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1Academic Journal
المؤلفون: Katherine A. White, Hemanth R. Nelvagal, Timothy A. Poole, Bin Lu, Tyler B. Johnson, Samantha Davis, Melissa A. Pratt, Jon Brudvig, Ana B. Assis, Shibi Likhite, Kathrin Meyer, Brian K. Kaspar, Jonathan D. Cooper, Shaomei Wang, Jill M. Weimer
المصدر: Molecular Therapy: Methods & Clinical Development, Vol 20, Iss , Pp 497-507 (2021)
مصطلحات موضوعية: CLN6, Batten disease, AAV9, NCL, Gene therapy, retina, Genetics, QH426-470, Cytology, QH573-671
وصف الملف: electronic resource
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2
المؤلفون: Tyler B. Johnson, Ana B. Assis, Jon Brudvig, Samantha Davis, Jonathan D. Cooper, Katherine A. White, Timothy A. Poole, Brian K. Kaspar, Shaomei Wang, Hemanth R. Nelvagal, Bin Lu, Melissa A. Pratt, Shibi Likhite, Jill M. Weimer, Kathrin Meyer
المصدر: Molecular Therapy. Methods & Clinical Development
Molecular Therapy: Methods & Clinical Development, Vol 20, Iss, Pp 497-507 (2021)مصطلحات موضوعية: Retinal degeneration, Batten disease, retina, vision, Visual acuity, lcsh:QH426-470, Thalamus, Gene therapy, Parenchyma, Genetics, medicine, lcsh:QH573-671, Molecular Biology, Retina, lcsh:Cytology, business.industry, Superior colliculus, NCL, CLN6, medicine.disease, lcsh:Genetics, medicine.anatomical_structure, Cerebral cortex, ICV, Molecular Medicine, Original Article, medicine.symptom, business, AAV9, Neuroscience