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1Dissertation/ Thesis
المؤلفون: Hoffmann, Tobias
المساهمون: University/Department: Universitat Pompeu Fabra. Departament de Ciències Experimentals i de la Salut
Thesis Advisors: Valcárcel, J. (Juan)
المصدر: TDX (Tesis Doctorals en Xarxa)
مصطلحات موضوعية: RBM10, Bladder tumor, Alternative splicing, Antisense oligonucleotides, Cancer, Vejiga, Oligonucleótidos antisentido, Cáncer
Time: 616.6
وصف الملف: application/pdf
URL الوصول: http://hdl.handle.net/10803/671595
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2Academic Journal
المؤلفون: Afsana Bhuiyan
المصدر: Exploration of Neuroprotective Therapy, Vol 4, Iss 6, Pp 485-496 (2024)
مصطلحات موضوعية: repeat expansion diseases (reds), gene therapy, antisense oligonucleotides (asos), rna interference (rnai), crispr/cas9 gene editing, Neurology. Diseases of the nervous system, RC346-429
وصف الملف: electronic resource
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3Academic Journal
المؤلفون: LIU Siyu, LAI Yuezhao, GUO Wenting, CHEN Xuejin
المصدر: Shiyan dongwu yu bijiao yixue, Vol 44, Iss 6, Pp 613-625 (2024)
مصطلحات موضوعية: duchenne muscular dystrophy, dystrophin, nucleic acid drugs, antisense oligonucleotides, gene therapy, exon skipping, Medicine
وصف الملف: electronic resource
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4Academic Journal
المصدر: RNA Biology, Vol 21, Iss 1, Pp 16-35 (2024)
مصطلحات موضوعية: Alternative splicing, splicing factors, long noncoding RNA, cancer, antisense oligonucleotides, Genetics, QH426-470
وصف الملف: electronic resource
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5
المؤلفون: Modder, Melanie, Panhuis, Wietse In Het, Li, Mohan, Afkir, Salwa, Dorn, Alexandra L., Pronk, Amanda C. M., Streefland, Trea C. M., Lalai, Reshma A., Pierrou, Stefan, Nilsson, Stefan K., Olivecrona, Gunilla, Kooijman, Sander, Rensen, Patrick C. N., Schonke, Milena
المصدر: Cardiovascular Research. 120(17):2179-2190
مصطلحات موضوعية: Hyperlipidaemia, Atherosclerosis, Angptl3, Angptl4, Antisense oligonucleotides
وصف الملف: electronic
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6Academic Journal
المؤلفون: Feichtenschlager, Valentin, Chen, Linan, Zheng, Yixuan James, Ho, Wilson, Sanlorenzo, Martina, Vujic, Igor, Fewings, Eleanor, Lee, Albert, Chen, Christopher, Callanan, Ciara, Lin, Kevin, Qu, Tiange, Hohlova, Dasha, Vujic, Marin, Hwang, Yeonjoo, Lai, Kevin, Chen, Stephanie, Nguyen, Thuan, Muñoz, Denise P, Kohwi, Yoshinori, Posch, Christian, Daud, Adil, Rappersberger, Klemens, Kohwi-Shigematsu, Terumi, Coppé, Jean-Philippe, Ortiz-Urda, Susana
المصدر: Molecular Cancer. 23(1)
مصطلحات موضوعية: Biomedical and Clinical Sciences, Oncology and Carcinogenesis, Genetics, Cancer, 5.1 Pharmaceuticals, Humans, Mice, Animals, Melanoma, RNA, Long Noncoding, Apoptosis, Oligonucleotides, Antisense, Cell Line, Tumor, Membrane Proteins, GTP Phosphohydrolases, T-RECS, lncRNA, MAPK-pathway, hnRNPA2/B1, Antisense oligonucleotides, HT-KAM, Oncology & Carcinogenesis, Biochemistry and cell biology, Oncology and carcinogenesis
وصف الملف: application/pdf
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7Academic Journal
المؤلفون: Araldi, Dionéia, Sucher, Anatol, Kober, Kord, Ohara, Peter, Levine, Jon, Bogen, Oliver
مصطلحات موضوعية: Antisense oligonucleotides, Isolectin B4, hyperalgesic priming, ligand-conjugated antisense, nociceptors, pain, Rats, Animals, Lectins, Nociceptors, Streptavidin, Rats, Sprague-Dawley, Nerve Fibers, Unmyelinated, Oligonucleotides, Antisense, Ganglia, Spinal
وصف الملف: application/pdf
