المؤلفون: Mets, Toomas, Kurata, Tatsuaki, Ernits, Karin, Johansson, Marcus J O, Craig, Sophie Z, Evora, Gabriel Medina, Buttress, Jessica A, Odai, Roni, Wallant, Kyo Coppieters't, Nakamoto, Jose A, Shyrokova, Lena, Egorov, Artyom A, Doering, Christopher Ross, Brodiazhenko, Tetiana, Laub, Michael T, Tenson, Tanel, Strahl, Henrik, Martens, Chloe, Harms, Alexander, Garcia-Pino, Abel, Atkinson, Gemma C, Hauryliuk, Vasili

المصدر: Cell Host and Microbe eSSENCE: The e-Science Collaboration. 32(7):8-1073

مصطلحات موضوعية: Medicin och hälsovetenskap, Medicinska och farmaceutiska grundvetenskaper, Cell- och molekylärbiologi, Medical and Health Sciences, Basic Medicine, Cell and Molecular Biology, Immunologi inom det medicinska området, Immunology in the medical area

URL الوصول: https://lup.lub.lu.se/record/90498675-3e13-470e-8378-993b712ebe62
http://dx.doi.org/10.1016/j.chom.2024.05.003

المؤلفون: Vassallo, Christopher N., Doering, Christopher R., Littlehale, Megan L., Teodoro, Gabriella I. C., Laub, Michael T.

المصدر: Nature Microbiology ; volume 9, issue 10, page 2760-2761 ; ISSN 2058-5276

الاتاحة: https://doi.org/10.1038/s41564-024-01724-8
https://www.nature.com/articles/s41564-024-01724-8.pdf
https://www.nature.com/articles/s41564-024-01724-8

المؤلفون: Vassallo, Christopher N., Doering, Christopher R., Laub, Michael T.

المصدر: Nature ; volume 636, issue 8041, page 190-197 ; ISSN 0028-0836 1476-4687

الاتاحة: https://doi.org/10.1038/s41586-024-08102-8
https://www.nature.com/articles/s41586-024-08102-8.pdf
https://www.nature.com/articles/s41586-024-08102-8

المؤلفون: Parwani, Kiran K., Branella, Gianna M., Burnham, Rebecca E., Burnham, Andre J., Bustamante, Austre Y. Schiaffino, Foppiani, Elisabetta Manuela, Knight, Kristopher A., Petrich, Brian G., Horwitz, Edwin M., Doering, Christopher B., Spencer, H. Trent

المصدر: Frontiers in Immunology ; volume 15 ; ISSN 1664-3224

الاتاحة: http://dx.doi.org/10.3389/fimmu.2024.1331322
https://www.frontiersin.org/articles/10.3389/fimmu.2024.1331322/full

المؤلفون: Coyle, Christopher W., Knight, Kristopher A., Brown, Harrison C., George, Stephan N., Denning, Gabriela, Branella, Gianna M., Childers, Kenneth C., Spiegel, P. Clint, Spencer, H. Trent, Doering, Christopher B.

المساهمون: National Hemophilia Foundation, NHLBI, Hemophilia of Georgia

المصدر: Journal of Thrombosis and Haemostasis ; volume 22, issue 3, page 633-644 ; ISSN 1538-7836

الاتاحة: http://dx.doi.org/10.1016/j.jtha.2023.11.010
https://api.elsevier.com/content/article/PII:S1538783623008486?httpAccept=text/xml
https://api.elsevier.com/content/article/PII:S1538783623008486?httpAccept=text/plain

المؤلفون: Rodriguez, Martin, Trevisan, Brady, Ramamurthy, Ritu M., George, Sunil K., Diaz, Jonathan, Alexander, Jordan, Meares, Diane, Schwahn, Denise J., Quilici, David R., Figueroa, Jorge, Gautreaux, Michael, Farland, Andrew, Atala, Anthony, Doering, Christopher B., Spencer, H. Trent, Porada, Christopher D., Almeida-Porada, Graça

