المؤلفون: Cudkowicz, Merit E, Lindborg, Stacy R, Goyal, Namita A, Miller, Robert G, Burford, Matthew J, Berry, James D, Nicholson, Katharine A, Mozaffar, Tahseen, Katz, Jonathan S, Jenkins, Liberty J, Baloh, Robert H, Lewis, Richard A, Staff, Nathan P, Owegi, Margaret A, Berry, Donald A, Gothelf, Yael, Levy, Yossef S, Aricha, Revital, Kern, Ralph Z, Windebank, Anthony J, Brown, Robert H

المصدر: Muscle & Nerve. 65(3)

مصطلحات موضوعية: Biomedical and Clinical Sciences, Clinical Sciences, Stem Cell Research, Brain Disorders, Clinical Trials and Supportive Activities, Stem Cell Research - Nonembryonic - Human, Rare Diseases, Stem Cell Research - Nonembryonic - Non-Human, Prevention, ALS, Neurosciences, Neurodegenerative, Clinical Research, Evaluation of treatments and therapeutic interventions, 6.1 Pharmaceuticals, Neurological, Amyotrophic Lateral Sclerosis, Double-Blind Method, Humans, Mesenchymal Stem Cells, Nerve Growth Factors, Transplantation, Autologous, ALSFRS-R, amyotrophic lateral sclerosis, biomarker, clinical trial, stem cells, Medical and Health Sciences, Neurology & Neurosurgery, Biological sciences, Biomedical and clinical sciences

وصف الملف: application/pdf

URL الوصول: https://escholarship.org/uc/item/4gw5b5kn

المؤلفون: Baxi, Emily G, Thompson, Terri, Li, Jonathan, Kaye, Julia A, Lim, Ryan G, Wu, Jie, Ramamoorthy, Divya, Lima, Leandro, Vaibhav, Vineet, Matlock, Andrea, Frank, Aaron, Coyne, Alyssa N, Landin, Barry, Ornelas, Loren, Mosmiller, Elizabeth, Thrower, Sara, Farr, S Michelle, Panther, Lindsey, Gomez, Emilda, Galvez, Erick, Perez, Daniel, Meepe, Imara, Lei, Susan, Mandefro, Berhan, Trost, Hannah, Pinedo, Louis, Banuelos, Maria G, Liu, Chunyan, Moran, Ruby, Garcia, Veronica, Workman, Michael, Ho, Richie, Wyman, Stacia, Roggenbuck, Jennifer, Harms, Matthew B, Stocksdale, Jennifer, Miramontes, Ricardo, Wang, Keona, Venkatraman, Vidya, Holewenski, Ronald, Sundararaman, Niveda, Pandey, Rakhi, Manalo, Danica-Mae, Donde, Aneesh, Huynh, Nhan, Adam, Miriam, Wassie, Brook T, Vertudes, Edward, Amirani, Naufa, Raja, Krishna, Thomas, Reuben, Hayes, Lindsey, Lenail, Alex, Cerezo, Aianna, Luppino, Sarah, Farrar, Alanna, Pothier, Lindsay, Prina, Carolyn, Morgan, Todd, Jamil, Arish, Heintzman, Sarah, Jockel-Balsarotti, Jennifer, Karanja, Elizabeth, Markway, Jesse, McCallum, Molly, Joslin, Ben, Alibazoglu, Deniz, Kolb, Stephen, Ajroud-Driss, Senda, Baloh, Robert, Heitzman, Daragh, Miller, Tim, Glass, Jonathan D, Patel-Murray, Natasha Leanna, Yu, Hong, Sinani, Ervin, Vigneswaran, Prasha, Sherman, Alexander V, Ahmad, Omar, Roy, Promit, Beavers, Jay C, Zeiler, Steven, Krakauer, John W, Agurto, Carla, Cecchi, Guillermo, Bellard, Mary, Raghav, Yogindra, Sachs, Karen, Ehrenberger, Tobias, Bruce, Elizabeth, Cudkowicz, Merit E, Maragakis, Nicholas, Norel, Raquel, Van Eyk, Jennifer E, Finkbeiner, Steven, Berry, James, Sareen, Dhruv, Thompson, Leslie M, Fraenkel, Ernest, Svendsen, Clive N