URL الوصول: https://escholarship.org/uc/item/83s1v8sz
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8Academic Journal
المؤلفون: Monika Szelest, Krzysztof Giannopoulos
المصدر: BMC Genomics, Vol 25, Iss 1, Pp 1-18 (2024)
مصطلحات موضوعية: Splicing, Antisense oligonucleotides, Therapy resistance, Leukemia, Splicing modulators, Biotechnology, TP248.13-248.65, Genetics, QH426-470
وصف الملف: electronic resource
Relation: https://doaj.org/toc/1471-2164
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9Academic Journal
المؤلفون: Young Hoon Jung, Yun Ji Lee, Tam Dao, Kyung Hee Jung, Junjie Yu, Ah-Reum Oh, Yelin Jeong, HyunJoon Gi, Young Un Kim, Dongryeol Ryu, Michele Carrer, Utpal B. Pajvani, Sang Bae Lee, Soon-Sun Hong, KyeongJin Kim
المصدر: Clinical and Molecular Hepatology, Vol 30, Iss 4, Pp 895-913 (2024)
مصطلحات موضوعية: hcc, kctd17, ras, lztr1, antisense oligonucleotides, Diseases of the digestive system. Gastroenterology, RC799-869
وصف الملف: electronic resource
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10Academic Journal
المؤلفون: Olga Golounina, Ildar Minniakhmetov, Ramil Salakhov, Rita Khusainova, Ekaterina Zakharova, Igor Bychkov, Natalia Mokrysheva
المصدر: Frontiers in Endocrinology, Vol 16 (2025)
مصطلحات موضوعية: endocrine diseases, molecular therapy, RNA therapeutics, antisense oligonucleotides (ASOs), small interfering RNA (siRNA), N-of-1, Diseases of the endocrine glands. Clinical endocrinology, RC648-665
وصف الملف: electronic resource
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11Academic Journal
المؤلفون: Cassandra Yun, Kazuki Fukami, Raku Shinkyo, Rongrong (Rosa) Jiang
المصدر: Frontiers in Pharmacology, Vol 15 (2025)
مصطلحات موضوعية: antisense oligonucleotides, plasma protein binding, ultrafiltration, MOE, PMO, binding saturation, Therapeutics. Pharmacology, RM1-950
وصف الملف: electronic resource
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12Academic Journal
المؤلفون: Inna Shomer, Nofar Mor, Shaul Raviv, Noga Budick-Harmelin, Tanya Matchevich, Sharon Avkin-Nachum, Yoach Rais, Rebecca Haffner-Krausz, Ariela Haimovich, Aviv Ziv, Reut Fluss, Bruria Ben-Ze’ev, Gali Heimer, Denis N. Silachev, Vladimir L. Katanaev, Dan Dominissini
المصدر: Molecular Therapy: Nucleic Acids, Vol 36, Iss 1, Pp 102432- (2025)
مصطلحات موضوعية: MT: Oligonucleotides: Therapies and Applications, GNAO1, personalized ASOs, antisense oligonucleotides, ASOs, individualized ASOs, Therapeutics. Pharmacology, RM1-950
Relation: http://www.sciencedirect.com/science/article/pii/S2162253124003196; https://doaj.org/toc/2162-2531; https://doaj.org/article/d79b5d60474b446aa200fe6a1350f381
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13Academic Journal
المؤلفون: Sajid Naeem, Ju Zhang, Yang Zhang, Yu Wang
المصدر: Molecular Therapy: Nucleic Acids, Vol 36, Iss 1, Pp 102440- (2025)
مصطلحات موضوعية: MT: Oligonucleotides: Therapies and Applications, nucleic acid therapeutics, antisense oligonucleotides, small interfering RNA, aptamer, messenger RNA, Therapeutics. Pharmacology, RM1-950
Relation: http://www.sciencedirect.com/science/article/pii/S2162253124003275; https://doaj.org/toc/2162-2531; https://doaj.org/article/56f7d10d037c4b2aa6e92962b44bb246
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14Academic Journal
المؤلفون: Xiujie Xie, H. Patrick Macknight, Amy L. Lu, Charles E. Chalfant
المصدر: Molecular Therapy: Nucleic Acids, Vol 36, Iss 1, Pp 102412- (2025)
مصطلحات موضوعية: MT: Non-coding RNAs, long non-coding RNAs, RNA splicing, non-small cell lung cancers, antisense oligonucleotides, CDKN2A, Therapeutics. Pharmacology, RM1-950
