نتائج البحث - "CYSTIC fibrosis"

1

Academic Journal

Formulate a concentrated highly branched poly(β-amino ester)/DNA polyplex – one step closer to application in lung cystic fibrosis disease.

المؤلفون: Qiu, Bei¹ (AUTHOR), Li, Yinghao¹ (AUTHOR), He, Zhonglei^2,3 (AUTHOR), Li, Zishan¹ (AUTHOR), Terreau, Sébastien¹ (AUTHOR), Wang, Xianqing¹ (AUTHOR), Lyu, Jing¹ (AUTHOR), Wang, Wenxin^1,2,3 (AUTHOR) wenxin.wang@ucd.ie, Lara-Sáez, Irene¹ (AUTHOR) irene.lara-saez@ucd.ie

المصدر: Drug Development & Industrial Pharmacy. Dec2024, p1-11. 11p. 6 Illustrations.

مصطلحات موضوعية: CYSTIC fibrosis transmembrane conductance regulator, PULMONARY fibrosis, CYSTIC fibrosis, EPITHELIAL cells, GENE therapy

2

Dissertation/ Thesis

Estudio de la modulación de los receptores adenosinérgicos como tratamiento complementario en la Fibrosis Quística

المؤلفون: Barranco Bartolomé, Paula

المساهمون: University/Department: Universitat de Barcelona. Facultat de Biologia

Thesis Advisors: Garcia Arumí, Elena, Tizzano, Eduardo F., Castro Palomino, Julio, Balcells Comas, Susana

المصدر: TDX (Tesis Doctorals en Xarxa)

مصطلحات موضوعية: Medicina personalitzada, Medicina Individualizada, Personalized medicine, Fibrosi quística, Fibrosis quística, Cystic fibrosis, Receptors cel·lulars, Receptores celulares, Cell receptors, Ciències Experimentals i Matemàtiques

وصف الملف: application/pdf

URL الوصول: http://hdl.handle.net/10803/691413

View record in TDX

3

Dissertation/ Thesis

Efecto del bicarbonato nebulizado en la vía aérea de pacientes pediátrico con Fibrosis Quística

المؤلفون: Vasquez Pérez, Amalui

المساهمون: University/Department: Universitat Rovira i Virgili. Departament de Medicina i Cirurgia

Thesis Advisors: Closa Monasterolo, Ricardo, Bosque Garcia, Montserrat, Parada Ricart, Esther

المصدر: TDX (Tesis Doctorals en Xarxa)

مصطلحات موضوعية: pH de l'ASL, Fibrosis Quística, Bicarbonat nebulitzat, Bicarbonato nebulizado, ASL pH, Cystic fibrosis, Inhaled bicarbonate, Ciències de la Salut

Time: 616.2

وصف الملف: application/pdf

URL الوصول: http://hdl.handle.net/10803/691359

View record in TDX

4

Academic Journal

Impact of Cystic Fibrosis Transmembrane Conductance Regulator Modulators on Maternal Outcomes During and After Pregnancy.

المؤلفون: Jain, Raksha¹ (AUTHOR) Raksha.Jain@utsouthwestern.edu, Peng, Giselle¹ (AUTHOR), Lee, MinJae¹ (AUTHOR), Keller, Ashley¹ (AUTHOR), Cosmich, Sophia¹ (AUTHOR), Reddy, Sarthak² (AUTHOR), West, Natalie E.³ (AUTHOR), Kazmerski, Traci M.⁴ (AUTHOR), Goralski, Jennifer L.⁵ (AUTHOR), Flume, Patrick A.⁶ (AUTHOR), Roe, Andrea H.⁷ (AUTHOR), Hadjiliadis, Denis⁷ (AUTHOR), Uluer, Ahmet⁸ (AUTHOR), Mody, Sheila⁹ (AUTHOR), Ladores, Sigrid¹⁰ (AUTHOR), Taylor-Cousar, Jennifer L.^11,12 (AUTHOR)

المصدر: CHEST. Feb2025, Vol. 167 Issue 2, p348-361. 14p.