المصدر: Nature Neuroscience. 25(2)

مصطلحات موضوعية: Stem Cell Research, Rare Diseases, Stem Cell Research - Induced Pluripotent Stem Cell, ALS, Clinical Research, Neurodegenerative, Genetics, Neurosciences, Human Genome, Stem Cell Research - Induced Pluripotent Stem Cell - Human, Brain Disorders, Neurological, Generic health relevance, Good Health and Well Being, Amyotrophic Lateral Sclerosis, Cell Line, Humans, Induced Pluripotent Stem Cells, Motor Neurons, Psychology, Cognitive Sciences, Neurology & Neurosurgery

وصف الملف: application/pdf

URL الوصول: https://escholarship.org/uc/item/0pm655p6

المؤلفون: Nowak, Richard J, Coffey, Christopher S, Goldstein, Jonathan M, Dimachkie, Mazen M, Benatar, Michael, Kissel, John T, Wolfe, Gil I, Burns, Ted M, Freimer, Miriam L, Nations, Sharon, Granit, Volkan, Smith, A Gordon, Richman, David P, Ciafaloni, Emma, Al-Lozi, Muhammad T, Sams, Laura Ann, Quan, Dianna, Ubogu, Eroboghene, Pearson, Brenda, Sharma, Aditi, Yankey, Jon W, Uribe, Liz, Shy, Michael, Amato, Anthony A, Conwit, Robin, O'Connor, Kevin C, Hafler, David A, Cudkowicz, Merit E, Barohn, Richard J, Team, on behalf of the NeuroNEXT NN103 BeatMG Study

المصدر: Neurology. 98(4)

مصطلحات موضوعية: Clinical Trials and Supportive Activities, Clinical Research, Neurosciences, Cancer, Rare Diseases, Evaluation of treatments and therapeutic interventions, 6.1 Pharmaceuticals, NeuroNEXT NN103 BeatMG Study Team, Clinical Sciences, Cognitive Sciences, Neurology & Neurosurgery

وصف الملف: application/pdf

URL الوصول: https://escholarship.org/uc/item/3kc6g1jn

المؤلفون: Weiss, Michael D, Macklin, Eric A, McIlduff, Courtney E, Vucic, Steve, Wainger, Brian J, Kiernan, Matthew C, Goutman, Stephen A, Goyal, Namita A, Rutkove, Seward B, Ladha, Shafeeq S, Chen, I‐Hweii Amy, Harms, Matthew B, Brannagan, Thomas H, Lacomis, David, Zivkovic, Sasha, Ma, Maxwell, Wang, Leo H, Simmons, Zachary, Rivner, Michael H, Shefner, Jeremy M, Cudkowicz, Merit E, Atassi, Nazem, Group, for the Mexiletine‐2 ALS Study

المصدر: Muscle & Nerve. 63(3)

مصطلحات موضوعية: Biomedical and Clinical Sciences, Clinical Sciences, Brain Disorders, Rare Diseases, Neurodegenerative, Clinical Research, ALS, Neurosciences, Clinical Trials and Supportive Activities, Evaluation of treatments and therapeutic interventions, 6.1 Pharmaceuticals, Neurological, Adult, Aged, Amyotrophic Lateral Sclerosis, Axons, Cortical Excitability, Double-Blind Method, Electrodiagnosis, Electromyography, Evoked Potentials, Motor, Female, Humans, Male, Median Nerve, Mexiletine, Middle Aged, Neural Conduction, Preliminary Data, Transcranial Magnetic Stimulation, Voltage-Gated Sodium Channel Blockers, amyotrophic lateral sclerosis, axonal excitability, outcome research, randomized controlled clinical trial, transcranial magnetic stimulation, Mexiletine-2 ALS Study Group, Medical and Health Sciences, Neurology & Neurosurgery, Biological sciences, Biomedical and clinical sciences

