora, Stijn Verhulst, Michael Lorenz, Jobst Roehmel, Wolfgang Gleiber, Susanne Naehrig, Florian Stehling, Silke van Koningsbruggen-Rietschel, Rainald Fischer, Damian Downey, Charles Haworth, Julian Legg, Peter Barry, Rebecca Thursfield, Simon James Doe, Tom Hilliard, Edward F Nash, Nicholas John Withers, Daniel Peckham, Helen Louise Barr, Timothy Lee, Robert Gray, Francois Vermeulen, Eef Vanderhelst, Philip J Robinson, Daniel J Smith, Siobhain A Mulrennan, Barry S Clements, Peter Wark
المساهمون: Aurora, Paul (Beitragende*r), Verhulst, Stijn (Beitragende*r), Lorenz, Michael (Beitragende*r), Roehmel, Jobst (Beitragende*r), Gleiber, Wolfgang (Beitragende*r), Naehrig, Susanne (Beitragende*r), Stehling, Florian (Beitragende*r), van Koningsbruggen-Rietschel, Silke (Beitragende*r), Fischer, Rainald (Beitragende*r), Haworth, Charles (Beitragende*r), Legg, Julian (Beitragende*r), Barry, Peter (Beitragende*r), Thursfield, Rebecca (Beitragende*r), Doe, Simon James (Beitragende*r), Hilliard, Tom (Beitragende*r), Nash, Edward F (Beitragende*r), Withers, Nicholas John (Beitragende*r), Peckham, Daniel (Beitragende*r), Barr, Helen Louise (Beitragende*r), Lee, Timothy (Beitragende*r), Gray, Robert (Beitragende*r), Vermeulen, Francois (Beitragende*r), Vanderhelst, Eef (Beitragende*r), Robinson, Philip J (Beitragende*r), Smith, Daniel J (Beitragende*r), Mulrennan, Siobhain A (Beitragende*r), Clements, Barry S (Beitragende*r), Wark, Peter (Beitragende*r), Physiotherapy, Human Physiology and Anatomy, Clinical sciences, Pneumology
المصدر: VX18-445-109 study group 2021, ' Efficacy and safety of elexacaftor plus tezacaftor plus ivacaftor versus tezacaftor plus ivacaftor in people with cystic fibrosis homozygous for F508del-CFTR: a 24-week, multicentre, randomised, double-blind, active-controlled, phase 3b trial ', The Lancet. Respiratory medicine . https://doi.org/10.1016/S2213-2600(21)00454-9
مصطلحات موضوعية: Pulmonary and Respiratory Medicine, Indoles, Pyrrolidines, F508del-CFTR allele, Cystic Fibrosis, aged 12 years or older, Pyridines, Medizin, Cystic Fibrosis Transmembrane Conductance Regulator, Quinolones, Aminophenols, Double-Blind Method, Mutation, Quality of Life, Humans, Pyrazoles, cystic fibrosis transmembrane conductance regulator (CFTR), Benzodioxoles, Child, Chloride Channel Agonists
وصف الملف: application/pdf
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16Priority areas in the assessment and treatment of CF exacerbations: Location, duration, inflammation
المؤلفون: Suzanne C, Carter, Edward F, McKone
المصدر: Journal of Cystic Fibrosis. 21:556-557
مصطلحات موضوعية: Inflammation, Pulmonary and Respiratory Medicine, Cystic Fibrosis, Pediatrics, Perinatology and Child Health, Disease Progression, Humans, Anti-Bacterial Agents
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17
المؤلفون: Harry G M Heijerman, Edward F McKone, Damian G Downey, Eva Van Braeckel, Steven M Rowe, Elizabeth Tullis, Marcus A Mall, John J Welter, Bonnie W Ramsey, Charlotte M McKee, Gautham Marigowda, Samuel M Moskowitz, David Waltz, Patrick R Sosnay, Christopher Simard, Neil Ahluwalia, Fengjuan Xuan, Yaohua Zhang, Jennifer L Taylor-Cousar, Karen S McCoy, Karen McCoy, Scott Donaldson, Seth Walker, James Chmiel, Ronald Rubenstein, Deborah K. Froh, Isabel Neuringer, Manu Jain, Kathryn Moffett, Jennifer L. Taylor-Cousar, Bruce Barnett, Gary Mueller, Patrick Flume, Floyd Livingston, Nighat Mehdi, Charlotte Teneback, John Welter, Raksha Jain, Dana Kissner, Kapilkumar Patel, Francisco J. Calimano, Jimmy Johannes, Cori Daines, Thomas Keens, Herschel Scher, Subramanyam Chittivelu, Sudhakar Reddivalam, Ross Carl Klingsberg, Larry G. Johnson, Stijn Verhulst, Patricia Macedo, Damien Downey, Gary Connett, Edward Nash, Nicholas Withers, Timothy Lee, Marleen Bakker, Harry Heijerman, Francois Vermeulen, Christiane Knoop, Elke De Wachter, Renske van der Meer, Petrus Merkus, Christof Majoor
المساهمون: Pulmonology, AII - Inflammatory diseases, Clinical sciences, Physiotherapy, Human Physiology and Anatomy, Pediatrics
المصدر: Lancet, 394(10212), 1940-1948. Elsevier Limited
VX17-445-103 Trial Group 2019, ' Efficacy and safety of the elexacaftor plus tezacaftor plus ivacaftor combination regimen in people with cystic fibrosis homozygous for the F508del mutation: a double-blind, randomised, phase 3 trial ', Lancet, vol. 394, no. 10212, pp. 1940 . https://doi.org/10.1016/S0140-6736(19)32597-8
Lancet