المساهمون: U.S. Department of Health & Human Services | NIH | National Heart, Lung, and Blood Institute, U.S. Department of Health & Human Services | NIH | National Institute of General Medical Sciences, Howard Hughes Medical Institute, U.S. Department of Health & Human Services | NIH | National Institute of Biomedical Imaging and Bioengineering

المصدر: Nature Communications ; volume 14, issue 1 ; ISSN 2041-1723

الاتاحة: http://dx.doi.org/10.1038/s41467-023-39986-1
https://www.nature.com/articles/s41467-023-39986-1.pdf
https://www.nature.com/articles/s41467-023-39986-1

المؤلفون: Guegler, Chantal K, Teodoro, Gabriella I C, Srikant, Sriram, Chetlapalli, Keerthana, Doering, Christopher R, Ghose, Dia A, Laub, Michael T

المساهمون: NSF, Howard Hughes Medical Institute Gilliam Fellowship, Merck Fellow of the Jane Coffin Childs Fund for Medical Research, Life Sciences Research Foundation, Howard Hughes Medical Institute

المصدر: Nucleic Acids Research ; volume 52, issue 3, page 1298-1312 ; ISSN 0305-1048 1362-4962

مصطلحات موضوعية: Genetics

الاتاحة: http://dx.doi.org/10.1093/nar/gkad1207
https://academic.oup.com/nar/article-pdf/52/3/1298/56640578/gkad1207.pdf

المؤلفون: Branella, Gianna M., Lee, Jasmine Y., Okalova, Jennifer, Parwani, Kiran K., Alexander, Jordan S., Arthuzo, Raquel F., Fedanov, Andrew, Yu, Bing, McCarty, David, Brown, Harrison C., Chandrakasan, Shanmuganathan, Petrich, Brian G., Doering, Christopher B., Spencer, H. Trent

المساهمون: Curing Kids Cancer, National Institutes of Health

المصدر: Frontiers in Immunology ; volume 14 ; ISSN 1664-3224

الاتاحة: http://dx.doi.org/10.3389/fimmu.2023.1294555
https://www.frontiersin.org/articles/10.3389/fimmu.2023.1294555/full

المؤلفون: Becker, Scott A., Petrich, Brian G., Yu, Bing, Knight, Kristopher A., Brown, Harrison C., Raikar, Sunil S., Doering, Christopher B., Spencer, H. Trent

المساهمون: Emory University, Curing Kids Cancer, National Institutes of Health

المصدر: Molecular Therapy - Oncolytics ; volume 29, page 145-157 ; ISSN 2372-7705

الاتاحة: http://dx.doi.org/10.1016/j.omto.2023.05.007
https://api.elsevier.com/content/article/PII:S2372770523000402?httpAccept=text/xml
https://api.elsevier.com/content/article/PII:S2372770523000402?httpAccept=text/plain

المؤلفون: Lee, Jasmine Y., Jonus, Hunter C., Sadanand, Arhanti, Branella, Gianna M., Maximov, Victor, Suttapitugsakul, Suttipong, Schniederjan, Matthew J., Shim, Jenny, Ho, Andrew, Parwani, Kiran K., Fedanov, Andrew, Pilgrim, Adeiye A., Silva, Jordan A., Schnepp, Robert W., Doering, Christopher B., Wu, Ronghu, Spencer, H. Trent, Goldsmith, Kelly C.

المساهمون: CURE Childhood Cancer, Children's Healthcare of Atlanta, Curing Kids Cancer, National Institutes of Health, Alex's Lemonade Stand Foundation for Childhood Cancer

المصدر: Cell Reports Medicine ; volume 4, issue 6, page 101091 ; ISSN 2666-3791

الاتاحة: http://dx.doi.org/10.1016/j.xcrm.2023.101091
https://api.elsevier.com/content/article/PII:S2666379123002100?httpAccept=text/xml
https://api.elsevier.com/content/article/PII:S2666379123002100?httpAccept=text/plain

المؤلفون: Kumar, Sandeep R .P., Xie, Jun, Hu, Shilang, Ko, Jihye, Huang, Qifeng, Brown, Harrison C., Srivastava, Alok, Markusic, David M., Doering, Christopher B., Spencer, H. Trent, Srivastava, Arun, Gao, Guangping, Herzog, Roland W.

