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1Academic Journal
المؤلفون: Bhattacharyya, Nihar, Chai, Niuzheng, Hafford-Tear, Nathaniel J, Sadan, Amanda N, Szabo, Anita, Zarouchlioti, Christina, Jedlickova, Jana, Leung, Szi Kay, Liao, Tianyi, Dudakova, Lubica, Skalicka, Pavlina, Parekh, Mohit, Moghul, Ismail, Jeffries, Aaron R, Cheetham, Michael E, Muthusamy, Kirithika, Hardcastle, Alison J, Pontikos, Nikolas, Liskova, Petra, Tuft, Stephen J, Davidson, Alice E
المساهمون: Orr, Harry T
المصدر: PLoS Genetics , 20 (5) , Article e1011230. (2024) (In press).
وصف الملف: text
Relation: https://discovery.ucl.ac.uk/id/eprint/10192102/1/journal.pgen.1011230.pdf; https://discovery.ucl.ac.uk/id/eprint/10192102/
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2Academic JournalEffective AAV-mediated gene replacement therapy in retinal organoids modelling AIPL1-associated LCA4
المؤلفون: Sai, Hali, Ollington, Bethany, Rezek, Farah O, Chai, Niuzheng, Lane, Amelia, Georgiadis, Tassos, Bainbridge, James, Michaelides, Michel, Sacristan-Reviriego, Almudena, Perdigão, Pedro RL, Leung, Amy, van der Spuy, Jacqueline
المصدر: Molecular Therapy - Nucleic Acids , 35 (1) , Article 102148. (2024)
مصطلحات موضوعية: MT: Delivery strategies, Leber congenital amaurosis, retinal organoid, aryl hydrocarbon receptor, interacting protein-like 1adeno-associated virus, inherited retinal degeneration, gene therapy, induced pluripotent stem cells
وصف الملف: application/pdf
Relation: https://discovery.ucl.ac.uk/id/eprint/10188446/1/OMTN102148_proof.pdf; https://discovery.ucl.ac.uk/id/eprint/10188446/