المؤلفون: Junnan Shi, Xianwen Chen, Hao Hu, Carolina Oi Lam Ung

المصدر: BMC Health Services Research, Vol 25, Iss 1, Pp 1-30 (2025)

مصطلحات موضوعية: Hospital pharmacy, Pharmaceutical care, Pharmacy practice, Advanced therapy medicinal products, Cell and gene therapy, Regeneration medicine, Public aspects of medicine, RA1-1270

وصف الملف: electronic resource

Relation: https://doaj.org/toc/1472-6963

URL الوصول: https://doaj.org/article/763802f71f644221add9dfe310d2fe3d

المؤلفون: Lidija Radenovic

المصدر: Exploration of Neuroprotective Therapy, Vol 4, Iss 6, Pp 459-484 (2024)

مصطلحات موضوعية: ischemic stroke, cerebral ischemia, treatment, target, stem cell and gene therapy, neuroregeneration, neuroprotection, rehabilitation, Neurology. Diseases of the nervous system, RC346-429

وصف الملف: electronic resource

Relation: https://www.explorationpub.com/Journals/ent/Article/100494; https://doaj.org/toc/2769-6510

URL الوصول: https://doaj.org/article/8cedcec30d5b482e8325c0fa7f5e58a5

المؤلفون: Yuxin Cai, Lijuan Sui, Jingjing Wang, Weilin Qian, Yeheng Peng, Luyao Gong, Weijia Wu, Yuan Gao

المصدر: BMC Medicine, Vol 22, Iss 1, Pp 1-23 (2024)

مصطلحات موضوعية: Cell and gene therapy products, Post-marketing surveillance, Regulations, Advanced therapy medicinal products, Medicine

وصف الملف: electronic resource

Relation: https://doaj.org/toc/1741-7015

URL الوصول: https://doaj.org/article/c9946b23617b4dcf8f586491879b709b

المؤلفون: Zibin Bu, Jintu Lou, Weiqun Xu, Lingyan Zhang, Yongmin Tang

المصدر: Stem Cell Research & Therapy, Vol 15, Iss 1, Pp 1-13 (2024)

مصطلحات موضوعية: Hemophilia B, Cell-based gene therapy, Human umbilical cord mesenchymal stem cells, scAAV-DJ/8-LP1-hFIXco, Medicine (General), R5-920, Biochemistry, QD415-436

وصف الملف: electronic resource

Relation: https://doaj.org/toc/1757-6512

URL الوصول: https://doaj.org/article/ca5af01cf7ac4774831111a086c17467

المؤلفون: Hiroshi Karasawa, Hirokuni Mizoguchi, Bryan Choi, Chia-Ling Hsieh, Masaaki Miyano, Yuu Moriya, Sasikumar Muthusamy, Koji Takakura, Kunihiko Suzuki, Yoshie Tsurumaki, Takeshi Watanabe, Karen Wen, Tomohiro Yoneda, Ta-Tung Yuan, Masayuki Nomura

المصدر: Regenerative Therapy, Vol 26, Iss , Pp 967-980 (2024)

مصطلحات موضوعية: APACRM, Cell and gene therapy product, AAV-Based gene therapies, Non-clinical, Quality, Regulatory guideline, Medicine (General), R5-920, Cytology, QH573-671

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2352320424001767; https://doaj.org/toc/2352-3204

URL الوصول: https://doaj.org/article/4806501293ea499390e9c584ceec36b2

المؤلفون: Liu Dan, Wu Ying Ying, Akshaya V. Prabhu, Ahmad Amirul bin Abdul Rahim, Zach Lee Jia Sheng

المصدر: Frontiers in Bioengineering and Biotechnology, Vol 12 (2024)

مصطلحات موضوعية: cell and gene therapy, cell manufacturing, automated sampling, aseptic sampling, process analytical technology, automation, Biotechnology, TP248.13-248.65

وصف الملف: electronic resource

Relation: https://www.frontiersin.org/articles/10.3389/fbioe.2024.1452674/full; https://doaj.org/toc/2296-4185

URL الوصول: https://doaj.org/article/95d1066f4ef345a3aadd27ae06085397

المؤلفون: Ina Pahl, Axel Pahl, Armin Hauk, Dana Budde, Sonja Sievers, Lothar Fruth, Roberto Menzel

المصدر: Scientific Reports, Vol 14, Iss 1, Pp 1-12 (2024)

مصطلحات موضوعية: Cell painting assay (CPA), Cell and gene therapy, Advanced therapy medicinal products (ATMP), Extractables and leachables, Single-use systems, Process equipment-related leachables (PERL), Medicine, Science

وصف الملف: electronic resource

Relation: https://doaj.org/toc/2045-2322

URL الوصول: https://doaj.org/article/a9e48b2bcc5e4cc58888ef316ed17922

المؤلفون: Fahimeh Mirakhori, Sarfaraz K. Niazi

المصدر: Pharmaceuticals, Vol 18, Iss 1, p 47 (2025)