المساهمون: Li Weibo Institute for Rare Diseases Research, Department of Microbiology and Physiological Systems, Horae Gene Therapy Center

المصدر: Molecular therapy. Methods and clinical development ; 23 ; 98-107

مصطلحات موضوعية: AAV, adeno-associated virus, antibodies, capsid, factor IX, hemophilia, immune response, liver, non-human primate, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Immunology and Infectious Disease, Molecular Biology, Therapeutics

Relation: Link to Article in PubMed; Kumar SRP, Xie J, Hu S, Ko J, Huang Q, Brown HC, Srivastava A, Markusic DM, Doering CB, Spencer HT, Srivastava A, Gao G, Herzog RW. Coagulation factor IX gene transfer to non-human primates using engineered AAV3 capsid and hepatic optimized expression cassette. Mol Ther Methods Clin Dev. 2021 Aug 26;23:98-107. doi:10.1016/j.omtm.2021.08.001. PMID: 34631930; PMCID: PMC8476648. Link to article on publisher's site; 2329-0501 (Linking); http://hdl.handle.net/20.500.14038/42100; https://escholarship.umassmed.edu/cgi/viewcontent.cgi?article=5935&context=oapubs&unstamped=1; https://escholarship.umassmed.edu/oapubs/4901; oapubs/4901

الاتاحة: https://doi.org/10.1016/j.omtm.2021.08.001
https://hdl.handle.net/20.500.14038/42100
https://escholarship.umassmed.edu/cgi/viewcontent.cgi?article=5935&context=oapubs&unstamped=1
https://escholarship.umassmed.edu/oapubs/4901

المؤلفون: Vassallo, Christopher N., Doering, Christopher R., Littlehale, Megan L., Teodoro, Gabriella I. C., Laub, Michael T.

المساهمون: U.S. Department of Health & Human Services | National Institutes of Health, Howard Hughes Medical Institute

المصدر: Nature Microbiology ; volume 7, issue 10, page 1568-1579 ; ISSN 2058-5276

الاتاحة: http://dx.doi.org/10.1038/s41564-022-01219-4
https://www.nature.com/articles/s41564-022-01219-4.pdf
https://www.nature.com/articles/s41564-022-01219-4

المؤلفون: Jonus, Hunter C., Burnham, Rebecca E., Ho, Andrew, Pilgrim, Adeiye A., Shim, Jenny, Doering, Christopher B., Spencer, H. Trent, Goldsmith, Kelly C.

المساهمون: National Institutes of Health, Rally Foundation

المصدر: OncoImmunology ; volume 11, issue 1 ; ISSN 2162-402X

الاتاحة: http://dx.doi.org/10.1080/2162402x.2022.2057012
https://www.tandfonline.com/doi/pdf/10.1080/2162402X.2022.2057012

المؤلفون: Patel, Seema R., Lundgren, Taran S., Baldwin, Wallace Hunter, Cox, Courtney, Parker, Ernest T., Healey, John F., Jajosky, Ryan P., Zerra, Patricia E., Josephson, Cassandra D., Doering, Christopher B., Stowell, Sean R., Meeks, Shannon L.

المساهمون: National Institutes of Health, Hemophilia of Georgia, National Hemophilia Foundation

المصدر: Frontiers in Immunology ; volume 13 ; ISSN 1664-3224

الاتاحة: http://dx.doi.org/10.3389/fimmu.2022.880829
https://www.frontiersin.org/articles/10.3389/fimmu.2022.880829/full

المؤلفون: Ramamurthy, Ritu M., Rodriguez, Martin, Ainsworth, Hannah C., Shields, Jordan, Meares, Diane, Bishop, Colin, Farland, Andrew, Langefeld, Carl D., Atala, Anthony, Doering, Christopher B., Spencer, H. Trent, Porada, Christopher D., Almeida-Porada, Graça

