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1Academic Journal
المؤلفون: Servais, Laurent, Strijbos, Paul, Poleur, Margaux, Mirea, Andrada, Butoianu, Nina, Sansone, Valeria A, Vuillerot, Carole, Schara-Schmidt, Ulrike, Scoto, Mariacristina, Seferian, Andreea M, Previtali, Stefano C, Tulinius, Már, Nascimento, Andrés, Furlong, Pat, Singh, Teji, Dreghici, Roxana Donisa, Goemans, Nathalie, Mercuri, Eugenio, Straub, Volker, Ormazabal, Maitea Guridi, Braid, Jessica, Muntoni, Francesco, Tricot, Alexis, Annoussamy, Mélanie, Eggenspieler, Damien
المصدر: Scientific Reports, 14 (1), 29681 (2024-11-29)
مصطلحات موضوعية: Digital endpoints, Duchenne muscular dystrophy, Regulatory qualification, Stride Velocity 95th Centile, V3 framework, Wearables, Humans, Adolescent, Child, Child, Preschool, Male, Wearable Electronic Devices, Disease Progression, Outcome Assessment, Health Care/methods, Treatment Outcome, Clinical Trials as Topic, Endpoint Determination, Muscular Dystrophy, Duchenne/drug therapy, Human health sciences, Pediatrics, Sciences de la santé humaine, Pédiatrie
Relation: https://www.nature.com/articles/s41598-024-80177-9.pdf; urn:issn:2045-2322
URL الوصول: https://orbi.uliege.be/handle/2268/324960
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2Academic Journal
المصدر: Cell and Gene Therapy Insights ; volume 08, issue 01, page 129-140 ; ISSN 2059-7800 2059-7800