وصف الملف: application/pdf

URL الوصول: https://escholarship.org/uc/item/49v0155t

المؤلفون: Neel, Dylan V., Baselga‐Garriga, Clara, Benson, Molly, Keegan, Mackenzie, Chase, Marianne, D'Agostino, Derek, Drake, Kristin, Hagar, Jennifer Linn, Hasenoehrl, Meredith Gibbons, Kulesa‐Kelley, Jennifer, Leite, Alex, Mohapatra, Silpa, Portaro, Susanna Marie, Pothier, Lindsay M., Rosenthal, Jesse, Sherman, Alexander V., Yu, Hong, McCaffrey, Alexandra, Ho, Doreen, Luppino, Sarah, Bedlack, Richard, Heitzman, Daragh, Ajroud‐Driss, Senda, Katz, Jonathan, Felice, Kevin, Whitaker, Charles, Ladha, Shafeeq, Alameda, Gustavo, Locatelli, Eduardo, Qureshi, Irfan A., Hotchkin, Michael T., Hayden, Michael R., Cudkowicz, Merit E., Babu, Suma, Berry, James D., Paganoni, Sabrina

المصدر: Muscle & Nerve ; volume 70, issue 2, page 232-239 ; ISSN 0148-639X 1097-4598

الاتاحة: https://doi.org/10.1002/mus.28169
https://onlinelibrary.wiley.com/doi/pdf/10.1002/mus.28169

المؤلفون: Lindborg, Stacy R., Goyal, Namita A., Katz, Jonathan, Burford, Matthew, Li, Jenny, Kaspi, Haggai, Abramov, Natalie, Boulanger, Bruno, Berry, James D., Nicholson, Katharine, Mozaffar, Tahseen, Miller, Robert, Jenkins, Liberty, Baloh, Robert H., Lewis, Richard, Staff, Nathan P., Owegi, Margaret Ayo, Dagher, Bob, Blondheim‐Shraga, Netta R., Gothelf, Yael, Levy, Yossef S., Kern, Ralph, Aricha, Revital, Windebank, Anthony J., Bowser, Robert, Brown, Robert H., Cudkowicz, Merit E.

المساهمون: California Institute for Regenerative Medicine, ALS Association

المصدر: Muscle & Nerve ; volume 69, issue 6, page 719-729 ; ISSN 0148-639X 1097-4598

الاتاحة: http://dx.doi.org/10.1002/mus.28093
https://onlinelibrary.wiley.com/doi/pdf/10.1002/mus.28093

المؤلفون: Paganoni, Sabrina, Hendrix, Suzanne, Dickson, Samuel P, Knowlton, Newman, Macklin, Eric A, Berry, James D, Elliott, Michael A, Maiser, Samuel, Karam, Chafic, Caress, James B, Owegi, Margaret Ayo, Quick, Adam, Wymer, James, Goutman, Stephen A, Heitzman, Daragh, Heiman‐Patterson, Terry D, Jackson, Carlayne E, Quinn, Colin, Rothstein, Jeffrey D, Kasarskis, Edward J, Katz, Jonathan, Jenkins, Liberty, Ladha, Shafeeq, Miller, Timothy M, Scelsa, Stephen N, Vu, Tuan H, Fournier, Christina N, Glass, Jonathan D, Johnson, Kristin M, Swenson, Andrea, Goyal, Namita A, Pattee, Gary L, Andres, Patricia L, Babu, Suma, Chase, Marianne, Dagostino, Derek, Hall, Meghan, Kittle, Gale, Eydinov, Matthew, McGovern, Michelle, Ostrow, Joseph, Pothier, Lindsay, Randall, Rebecca, Shefner, Jeremy M, Sherman, Alexander V, St Pierre, Maria E, Tustison, Eric, Vigneswaran, Prasha, Walker, Jason, Yu, Hong, Chan, James, Wittes, Janet, Yu, Zi‐Fan, Cohen, Joshua, Klee, Justin, Leslie, Kent, Tanzi, Rudolph E, Gilbert, Walter, Yeramian, Patrick D, Schoenfeld, David, Cudkowicz, Merit E

المصدر: Muscle & Nerve. 63(1)