Relation: http://www.sciencedirect.com/science/article/pii/S2162253124002993; https://doaj.org/toc/2162-2531; https://doaj.org/article/f05bde14134b4a86860d52be74b17c78
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15Academic Journal
المؤلفون: Shuqi Wu, Fang Nan, Kewen Zhang, Wan Hao, Di Shi, Yang Li, Wei Deng, Nur Jarhen, Kaixuan Li, Yunyun Xiao, Jun Li, Xiao Lin
المصدر: Aggregate, Vol 5, Iss 6, Pp n/a-n/a (2024)
مصطلحات موضوعية: antisense oligonucleotides, cartilage metabolism, drug delivery, IrO2 nanozyme, osteoarthritis treatment, reactive oxygen species scavenging, Chemistry, QD1-999, Biology (General), QH301-705.5
وصف الملف: electronic resource
Relation: https://doaj.org/toc/2692-4560
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16Academic Journal
المؤلفون: Johanna Hörberg, Antonio Carlesso, Anna Reymer
المصدر: Molecular Therapy: Nucleic Acids, Vol 35, Iss 4, Pp 102351- (2024)
مصطلحات موضوعية: MT: Oligonucleotides: Therapies and Applications, antisense oligonucleotides, RNA hairpin, molecular recognition, molecular dynamics simulations, Therapeutics. Pharmacology, RM1-950
وصف الملف: electronic resource
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17Academic Journal
المؤلفون: Bao Nengcheng, Wang Zhechao, Fu Jiayan, Dong Haiyang, Jin Yongfeng
المصدر: Acta Biochimica et Biophysica Sinica, Vol 57, Pp 3-21 (2024)
مصطلحات موضوعية: aberrant splicing, antisense oligonucleotides (ASOs), RNA secondary structure, RNA-targeted therapy, splicing regulation, Biochemistry, QD415-436, Genetics, QH426-470
وصف الملف: electronic resource
Relation: https://doaj.org/toc/1672-9145
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18Academic Journal
المؤلفون: S. K. Miroshnichenko, O. A. Patutina, M. A. Zenkova
المصدر: Биопрепараты: Профилактика, диагностика, лечение, Vol 24, Iss 2, Pp 140-156 (2024)
مصطلحات موضوعية: mirna, mirna-targeted oligonucleotide constructs, carcinogenesis, small non-coding rna, malignant neoplasms, mirna-masking oligonucleotides, crispr/cas, mirna sponges, antisense oligonucleotides, mirnases, Biotechnology, TP248.13-248.65, Medicine
وصف الملف: electronic resource
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19Academic Journal
المؤلفون: Tommaso Tabaglio, Taniya Agarwal, Wei Yuan Cher, Jin Rong Ow, Ah Keng Chew, Priscila Yun Qian Sun, Raja Sekhar Reddy Gurrampati, Hongfang Lu, Praveena Naidu, Hong Kai Ng, Xavier Le Guezennec, Shi Yan Ng, Manikandan Lakshmanan, Ernesto Guccione, Keng Boon Wee
المصدر: Molecular Therapy: Nucleic Acids, Vol 36, Iss 1, Pp 102422- (2025)
مصطلحات موضوعية: MT: Oligonucleotides: Therapies and Applications, antisense oligonucleotides, nucleic acid therapeutics, reporter system, nucleic acid chemical modifications, mixmers, Therapeutics. Pharmacology, RM1-950
وصف الملف: electronic resource
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20Academic Journal
المؤلفون: Kunihiko Kanatsu, Yoshinori Takahashi, Tetsuya Sakaguchi, Dae-Shik Kim, Miki Murota, Mingde Shan, Kazuki Fukami, Wataru Itano, Kenji Kikuta, Hikaru Yoshimura, Toshiki Kurokawa, Yuko Nagayama, Rena Ishikawa, Ryo Dairiki, Zhi Zhou, Kristen Sanders, Jacob Stupalski, So Yasui, Diana Liu, Farid Benayoud, Hui Fang, Enxuan Jing, Makoto Ogo, Francis G. Fang, John Wang, Hyeong-wook Choi
المصدر: Molecular Therapy: Nucleic Acids, Vol 36, Iss 1, Pp 102404- (2025)
مصطلحات موضوعية: MT: Oligonucleotides: Therapies and Applications, tau, tauopathy, antisense oligonucleotides, PMO, gapmer, Therapeutics. Pharmacology, RM1-950
وصف الملف: electronic resource