المساهمون: National Heart, Lung, and Blood Institute

المصدر: Frontiers in Immunology ; volume 13 ; ISSN 1664-3224

الاتاحة: http://dx.doi.org/10.3389/fimmu.2022.954984
https://www.frontiersin.org/articles/10.3389/fimmu.2022.954984/full

المؤلفون: Kumar, Sandeep R. P., Xie, Jun, Hu, Shilang, Ko, Jihye, Huang, Qifeng, Brown, Harrison C., Srivastava, Alok, Markusic, David M., Doering, Christopher B., Spencer, H. Trent, Srivastava, Arun, Gao, Guangping, Herzog, Roland W.

المساهمون: Pediatrics, School of Medicine

المصدر: PMC

مصطلحات موضوعية: Adeno-associated virus (AAV), Hemophilia, Factor IX, Liver, Non-human primate, Immune response, Capsid, Antibodies

وصف الملف: application/pdf

Relation: Molecular Therapy - Methods & Clinical Development; Kumar SRP, Xie J, Hu S, et al. Coagulation factor IX gene transfer to non-human primates using engineered AAV3 capsid and hepatic optimized expression cassette. Mol Ther Methods Clin Dev. 2021;23:98-107. Published 2021 Aug 26. doi:10.1016/j.omtm.2021.08.001; https://hdl.handle.net/1805/39834

الاتاحة: https://hdl.handle.net/1805/39834

المؤلفون: Dasgupta, Anindya, Herzegh, Kristen, Spencer, H. Trent, Doering, Christopher, Day, Eric, Swaney, William P.

المساهمون: None

المصدر: Current Stem Cell Reports ; volume 7, issue 4, page 129-139 ; ISSN 2198-7866

الاتاحة: http://dx.doi.org/10.1007/s40778-021-00196-4
https://link.springer.com/content/pdf/10.1007/s40778-021-00196-4.pdf
https://link.springer.com/article/10.1007/s40778-021-00196-4/fulltext.html

المؤلفون: Zoine, Jaquelyn T., Prince, Chengyu, Story, Jamie Y., Branella, Gianna M., Lytle, Allison M., Fedanov, Andrew, Alexander, Jordan S., Porter, Christopher C., Doering, Christopher B., Spencer, H. Trent, Chandrakasan, Shanmuganathan

المساهمون: U.S. Department of Health & Human Services | NIH | National Heart, Lung, and Blood Institute, U.S. Department of Health & Human Services | NIH | Eunice Kennedy Shriver National Institute of Child Health and Human Development

المصدر: Gene Therapy ; volume 29, issue 5, page 1-12 ; ISSN 0969-7128 1476-5462

الاتاحة: http://dx.doi.org/10.1038/s41434-021-00283-5
https://www.nature.com/articles/s41434-021-00283-5.pdf
https://www.nature.com/articles/s41434-021-00283-5

المؤلفون: Stem, Christopher, Rodman, Christopher, Ramamurthy, Ritu M., George, Sunil, Meares, Diane, Farland, Andrew, Atala, Anthony, Doering, Christopher B., Spencer, H. Trent, Porada, Christopher D., Almeida-Porada, Graça

المساهمون: National Heart, Lung, and Blood Institute

المصدر: Frontiers in Cell and Developmental Biology ; volume 9 ; ISSN 2296-634X

الاتاحة: http://dx.doi.org/10.3389/fcell.2021.678117
https://www.frontiersin.org/articles/10.3389/fcell.2021.678117/full

المؤلفون: Ronayne, Estelle K., Peters, Shaun C., Gish, Joseph S., Wilson, Celena, Spencer, H. Trent, Doering, Christopher B., Lollar, Pete, Spiegel, P. Clint, Childers, Kenneth C.

المساهمون: National Heart, Lung, and Blood Institute, National Institutes of Health

المصدر: Frontiers in Immunology ; volume 12 ; ISSN 1664-3224

الاتاحة: http://dx.doi.org/10.3389/fimmu.2021.697602
https://www.frontiersin.org/articles/10.3389/fimmu.2021.697602/full