مصطلحات موضوعية: Brain Disorders, Rare Diseases, Neurodegenerative, Clinical Trials and Supportive Activities, Clinical Research, ALS, Evaluation of treatments and therapeutic interventions, 6.1 Pharmaceuticals, Adolescent, Adult, Aged, Aged, 80 and over, Amyotrophic Lateral Sclerosis, Double-Blind Method, Female, Humans, Male, Middle Aged, Neuroprotective Agents, Phenylbutyrates, Taurochenodeoxycholic Acid, Time, Young Adult, amyotrophic lateral sclerosis, CENTAUR, motor neuron disease, sodium phenylbutyrate‐, taurursodiol, survival analysis, sodium phenylbutyrate-taurursodiol, Medical and Health Sciences, Neurology & Neurosurgery

وصف الملف: application/pdf

URL الوصول: https://escholarship.org/uc/item/6bn8q913

المؤلفون: Paganoni, Sabrina, Macklin, Eric A, Hendrix, Suzanne, Berry, James D, Elliott, Michael A, Maiser, Samuel, Karam, Chafic, Caress, James B, Owegi, Margaret A, Quick, Adam, Wymer, James, Goutman, Stephen A, Heitzman, Daragh, Heiman-Patterson, Terry, Jackson, Carlayne E, Quinn, Colin, Rothstein, Jeffrey D, Kasarskis, Edward J, Katz, Jonathan, Jenkins, Liberty, Ladha, Shafeeq, Miller, Timothy M, Scelsa, Stephen N, Vu, Tuan H, Fournier, Christina N, Glass, Jonathan D, Johnson, Kristin M, Swenson, Andrea, Goyal, Namita A, Pattee, Gary L, Andres, Patricia L, Babu, Suma, Chase, Marianne, Dagostino, Derek, Dickson, Samuel P, Ellison, Noel, Hall, Meghan, Hendrix, Kent, Kittle, Gale, McGovern, Michelle, Ostrow, Joseph, Pothier, Lindsay, Randall, Rebecca, Shefner, Jeremy M, Sherman, Alexander V, Tustison, Eric, Vigneswaran, Prasha, Walker, Jason, Yu, Hong, Chan, James, Wittes, Janet, Cohen, Joshua, Klee, Justin, Leslie, Kent, Tanzi, Rudolph E, Gilbert, Walter, Yeramian, Patrick D, Schoenfeld, David, Cudkowicz, Merit E

المصدر: New England Journal of Medicine. 383(10)

مصطلحات موضوعية: Biomedical and Clinical Sciences, Clinical Sciences, Clinical Trials and Supportive Activities, Neurodegenerative, Rare Diseases, Clinical Research, ALS, Brain Disorders, Neurosciences, Evaluation of treatments and therapeutic interventions, 6.1 Pharmaceuticals, Aged, Amyotrophic Lateral Sclerosis, Disease Progression, Double-Blind Method, Drug Combinations, Female, Humans, Intention to Treat Analysis, Male, Middle Aged, Phenylbutyrates, Severity of Illness Index, Taurochenodeoxycholic Acid, Treatment Outcome, Medical and Health Sciences, General & Internal Medicine, Biomedical and clinical sciences, Health sciences

وصف الملف: application/pdf

URL الوصول: https://escholarship.org/uc/item/2hn1s0pw

المؤلفون: Howard, Ileana M., Babu, Suma, Carter, Chelsey, Sakowski, Stacey A., Kurent, Jerome E., Cudkowicz, Merit E., Feldman, Eva L.

المصدر: Annals of Neurology; Dec2024, Vol. 96 Issue 6, p1035-1039, 5p

مصطلحات موضوعية: AMYOTROPHIC lateral sclerosis, SKELETAL muscle, NEURODEGENERATION, DELAYED diagnosis, QUALITY of life