مصطلحات موضوعية: *CYSTIC fibrosis transmembrane conductance regulator, *PREGNANCY outcomes, *CYSTIC fibrosis, *PSEUDOMONAS aeruginosa, *REGRESSION analysis

5

Academic Journal

VX-770, C act -A1, and Increased Intracellular cAMP Have Distinct Acute Impacts upon CFTR Activity.

المؤلفون: Nick, Heidi J.¹ (AUTHOR) nickh@njhealth.org, Christeson, Sarah E.¹ (AUTHOR) christesons@njhealth.org, Bratcher, Preston E.^1,2 (AUTHOR) bratcherp@njhealth.org

المصدر: International Journal of Molecular Sciences. Jan2025, Vol. 26 Issue 2, p471. 16p.

مصطلحات موضوعية: *CYSTIC fibrosis transmembrane conductance regulator, *ION transport (Biology), *ION bombardment, *CYSTIC fibrosis, *CELL physiology

Full Text Finder

6

Academic Journal

Human Induced Lung Organoids: A Promising Tool for Cystic Fibrosis Drug Screening.

المؤلفون: Demchenko, Anna¹ (AUTHOR) demchenkoanna@med-gen.ru, Balyasin, Maxim^2,3 (AUTHOR), Nazarova, Aleksandra¹ (AUTHOR), Grigorieva, Olga¹ (AUTHOR), Panchuk, Irina¹ (AUTHOR), Kondrateva, Ekaterina¹ (AUTHOR), Tabakov, Vyacheslav⁴ (AUTHOR), Schagina, Olga⁵ (AUTHOR), Amelina, Elena⁶ (AUTHOR), Smirnikhina, Svetlana¹ (AUTHOR) smirnikhinas@gmail.com

المصدر: International Journal of Molecular Sciences. Jan2025, Vol. 26 Issue 2, p437. 16p.

مصطلحات موضوعية: *PLURIPOTENT stem cells, *CYSTIC fibrosis, *CYSTIC fibrosis transmembrane conductance regulator, *LUNGS, *SENSITIVITY & specificity (Statistics), *PREDICTION models

Full Text Finder

7

Academic Journal

Bridging the gap: Challenging lung infections and clinical trial development in cystic fibrosis.

المؤلفون: Downey, Damian G.¹ (AUTHOR) d.downey@qub.ac.uk, Simmonds, Nicholas J.^2,3 (AUTHOR), van-Koningsbruggen-Rietschel, Silke^4,5 (AUTHOR), Bend, Jutta⁶ (AUTHOR), Dunlevy, Fiona⁷ (AUTHOR), Hill, Kate^7,8 (AUTHOR), Dupont, Lieven⁹ (AUTHOR)

المصدر: Journal of Cystic Fibrosis. Jan2025, Vol. 24 Issue 1, p79-82. 4p.

مصطلحات موضوعية: *CYSTIC fibrosis, *EXPERIMENTAL design, *LUNG infections, *CYSTIC fibrosis transmembrane conductance regulator, *CLINICAL trials

8

Academic Journal

A phase I study assessing the safety and tolerability of SPL84, an inhaled antisense oligonucleotide for treatment of cystic fibrosis patients with the 3849 +10kb C->T.

المؤلفون: Caraco, Yoseph¹ (AUTHOR), Wanounou, Maor¹ (AUTHOR), Blotnick, Simcha¹ (AUTHOR), Friedman, Lital² (AUTHOR), Cohen, Asaf² (AUTHOR), Hart, Gili^1,2 (AUTHOR) gili@splisense.com, Kerem, Eitan³ (AUTHOR)

المصدر: Journal of Cystic Fibrosis. Jan2025, Vol. 24 Issue 1, p66-71. 6p.