The Lancet, 394(10212), 1940. Elsevier Limitedمصطلحات موضوعية: Male, Indoles, Pyrrolidines, Cystic Fibrosis, Pyridines, Clinical Trial, Phase III, Phases of clinical research, Cystic Fibrosis Transmembrane Conductance Regulator, 030204 cardiovascular system & hematology, Quinolones, Aminophenols, Cystic fibrosis, law.invention, Ivacaftor, chemistry.chemical_compound, 0302 clinical medicine, Randomized controlled trial, law, 030212 general & internal medicine, Pyridines/administration & dosage, Non-U.S. Gov't, Chloride Channel Agonists, Sweat, Child, Chloride Channel Agonists/administration & dosage, Medicine(all), biology, Research Support, Non-U.S. Gov't, Lumacaftor, General Medicine, Indoles/administration & dosage, Clinical Trial, Cystic fibrosis transmembrane conductance regulator, Pyrrolidines/administration & dosage, Quinolones/administration & dosage, Randomized Controlled Trial, Combination, Drug Therapy, Combination, Female, medicine.drug, medicine.medical_specialty, Adolescent, Research Support, Article, Benzodioxoles/administration & dosage, Sweat/chemistry, N.I.H, 03 medical and health sciences, Phase III, Research Support, N.I.H., Extramural, Double-Blind Method, Drug Therapy, Internal medicine, Journal Article, medicine, Aminophenols/administration & dosage, Humans, Benzodioxoles, business.industry, Extramural, medicine.disease, Pyrazoles/administration & dosage, Clinical trial, Regimen, chemistry, biology.protein, Pyrazoles, Cystic Fibrosis Transmembrane Conductance Regulator/genetics, sense organs, Cystic Fibrosis/drug therapy, business
وصف الملف: application/pdf; text/plain
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18
المؤلفون: Herman de Kock, D. Kanters, Florence Namour, Katja Conrath, Olivier Van de Steen, Pavel Drevinek, Edward F. McKone, Nico Derichs, Jane C. Davies, Silke van Koningsbruggen-Rietschel, Lisa Allamassey
المصدر: Journal of Cystic Fibrosis. 18:693-699
مصطلحات موضوعية: Male, 0301 basic medicine, Cystic Fibrosis, Respiratory System, Cystic Fibrosis Transmembrane Conductance Regulator, Quinolones, Aminophenols, Cystic fibrosis, Ivacaftor, 0302 clinical medicine, Chloride Channel Agonists, Sweat, G551D, medicine.diagnostic_test, biology, Drug Substitution, Cystic fibrosis transmembrane conductance regulator, Respiratory Function Tests, Treatment Outcome, Female, Drug Monitoring, Gating mutation, medicine.drug, Adult, Pulmonary and Respiratory Medicine, Spirometry, medicine.medical_specialty, 03 medical and health sciences, Pharmacokinetics, Internal medicine, medicine, Humans, Adverse effect, CFTR modulator, Pyrans, Dose-Response Relationship, Drug, business.industry, 1103 Clinical Sciences, Potentiator, medicine.disease, Clinical trial, GLPG1837, 030104 developmental biology, Withholding Treatment, 030228 respiratory system, Pediatrics, Perinatology and Child Health, biology.protein, Pyrazoles, business
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المؤلفون: Despo Ierodiakonou, Scott T. Weiss, Joel Schwartz, Damien C. Croteau-Chonka, Brent A. Coull, Antonella Zanobetti, Petros Koutrakis, H. Marike Boezen, Diane R. Gold, Jonathan S. Schildcrout, Dirkje S. Postma, Thomas Lumley, Judith M. Vonk, Edward F. McKone, Gerard H. Koppelman
المساهمون: Groningen Research Institute for Asthma and COPD (GRIAC), Life Course Epidemiology (LCE)
المصدر: Journal of exposure science & environmental epidemiology, 29(4), 539-547. Nature Publishing Group
مصطلحات موضوعية: medicine.medical_specialty, Epidemiology, CITY, Air pollution, CYCLASE-ACTIVATING PEPTIDE, Locus (genetics), Single-nucleotide polymorphism, Genome-wide association study, 030501 epidemiology, Biology, Toxicology, Biological pathway, 03 medical and health sciences, INFLAMMATION, Molecular genetics, medicine, Genome-wide, EXPOSURE, OXIDATIVE STRESS, Pathways, Gene, Genetic association, Genetics, SET ENRICHMENT ANALYSIS, Public Health, Environmental and Occupational Health, ASSOCIATION, Pollution, Asthma, Gene-environment interaction, Lung function, LUNG-FUNCTION, Metabolic pathway, RESPIRATORY SYMPTOMS, HEALTH, 0305 other medical science
وصف الملف: application/pdf
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20
المؤلفون: Kathleen J. Ramos, E. Tallarico, Amy Lucy, Edward F. McKone, Sarah E. Hempstead, Patrick Smith, Daniel B. Rosenbluth, Albert Faro, Joseph M. Pilewski, Alice L. Gray, Jordan M. Dunitz
المصدر: J Cyst Fibros
مصطلحات موضوعية: 0301 basic medicine, Pulmonary and Respiratory Medicine, medicine.medical_specialty, Cystic Fibrosis, Referral, medicine.medical_treatment, Cystic fibrosis, Article, 03 medical and health sciences, 0302 clinical medicine, medicine, Humans, Lung transplantation, Guideline development, Intensive care medicine, Referral and Consultation, Lung, business.industry, Patient Selection, Foundation (evidence), medicine.disease, Focus group, surgical procedures, operative, 030104 developmental biology, medicine.anatomical_structure, 030228 respiratory system, Transplant referral, Practice Guidelines as Topic, Pediatrics, Perinatology and Child Health, business, Decision Making, Shared, Lung Transplantation