المؤلفون: Fox, Robert J, Coffey, Christopher S, Conwit, Robin, Cudkowicz, Merit E, Gleason, Trevis, Goodman, Andrew, Klawiter, Eric C, Matsuda, Kazuko, McGovern, Michelle, Naismith, Robert T, Ashokkumar, Akshata, Barnes, Janel, Ecklund, Dixie, Klingner, Elizabeth, Koepp, Maxine, Long, Jeffrey D, Natarajan, Sneha, Thornell, Brenda, Yankey, Jon, Bermel, Robert A, Debbins, Josef P, Huang, Xuemei, Jagodnik, Patricia, Lowe, Mark J, Nakamura, Kunio, Narayanan, Sridar, Sakaie, Ken E, Thoomukuntla, Bhaskar, Zhou, Xiaopeng, Krieger, Stephen, Alvarez, Enrique, Apperson, Michelle, Bashir, Khurram, Cohen, Bruce A, Coyle, Patricia K, Delgado, Silvia, Dewitt, L Dana, Flores, Angela, Giesser, Barbara S, Goldman, Myla D, Jubelt, Burk, Lava, Neil, Lynch, Sharon G, Moses, Harold, Ontaneda, Daniel, Perumal, Jai S, Racke, Michael, Repovic, Pavle, Riley, Claire S, Severson, Christopher, Shinnar, Shlomo, Suski, Valerie, Weinstock-Guttman, Bianca, Yadav, Vijayshree, Zabeti, Aram

المصدر: New England Journal of Medicine. 379(9)

مصطلحات موضوعية: Neurosciences, Neurodegenerative, Brain Disorders, Clinical Trials and Supportive Activities, Autoimmune Disease, Multiple Sclerosis, Clinical Research, Evaluation of treatments and therapeutic interventions, 6.1 Pharmaceuticals, Neurological, Adult, Atrophy, Brain, Depression, Diffusion Tensor Imaging, Disease Progression, Double-Blind Method, Female, Gastrointestinal Diseases, Headache, Humans, Male, Middle Aged, Multiple Sclerosis, Chronic Progressive, Phosphodiesterase Inhibitors, Pyridines, NN102/SPRINT-MS Trial Investigators, Medical and Health Sciences, General & Internal Medicine

وصف الملف: application/pdf

URL الوصول: https://escholarship.org/uc/item/2v87p5vz

المؤلفون: Oskarsson, Björn, Moore, Dan, Mozaffar, Tahseen, Ravits, John, Wiedau-Pazos, Martina, Parziale, Nicholas, Joyce, Nanette C, Mandeville, Ross, Goyal, Namita, Cudkowicz, Merit E, Weiss, Michael, Miller, Robert G, McDonald, Craig M

المصدر: Muscle & Nerve. 58(1)

مصطلحات موضوعية: Muscle cramp, amyotrophic lateral sclerosis, fasciculations, neuromuscular, quality of life

وصف الملف: application/pdf

URL الوصول: https://escholarship.org/uc/item/8gr8w1pw

المؤلفون: Shefner, Jeremy M, Al-Chalabi, Ammar, Andrews, Jinsy A, Chio, Adriano, De Carvalho, Mamede, Cockroft, Bettina M, Corcia, Philippe, Couratier, Philippe, Cudkowicz, Merit E, Genge, Angela, Hardiman, Orla, Heiman-Patterson, Terry, Henderson, Robert D, Ingre, Caroline, Jackson, Carlayne E, Johnston, Wendy, Lechtzin, Noah, Ludolph, Albert, Maragakis, Nicholas J, Miller, Timothy M, Mora Pardina, Jesus S, Petri, Susanne, Simmons, Zachary, Van Den Berg, Leonard H, Zinman, Lorne, Kupfer, Stuart, Malik, Fady I, Meng, Lisa, Simkins, Tyrell J, Wei, Jenny, Wolff, Andrew A, Rudnicki, Stacy A

المساهمون: Neurologen, Projectafdeling ALS, Brain, Regenerative Medicine and Stem Cells

مصطلحات موضوعية: ALSFRS-R, Amyotrophic lateral sclerosis, randomized clinical trial, reldesemtiv, Clinical Neurology, Neurology, Journal Article

وصف الملف: application/pdf

Relation: https://dspace.library.uu.nl/handle/1874/449379

الاتاحة: https://dspace.library.uu.nl/handle/1874/449379

المؤلفون: van Unnik, Jordi W J, Nikolakopoulos, Stavros, Eijkemans, Marinus J C, Gonzalez-Bermejo, Jésus, Bruneteau, Gaelle, Morelot-Panzini, Capucine, van den Berg, Leonard H, Cudkowicz, Merit E, McDermott, Christopher J, Similowski, Thomas, van Eijk, Ruben P A

