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1Academic Journal
المؤلفون: Socheata Ly, Dimas Echeverria, Jacquelyn Sousa, Anastasia Khvorova
المصدر: Molecular Therapy: Nucleic Acids, Vol 21, Iss , Pp 991-1005 (2020)
مصطلحات موضوعية: siRNAs, chemically modified siRNAs, cholesterol conjugated siRNAs, siRNA trafficking, phosphorothioate, Therapeutics. Pharmacology, RM1-950
وصف الملف: electronic resource
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2Academic Journal
المؤلفون: Scherman, D., Rousseau, A., Bigey, P., Escriou, V.
المساهمون: Unité de Technologies Chimiques et Biologiques pour la Santé (UTCBS - UM 4 (UMR 8258 / U1022)), Ecole Nationale Supérieure de Chimie de Paris - Chimie ParisTech-PSL (ENSCP), Université Paris Sciences et Lettres (PSL)-Université Paris Sciences et Lettres (PSL)-Université Paris Descartes - Paris 5 (UPD5)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Institut de Chimie - CNRS Chimie (INC-CNRS)-Centre National de la Recherche Scientifique (CNRS)
المصدر: ISSN: 0969-7128.
مصطلحات موضوعية: CHEMICALLY-MODIFIED SIRNAS, IN-VIVO, CATIONIC LIPOSOME, SYSTEMIC DELIVERY, RNA INTERFERENCE, MACULAR DEGENERATION, LIPOPLEXES, DNA, EFFICIENT, PF-04523655, [SDV.BIO]Life Sciences [q-bio]/Biotechnology
Relation: hal-03292055; https://cnrs.hal.science/hal-03292055; WOS: 000398055600006
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3
المؤلفون: Virginie Escriou, Daniel Scherman, Pascal Bigey, Antoine Rousseau
المساهمون: Unité de Technologies Chimiques et Biologiques pour la Santé (UTCBS - UM 4 (UMR 8258 / U1022)), Ecole Nationale Supérieure de Chimie de Paris - Chimie ParisTech-PSL (ENSCP), Université Paris sciences et lettres (PSL)-Université Paris sciences et lettres (PSL)-Université Paris Descartes - Paris 5 (UPD5)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Centre National de la Recherche Scientifique (CNRS)-Institut de Chimie du CNRS (INC)
المصدر: Gene Therapy
Gene Therapy, Nature Publishing Group, 2017, 24 (3), pp.151-156. ⟨10.1038/gt.2017.6⟩مصطلحات موضوعية: 0301 basic medicine, Small interfering RNA, Ribonucleotide, [SDV.BIO]Life Sciences [q-bio]/Biotechnology, EFFICIENT, CHEMICALLY-MODIFIED SIRNAS, 02 engineering and technology, Pharmacology, Biology, Small hairpin RNA, 03 medical and health sciences, Transcription (biology), RNA interference, Genetics, Gene silencing, Animals, Humans, SYSTEMIC DELIVERY, RNA, Small Interfering, Molecular Biology, IN-VIVO, Messenger RNA, Clinical Trials as Topic, PF-04523655, CATIONIC LIPOSOME, LIPOPLEXES, DNA, 021001 nanoscience & nanotechnology, MACULAR DEGENERATION, RNA silencing, 030104 developmental biology, RNAi Therapeutics, RNA INTERFERENCE, Molecular Medicine, Nanoparticles, 0210 nano-technology
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4Academic Journal
المؤلفون: Huang, Yuanyu, Cheng, Qiang, Ji, Jia-Li, Zheng, Shuquan, Du, Lili, Meng, Lingwei, Wu, Yidi, Zhao, Deyao, Wang, Xiaoxia, Lai, Li, Cao, Huiqing, Xiao, Kai, Gao, Shan, Liang, Zicai
المساهمون: Huang, YY, Liang, ZC (reprint author), Peking Univ, Inst Mol Med, Beijing 100871, Peoples R China., Liang, ZC (reprint author), Collaborat Innovat Ctr Chem Sci & Engn Tianjin, Tianjin 300072, Peoples R China., Peking Univ, Inst Mol Med, Beijing 100871, Peoples R China., Suzhou Ribo Life Sci Co Ltd, Suzhou 215300, Jiangsu, Peoples R China., Collaborat Innovat Ctr Chem Sci & Engn Tianjin, Tianjin 300072, Peoples R China., Sichuan Univ, Natl Chengdu Ctr Safety Evaluat Drugs, West China Hosp, State Key Lab Biotherapy,Collaborat Innovat Ctr B, Chengdu 610041, Peoples R China.
