المؤلفون: Anna J Kordala, Jessica Stoodley, Nina Ahlskog, Muhammad Hanifi, Antonio Garcia Guerra, Amarjit Bhomra, Wooi Fang Lim, Lyndsay M Murray, Kevin Talbot, Suzan M Hammond, Matthew JA Wood, Carlo Rinaldi

المصدر: EMBO Molecular Medicine, Vol 15, Iss 11, Pp 1-16 (2023)

مصطلحات موضوعية: nusinersen, PRMT inhibitor, small molecule, spinal muscular atrophy, Medicine (General), R5-920, Genetics, QH426-470

وصف الملف: electronic resource

Relation: https://doaj.org/toc/1757-4676; https://doaj.org/toc/1757-4684

URL الوصول: https://doaj.org/article/0a6be327d14849d1ae2a1fc49bf73886

المؤلفون: Olivier G. de Jong, Daniel E. Murphy, Imre Mäger, Eduard Willms, Antonio Garcia-Guerra, Jerney J. Gitz-Francois, Juliet Lefferts, Dhanu Gupta, Sander C. Steenbeek, Jacco van Rheenen, Samir El Andaloussi, Raymond M. Schiffelers, Matthew J. A. Wood, Pieter Vader

المصدر: Nature Communications, Vol 11, Iss 1, Pp 1-13 (2020)

مصطلحات موضوعية: Science

وصف الملف: electronic resource

Relation: https://doaj.org/toc/2041-1723

URL الوصول: https://doaj.org/article/1db2023ed1d94f558ace5b4d70bad252

المؤلفون: Olivier G. de Jong, Daniel E. Murphy, Imre Mäger, Eduard Willms, Antonio Garcia-Guerra, Jerney J. Gitz-Francois, Juliet Lefferts, Dhanu Gupta, Sander C. Steenbeek, Jacco van Rheenen, Samir El Andaloussi, Raymond M. Schiffelers, Matthew J. A. Wood, Pieter Vader

المصدر: Nature Communications, Vol 11, Iss 1, Pp 1-1 (2020)

مصطلحات موضوعية: Science

Relation: https://doi.org/10.1038/s41467-020-15347-0; https://doaj.org/toc/2041-1723; https://doaj.org/article/c79299af34a74ba6b50b6a6e5e719242

الاتاحة: https://doi.org/10.1038/s41467-020-15347-0
https://doaj.org/article/c79299af34a74ba6b50b6a6e5e719242

المؤلفون: Matthew J.A. Wood, Raymond M. Schiffelers, Dhanu Gupta, Samir El Andaloussi, Olivier G. de Jong, Antonio Garcia-Guerra, Jerney J. Gitz-Francois, Juliet Lefferts, Sander C. Steenbeek, Jacco van Rheenen, Imre Mäger, Pieter Vader, Daniel E. Murphy, Eduard Willms

المصدر: Nature Communications, Vol 11, Iss 1, Pp 1-1 (2020)

مصطلحات موضوعية: Multidisciplinary, Chemistry, Science, Cell, General Physics and Astronomy, RNA, General Chemistry, Extracellular vesicle, General Biochemistry, Genetics and Molecular Biology, Cell biology, medicine.anatomical_structure, medicine, CRISPR, lcsh:Q, lcsh:Science

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::f624691f3ea572ad151d544ef7645592
https://doaj.org/article/c79299af34a74ba6b50b6a6e5e719242

المؤلفون: John F. Morris, Samir El-Andaloussi, Mark A. Behlke, Aurélie Goyenvalle, Matthew J.A. Wood, Graham McClorey, Yoshitsugu Aoki, Amer F. Saleh, Leif Benner, Joel Z. Nordin, Anna M.L. Coenen-Stass, Liz O'Donovan, Christian J. Leumann, Taavi Lehto, Antonio Garcia-Guerra, Siamon Gordon, Michael J. Gait, Kariem Ezzat, Taeyoung Koo, Branislav Dugovic

المصدر: Ahmed, Kariem; Aoki, Yoshitsugu; Koo, Taeyoung; McClorey, Graham; Benner, Leif; Coenen-Stass, Anna; O'Donovan, Liz; Lehto, Taavi; Garciaguerra, Antonio; Nordin, Joel Zacharias; Saleh, Amer F.; Behlke, Mark A.; Morris, John; Goyenvalle, Aurelie; Dugovic, Branislav; Leumann, Christian Joerg; Gordon, Siamon; Gait, Michael J.; El-Andaloussi, Samir and Wood, Matthew J. A. (2015). Self-assembly into nanoparticles is essential for receptor mediated uptake of therapeutic antisense oligonucleotides. Nano letters, 15(7), pp. 4364-4374. American Chemical Society 10.1021/acs.nanolett.5b00490 <http://dx.doi.org/10.1021/acs.nanolett.5b00490>

مصطلحات موضوعية: Morpholino, Duchenne muscular dystrophy, Bioengineering, Micelle, Article, Cell Line, chemistry.chemical_compound, Mice, 540 Chemistry, medicine, Animals, General Materials Science, Micelles, Mice, Knockout, Base Sequence, Oligonucleotide, Mechanical Engineering, Scavenger Receptors, Class A, General Chemistry, Receptor-mediated endocytosis, Exons, Genetic Therapy, Oligonucleotides, Antisense, Condensed Matter Physics, medicine.disease, Exon skipping, Mice, Inbred C57BL, Muscular Dystrophy, Duchenne, chemistry, Biochemistry, Cell culture, Biophysics, 570 Life sciences, biology, Nanoparticles, DNA

وصف الملف: application/pdf

URL الوصول: https://explore.openaire.eu/search/publication?articleId=doi_dedup___::5f63c829ff79f84d4fe2029f153b043b
https://pubmed.ncbi.nlm.nih.gov/26042553