المساهمون: Projectafdeling ALS, Biostatistiek Onderzoek, JC onderzoeksprogramma Methodologie, Child Health, Circulatory Health, Infection & Immunity, JC onderzoeksprogramma Infectieziekten, Neurologen, Brain, Regenerative Medicine and Stem Cells

مصطلحات موضوعية: Amyotrophic Lateral Sclerosis/drug therapy, Computer Simulation, Humans, Medical Futility, Research Design, Retrospective Studies, Uncertainty, Journal Article

وصف الملف: application/pdf

Relation: https://dspace.library.uu.nl/handle/1874/449059

الاتاحة: https://dspace.library.uu.nl/handle/1874/449059

المؤلفون: Cudkowicz, Merit E, Lindborg, Stacy R, Goyal, Namita A, Miller, Robert G, Burford, Matthew J, Berry, James D, Nicholson, Katharine A, Mozaffar, Tahseen, Katz, Jonathan S, Jenkins, Liberty J, Baloh, Robert H, Lewis, Richard A, Staff, Nathan P, Owegi, Margaret A, Berry, Donald A, Gothelf, Yael, Levy, Yossef S, Aricha, Revital, Kern, Ralph Z, Windebank, Anthony J, Brown, Robert H

المساهمون: Neurology

المصدر: Muscle & nerve ; 65 ; 3 ; 291 ; 302 ; United States

مصطلحات موضوعية: ALSFRS-R, amyotrophic lateral sclerosis, biomarker, clinical trial, stem cells

Relation: Muscle & Nerve; https://doi.org/10.1002/mus.27472; Cudkowicz ME, Lindborg SR, Goyal NA, Miller RG, Burford MJ, Berry JD, Nicholson KA, Mozaffar T, Katz JS, Jenkins LJ, Baloh RH, Lewis RA, Staff NP, Owegi MA, Berry DA, Gothelf Y, Levy YS, Aricha R, Kern RZ, Windebank AJ, Brown RH Jr. A randomized placebo-controlled phase 3 study of mesenchymal stem cells induced to secrete high levels of neurotrophic factors in amyotrophic lateral sclerosis. Muscle Nerve. 2022 Mar;65(3):291-302. doi:10.1002/mus.27472. Epub 2022 Jan 5. Erratum in: Muscle Nerve. 2022 Oct;66(4):E26-E27. PMID: 34890069; PMCID: PMC9305113.; http://hdl.handle.net/20.500.14038/52196

الاتاحة: https://doi.org/10.1002/mus.27472
https://hdl.handle.net/20.500.14038/52196

المؤلفون: van Unnik, Jordi W.J., Nikolakopoulos, Stavros, Eijkemans, Marinus J.C., Gonzalez-Bermejo, Jésus, Bruneteau, Gaelle, Morelot-Panzini, Capucine, van den Berg, Leonard, H, Cudkowicz, Merit, E, Mcdermott, Christopher, J, Similowski, Thomas, van Eijk, Ruben P.A.

المساهمون: Sorbonne Université (SU), Institut du Cerveau = Paris Brain Institute (ICM), Assistance publique - Hôpitaux de Paris (AP-HP) (AP-HP)-Institut National de la Santé et de la Recherche Médicale (INSERM)-CHU Pitié-Salpêtrière AP-HP, Assistance publique - Hôpitaux de Paris (AP-HP) (AP-HP)-Sorbonne Université (SU)-Sorbonne Université (SU)-Sorbonne Université (SU)-Centre National de la Recherche Scientifique (CNRS), This study was funded by Stichting ALS Nederland (TRICALS-Reactive II). The DiPALS study was funded by the NationalInstitute for Health Research Health Technology Assessmentprogram (09/55/33) and by the Motor Neurone Disease As-sociation of England, Wales, and Northern Ireland. TheRespiStimALS study was funded by the Hospital Program forClinical Research, French Ministry of Health (grant no.P110133), and by a “Contrat de Recherche Clinique” of theDirection de la Recherche Clinique et du D´eveloppement(DRCD), Assistance Publique-Hˆopitaux de Paris, Paris, France(grant no. CRC15017-R02), which also served as the studysponsor. It was also funded by the French patients’ associationfor ALS research (“Association pour la Rercherche sur laScl´erose Lat´erale Amyotrophique,” ARSLA) and by the Thierryde Latran foundation for Amyotrophic Lateral Sclerosis. TheCeftriaxone-ALS study was funded by the National Institute ofNeurological Disorders and Stroke (grant 5 U01-NS-049640).