المصدر: SCI ; PubMed
مصطلحات موضوعية: siRNA, pharmacokinetics, submandibular gland, biodistribution, CHEMICALLY-MODIFIED SIRNAS, TUMOR-TARGETED DELIVERY, PLURIPOTENT STEM-CELLS, IN-VIVO, RNA INTERFERENCE, POLY(2-DIMETHYLAMINOETHYL METHACRYLATE), NONHUMAN-PRIMATES, NANOPARTICLES, DESATURASE
Relation: THERANOSTICS.2016,6(10),1528-1541.; 1436816; http://hdl.handle.net/20.500.11897/492548; WOS:000378596800005
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5
المؤلفون: Musa Marimani, Stefan Bernhardt, Virginie Escriou, Joachim W. Engels, Patrick Arbuthnot, Abdullah Ely, Maximilian C.R. Buff, Daniel Scherman
المساهمون: University of the Witwatersrand [Johannesburg] (WITS), Institute of Organic Chemistry and Chemical Biology, Goethe-Universität Frankfurt am Main, Unité de Technologies Chimiques et Biologiques pour la Santé (UTCBS - UM 4 (UMR 8258 / U1022)), Ecole Nationale Supérieure de Chimie de Paris - Chimie ParisTech-PSL (ENSCP), Université Paris sciences et lettres (PSL)-Université Paris sciences et lettres (PSL)-Université Paris Descartes - Paris 5 (UPD5)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Centre National de la Recherche Scientifique (CNRS)-Institut de Chimie du CNRS (INC)
المصدر: Journal of Controlled Release
Journal of Controlled Release, Elsevier, 2015, 209, pp.198-206. ⟨10.1016/j.jconrel.2015.04.042⟩مصطلحات موضوعية: EXPRESSION, Small interfering RNA, Hepatitis B virus, [SDV.BIO]Life Sciences [q-bio]/Biotechnology, Polymers, ADENOVIRUS VECTORS, Pharmaceutical Science, CHEMICALLY-MODIFIED SIRNAS, Mice, Transgenic, Biology, medicine.disease_cause, Virus Replication, Guanidines, Virus, 03 medical and health sciences, 0302 clinical medicine, RNA interference, In vivo, [SDV.MHEP.MI]Life Sciences [q-bio]/Human health and pathology/Infectious diseases, HEPATOCELLULAR-CARCINOMA, medicine, NANOPARTICLES, Animals, VITRO, RNA, Messenger, RNA, Small Interfering, 030304 developmental biology, RNA Cleavage, 0303 health sciences, Hepatitis B Surface Antigens, Polyglutamate, MRNA cleavage, DNA, Virology, SMALL INTERFERING RNAS, 3. Good health, IN-VIVO DELIVERY, Viral replication, Liver, 030220 oncology & carcinogenesis, Liposomes, Cytokines, RNA, Viral, Plasmids
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6Academic Journal
المؤلفون: Marimani, Musa D., Ely, Abdullah, Buff, Maximilian C. R., Bernhardt, Stefan, Engels, Joachim W., Scherman, Daniel, Escriou, Virginie, Arbuthnot, Patrick
المساهمون: University of the Witwatersrand Johannesburg (WITS), Institute of Organic Chemistry and Chemical Biology, Goethe-Universität Frankfurt am Main, Unité de Technologies Chimiques et Biologiques pour la Santé (UTCBS - UM 4 (UMR 8258 / U1022)), Ecole Nationale Supérieure de Chimie de Paris - Chimie ParisTech-PSL (ENSCP), Université Paris Sciences et Lettres (PSL)-Université Paris Sciences et Lettres (PSL)-Université Paris Descartes - Paris 5 (UPD5)-Institut National de la Santé et de la Recherche Médicale (INSERM)-Institut de Chimie - CNRS Chimie (INC-CNRS)-Centre National de la Recherche Scientifique (CNRS)
المصدر: ISSN: 0168-3659.
مصطلحات موضوعية: CHEMICALLY-MODIFIED SIRNAS, SMALL INTERFERING RNAS, IN-VIVO DELIVERY, HEPATOCELLULAR-CARCINOMA, ADENOVIRUS VECTORS, LIVER, VITRO, DNA, NANOPARTICLES, EXPRESSION, [SDV.BIO]Life Sciences [q-bio]/Biotechnology, [SDV.MHEP.MI]Life Sciences [q-bio]/Human health and pathology/Infectious diseases
Relation: hal-03292043; https://cnrs.hal.science/hal-03292043; WOS: 000355674300021