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1Academic Journal
المؤلفون: Meyer, Alayne P, Connolly, Anne M, Vannatta, Kathryn, Hacker, Natasha, Hatfield, Andrea, Decipeda, Abigail, Parker, Patricia, Willoughby, Ava, Waldrop, Megan A
المصدر: J Neuromuscul Dis ; ISSN:2214-3602 ; Volume:11 ; Issue:1
مصطلحات موضوعية: Onasemnogene abeparvovec-xioi, Spinal muscular atrophy, genetic therapy, neonatal screening
Relation: https://doi.org/10.3233/JND-230082; https://pubmed.ncbi.nlm.nih.gov/38160362; https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10789343/