المصدر: ISSN: 0028-3878.

مصطلحات موضوعية: MESH: Humans, MESH: Amyotrophic Lateral Sclerosis, MESH: Retrospective Studies, MESH: Computer Simulation, MESH: Medical Futility, MESH: Uncertainty, MESH: Research Design, [SDV.MHEP]Life Sciences [q-bio]/Human health and pathology

Relation: info:eu-repo/semantics/altIdentifier/pmid/37085329; hal-04590527; https://hal.sorbonne-universite.fr/hal-04590527; https://hal.sorbonne-universite.fr/hal-04590527/document; https://hal.sorbonne-universite.fr/hal-04590527/file/WNL-2023-000182.pdf; PUBMED: 37085329; PUBMEDCENTRAL: PMC10256133

الاتاحة: https://hal.sorbonne-universite.fr/hal-04590527
https://hal.sorbonne-universite.fr/hal-04590527/document
https://hal.sorbonne-universite.fr/hal-04590527/file/WNL-2023-000182.pdf
https://doi.org/10.1212/WNL.0000000000207306

المؤلفون: Walk, David, Nicholson, Katharine, Locatelli, Eduardo, Chan, James, Macklin, Eric A., Ferment, Valerie, Manousakis, Georgios, Chase, Marianne, Connolly, Mariah, Dagostino, Derek, Hall, Meghan, Ostrow, Joseph, Pothier, Lindsay, Lieberman, Cassandra, Gelevski, Dario, Randall, Rebecca, Sherman, Alexander V., Steinhart, Erin, Walker, Daniela Grasso, Walker, Jason, Yu, Hong, Wills, Anne‐Marie, Schwarzschild, Michael A., Beukenhorst, Anna L., Onnela, Jukka‐Pekka, Berry, James D., Cudkowicz, Merit E., Paganoni, Sabrina

المساهمون: Salah Foundation

المصدر: Muscle & Nerve ; volume 67, issue 5, page 378-386 ; ISSN 0148-639X 1097-4598

الاتاحة: http://dx.doi.org/10.1002/mus.27807
https://onlinelibrary.wiley.com/doi/pdf/10.1002/mus.27807
https://onlinelibrary.wiley.com/doi/full-xml/10.1002/mus.27807

المؤلفون: Yerton, Megan, Winter, Allison, Gelevski, Dario, Addy, Grace, Kostov, Anthony, Lieberman, Cassandra, Weber, Harli, Doyle, Michael, Kane, Geli, Cohen, Caroline, Parikh, Neil, Burke, Katherine M., Rohrer, Margot, Stirrat, Taylor, Bruno, Margaret, Hochman, Alison, Luppino, Sarah, Scalia, Jennifer, D'Agostino, Derek, Sinani, Ervin, Yu, Hong, Drake, Kristin, Hagar, Jennifer, Sherman, Alexander V., Babu, Suma, Berry, James D., Cudkowicz, Merit E., Paganoni, Sabrina

المصدر: Muscle & Nerve ; volume 67, issue 6, page 456-463 ; ISSN 0148-639X 1097-4598

الاتاحة: http://dx.doi.org/10.1002/mus.27819
https://onlinelibrary.wiley.com/doi/pdf/10.1002/mus.27819

المؤلفون: Shefner, Jeremy M., Al-Chalabi, Ammar, Andrews, Jinsy A., Chio, Adriano, De Carvalho, Mamede, Cockroft, Bettina M., Corcia, Philippe, Couratier, Philippe, Cudkowicz, Merit E., Genge, Angela, Hardiman, Orla, Heiman-Patterson, Terry, Henderson, Robert D., Ingre, Caroline, Jackson, Carlayne E., Johnston, Wendy, Lechtzin, Noah, Ludolph, Albert, Maragakis, Nicholas J., Miller, Timothy M., Mora Pardina, Jesus S., Petri, Susanne, Simmons, Zachary, Van Den Berg, Leonard H., Zinman, Lorne, Kupfer, Stuart, Malik, Fady I., Meng, Lisa, Simkins, Tyrell J., Wei, Jenny, Wolff, Andrew A., Rudnicki, Stacy A.