مصطلحات موضوعية: artificial intelligence (AI), drug product development, regulatory frameworks, ethical consideration, biologics, cell and gene therapy (CGT), Medicine, Pharmacy and materia medica, RS1-441

وصف الملف: electronic resource

Relation: https://www.mdpi.com/1424-8247/18/1/47; https://doaj.org/toc/1424-8247

URL الوصول: https://doaj.org/article/12c97a83cd304ecd98cd271c6e52f777

المؤلفون: Victoria W. Dayer, Michael F. Drummond, Omar Dabbous, Mondher Toumi, Peter Neumann, Sean Tunis, Nelson Teich, Shadi Saleh, Ulf Persson, Johann-Matthias Graf von der Schulenburg, Daniel C. Malone, Tay Salimullah, Sean D. Sullivan

المصدر: Orphanet Journal of Rare Diseases, Vol 19, Iss 1, Pp 1-12 (2024)

مصطلحات موضوعية: Cell and gene therapy, Coverage determination, Coverage with evidence development, Health technology assessment, Rare disease, Real world evidence, Medicine

وصف الملف: electronic resource

Relation: https://doaj.org/toc/1750-1172

URL الوصول: https://doaj.org/article/18f7fcfcb90a4c4685fa9f6e8e16039b

المؤلفون: Varsha Dalal, Geeta Jotwani, Munna Lal Yadav

المصدر: Perspectives in Clinical Research, Vol 15, Iss 1, Pp 4-9 (2024)

مصطلحات موضوعية: cell and gene therapy, clinical trial, governance, guidelines, informed consent form, legislation, medical ethics, medical innovation, regulation, transforming healthcare, Medicine, Medicine (General), R5-920

وصف الملف: electronic resource

Relation: http://www.picronline.org/article.asp?issn=2229-3485;year=2024;volume=15;issue=1;spage=4;epage=9;aulast=; https://doaj.org/toc/2229-3485

URL الوصول: https://doaj.org/article/8c785e8b366744068b9ded994f4f5bae

المؤلفون: Ekaterina A. Lesovaya, Timur I. Fetisov, Beniamin Yu. Bokhyan, Varvara P. Maksimova, Evgeny P. Kulikov, Gennady A. Belitsky, Kirill I. Kirsanov, Marianna G. Yakubovskaya

المصدر: Cells, Vol 13, Iss 20, p 1695 (2024)

مصطلحات موضوعية: synovial sarcoma, chromosomal translocation, SS18-SSX, epigenetic changes, T-cell receptor gene therapy, targeted therapy, Cytology, QH573-671

وصف الملف: electronic resource

Relation: https://www.mdpi.com/2073-4409/13/20/1695; https://doaj.org/toc/2073-4409

URL الوصول: https://doaj.org/article/9ddb95398b384953a65821cc12e4ce2b

المؤلفون: Mendes, Marisa Vieira da Silva

مصطلحات موضوعية: ATMPs, Cell and Gene Therapy, Trends, Market Access, Regulatory Landscape, Terapias celulares e genéticas, Tendências, Acesso Comercial, Enquadramento Regulamentar

الاتاحة: https://hdl.handle.net/10316/112697

المؤلفون: Jan Pachocki, Frances Verter

المصدر: Frontiers in Immunology, Vol 15 (2024)

مصطلحات موضوعية: advanced therapy medicinal products (ATMPs), cell and gene therapy (CGT), hospital exemptions (HE), mesenchymal stromal cells (MSC), regulatory affairs, national licensing provisions, Immunologic diseases. Allergy, RC581-607

وصف الملف: electronic resource

Relation: https://www.frontiersin.org/articles/10.3389/fimmu.2024.1379134/full; https://doaj.org/toc/1664-3224

URL الوصول: https://doaj.org/article/6ec5b90b574347cc8361c85d11a73de2

المؤلفون: Anshika Jain, Gaspar E. Canepa, Mei-Ling Liou, Emily L. Fledderman, Andrei I. Chapoval, Lingzhi Xiao, Ipsita Mukherjee, Bushirat M. Balogun, Hellen Huaman-Vergara, Jeffrey A. Galvin, Princy N. Kumar, José Bordon, Marcus A. Conant, Jefferey S. Boyle

المصدر: Frontiers in Medicine, Vol 11 (2024)

مصطلحات موضوعية: Human Immunodeficiency Virus (HIV), CD4 /CD8 lymphocytes + +, AGT103-T, immunotherapy, cell and gene therapy (CGT), CCR5, Medicine (General), R5-920

وصف الملف: electronic resource

Relation: https://www.frontiersin.org/articles/10.3389/fmed.2024.1342476/full; https://doaj.org/toc/2296-858X