المساهمون: Cytokinetics

المصدر: Amyotrophic Lateral Sclerosis and Frontotemporal Degeneration ; volume 24, issue 5-6, page 523-534 ; ISSN 2167-8421 2167-9223

الاتاحة: http://dx.doi.org/10.1080/21678421.2023.2216223
https://www.tandfonline.com/doi/pdf/10.1080/21678421.2023.2216223

المؤلفون: Miller, Timothy M, Cudkowicz, Merit E, Genge, Angela, Shaw, Pamela J, Sobue, Gen, Bucelli, Robert C, Chiò, Adriano, Van Damme, Philip, Ludolph, Albert C, Glass, Jonathan D, Andrews, Jinsy A, Babu, Suma, Benatar, Michael, McDermott, Christopher J, Cochrane, Thos, Chary, Sowmya, Chew, Sheena, Zhu, Han, Wu, Fan, Nestorov, Ivan, Graham, Danielle, Sun, Peng, McNeill, Manjit, Fanning, Laura, Ferguson, Toby A, Fradette, Stephanie

المساهمون: Miller, Timothy M, Cudkowicz, Merit E, Genge, Angela, Shaw, Pamela J, Sobue, Gen, Bucelli, Robert C, Chiò, Adriano, Van Damme, Philip, Ludolph, Albert C, Glass, Jonathan D, Andrews, Jinsy A, Babu, Suma, Benatar, Michael, McDermott, Christopher J, Cochrane, Tho, Chary, Sowmya, Chew, Sheena, Zhu, Han, Wu, Fan, Nestorov, Ivan, Graham, Danielle, Sun, Peng, McNeill, Manjit, Fanning, Laura, Ferguson, Toby A, Fradette, Stephanie

مصطلحات موضوعية: Adult, Biomarker, Double-Blind Method, Human, Injections, Spinal, Neurofilament Protein, Recovery of Function, Amyotrophic Lateral Sclerosi, Oligonucleotides, Antisense, Superoxide Dismutase-1

Relation: info:eu-repo/semantics/altIdentifier/pmid/36129998; info:eu-repo/semantics/altIdentifier/wos/WOS:000865461700006; volume:387; issue:12; firstpage:1099; lastpage:1110; numberofpages:12; journal:NEW ENGLAND JOURNAL OF MEDICINE; https://hdl.handle.net/2318/1880712; info:eu-repo/semantics/altIdentifier/scopus/2-s2.0-85138249559

الاتاحة: https://hdl.handle.net/2318/1880712
https://doi.org/10.1056/NEJMoa2204705

المؤلفون: Bali, Taha, Self, Wade, Liu, Jingxia, Siddique, Teepu, Wang, Leo H, Bird, Thomas D, Ratti, Elena, Atassi, Nazem, Boylan, Kevin B, Glass, Jonathan D, Maragakis, Nicholas J, Caress, James B, McCluskey, Leo F, Appel, Stanley H, Wymer, James P, Gibson, Summer, Zinman, Lorne, Mozaffar, Tahseen, Callaghan, Brian, McVey, April L, Jockel-Balsarotti, Jennifer, Allred, Peggy, Fisher, Elena R, Lopate, Glenn, Pestronk, Alan, Cudkowicz, Merit E, Miller, Timothy M

المصدر: Journal of Neurology Neurosurgery & Psychiatry. 88(2)

مصطلحات موضوعية: Biomedical and Clinical Sciences, Clinical Sciences, Brain Disorders, Neurosciences, ALS, Rare Diseases, Clinical Research, Neurodegenerative, Clinical Trials and Supportive Activities, Adult, Age of Onset, Amyotrophic Lateral Sclerosis, Clinical Trials as Topic, Disease Progression, Humans, Middle Aged, Mutation, Research Design, Retrospective Studies, Superoxide Dismutase, Vital Capacity, Medical and Health Sciences, Psychology and Cognitive Sciences, Neurology & Neurosurgery, Clinical sciences

وصف الملف: application/pdf

URL الوصول: https://escholarship.org/uc/item/0k87d0jh