URL الوصول: https://doaj.org/article/20e27262bdc947c882faadf853294a85

المؤلفون: Xinwen Chen, Jingjing Du, Shaowei Yun, Chaoyou Xue, Yao Yao, Shuquan Rao

المصدر: Molecular Therapy: Nucleic Acids, Vol 35, Iss 1, Pp 102138- (2024)

مصطلحات موضوعية: MT: RNA/DNA editing, programmable genome insertion, DSB-dependent knock-in, prime editing, CRISPR-associated transposon, cell and gene therapy, Therapeutics. Pharmacology, RM1-950

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2162253124000258; https://doaj.org/toc/2162-2531

URL الوصول: https://doaj.org/article/828f5721e0e64867a6a78a6056125f68

المؤلفون: Sanchez-Guijo, Fermin, Vives, Joaquim, Ruggeri, Annalisa, Chabannon, Christian, Corbacioglu, Selim, Dolstra, Harry, Farge, Dominique, Gagelmann, Nico, Horgan, Claire, Kuball, Jurgen, Neven, Benedicte, Rintala, Tuula, Rocha, Vanderson, Sanchez-Ortega, Isabel, Snowden, John A, Zwaginga, Jaap Jan, Gnecchi, Massimiliano, Sureda, Anna

المساهمون: CTI Kuball, MS Hematologie, Cancer, Infection & Immunity, Regenerative Medicine and Stem Cells

مصطلحات موضوعية: ATMPs, benchmarking, CAR-T, cell and gene therapy, EBMT, education, EMA, Europe, ISCT, JACIE, MSC, registry, reimbursement, Genetics(clinical), Transplantation, Oncology, Cancer Research, Immunology and Allergy, Cell Biology, Immunology, Journal Article

وصف الملف: application/pdf

Relation: https://dspace.library.uu.nl/handle/1874/453261

الاتاحة: https://dspace.library.uu.nl/handle/1874/453261

المؤلفون: Dayer, Victoria W., Drummond, Michael F., Dabbous, Omar, Toumi, Mondher, Neumann, Peter, Tunis, Sean, Teich, Nelson, Saleh, Shadi, Persson, Ulf, Schulenburg, Johann-Matthias Graf von der, Malone, Daniel C., Salimullah, Tay, Sullivan, Sean D.

المصدر: Orphanet Journal of Rare Diseases 19 (2024), Nr. 1 ; Orphanet Journal of Rare Diseases

مصطلحات موضوعية: Cell and gene therapy, Coverage determination, Coverage with evidence development, Health technology assessment, Rare disease, Real world evidence, ddc:610

Relation: ESSN:1750-1172; http://dx.doi.org/10.15488/16753; https://www.repo.uni-hannover.de/handle/123456789/16880

الاتاحة: https://www.repo.uni-hannover.de/handle/123456789/16880
https://doi.org/10.15488/16753

المؤلفون: Carolyn A. Wills, Daniela Drago, Robert G. Pietrusko

المصدر: Molecular Therapy: Methods & Clinical Development, Vol 31, Iss , Pp 101125- (2023)

مصطلحات موضوعية: clinical hold, cell and gene therapy, IND, regulatory submissions, FDA, Genetics, QH426-470, Cytology, QH573-671

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S232905012300164X; https://doaj.org/toc/2329-0501

URL الوصول: https://doaj.org/article/4a1ef40c0380415c9f0f15824836295f

المؤلفون: Jinjuan Yang, Xiaoxian Zhang, Meng Kou, Boon Xuan Lian, Zhixin Chiang, Jace Chen, Xiaoya Zhou, Ziyue Li, Jinqiu Zhang, Xiao Su, Qizhou Lian

المصدر: Translational Medicine of Aging, Vol 7, Iss , Pp 98-108 (2023)

مصطلحات موضوعية: Mitochondrial cardiomyopathy, Cell and gene therapy, Pharmacological approaches, Mitochondrial augmentation therapy, mtDNA replacement therapy, Medicine

وصف الملف: electronic resource

Relation: http://www.sciencedirect.com/science/article/pii/S2468501123000135; https://doaj.org/toc/2468-5011

URL الوصول: https://doaj.org/article/90f7f2eb9ce34e87852ecafdee37d3cf

المؤلفون: Niklas Bäckel, Simon Hort, Tamás Kis, David F. Nettleton, Joseph R. Egan, John J. L. Jacobs, Dennis Grunert, Robert H. Schmitt

المصدر: Frontiers in Molecular Medicine, Vol 3 (2023)

مصطلحات موضوعية: CAR-T manufacturing, artificial intelligence, machine learning, cell and gene therapy, immunotherapy, data analytics, Computer applications to medicine. Medical informatics, R858-859.7

وصف الملف: electronic resource

Relation: https://www.frontiersin.org/articles/10.3389/fmmed.2023.1250508/full; https://doaj.org/toc/2674-0095

URL الوصول: https://doaj.org/article/91bf0e4959f147c7939554fa0cf7814f