مصطلحات موضوعية: *CYSTIC fibrosis transmembrane conductance regulator, *RNA splicing, *RNA, *NUCLEIC acids, *CYSTIC fibrosis, *VITAL signs

9

Academic Journal

A W1282X cystic fibrosis mouse allows the study of pharmacological and gene-editing therapeutics to restore CFTR function.

المؤلفون: Michicich, Margaret¹ (AUTHOR), Traylor, Zachary¹ (AUTHOR), McCoy, Caitlan¹ (AUTHOR), Valerio, Dana M.¹ (AUTHOR), Wilson, Alma¹ (AUTHOR), Schneider, Molly¹ (AUTHOR), Davis, Sakeena¹ (AUTHOR), Barabas, Amanda¹ (AUTHOR), Mann, Rachel J.¹ (AUTHOR), LePage, David F.¹ (AUTHOR), Jiang, Weihong¹ (AUTHOR), Drumm, Mitchell L.¹ (AUTHOR), Kelley, Thomas J.¹ (AUTHOR), Conlon, Ronald A.¹ (AUTHOR), Hodges, Craig A.¹ (AUTHOR) craig.hodges@case.edu

المصدر: Journal of Cystic Fibrosis. Jan2025, Vol. 24 Issue 1, p164-174. 11p.

مصطلحات موضوعية: *CYSTIC fibrosis transmembrane conductance regulator, *NONSENSE mutation, *GENOME editing, *CYSTIC fibrosis, *SHORT circuits

10

Academic Journal

Elexacaftor/tezacaftor/ivacaftor efficacy in intestinal organoids with rare CFTR variants in comparison to CFTR-F508del and CFTR-wild type controls.

المؤلفون: Kroes, Suzanne^1,2 (AUTHOR), Bierlaagh, Marlou C.¹ (AUTHOR), Lefferts, Juliet W.^1,2 (AUTHOR), Boni, Alessandra³ (AUTHOR), Muilwijk, Danya¹ (AUTHOR), Viscomi, Carla³ (AUTHOR), Keijzer-Nieuwenhuijze, Natascha D.A.^1,2 (AUTHOR), Cristiani, Luca³ (AUTHOR), Niemöller, Paul J.^1,2 (AUTHOR), Verburg, Tibo F.^1,2 (AUTHOR), Cutrera, Renato³ (AUTHOR), Fiocchi, Alessandro G.⁴ (AUTHOR), Lucidi, Vincenzina⁵ (AUTHOR), van der Ent, Cornelis K.¹ (AUTHOR), Beekman, Jeffrey M.¹ (AUTHOR) j.beekman@umcutrecht.nl, Alghisi, Federico³ (AUTHOR), Ciciriello, Fabiana^1,3 (AUTHOR) fabiana.ciciriello@opbg.net

المصدر: Journal of Cystic Fibrosis. Jan2025, Vol. 24 Issue 1, p175-182. 8p.

مصطلحات موضوعية: *CYSTIC fibrosis transmembrane conductance regulator, *REGULATOR genes, *CYSTIC fibrosis, *GENETIC disorders

11

Academic Journal

Theranostics vs theratyping or theranostics plus theratyping?

المؤلفون: Amaral, Margarida D.¹ (AUTHOR) mdamaral@fc.ul.pt, Pankonien, Ines¹ (AUTHOR)

المصدر: Journal of Cystic Fibrosis. Jan2025, Vol. 24 Issue 1, p10-15. 6p.

مصطلحات موضوعية: *INDIVIDUALIZED medicine, *CYSTIC fibrosis transmembrane conductance regulator, *COMPANION diagnostics, *CELL lines, *CYSTIC fibrosis

12

Academic Journal

Differential times of submission and approval of CFTR modulators for the treatment of Cystic Fibrosis in the United States and the European Union.

المؤلفون: Costa, Enrico¹ (AUTHOR) e.costa@uu.nl, Girotti, Silvia² (AUTHOR), Mathieu, Clément³ (AUTHOR), Castellani, Carlo⁴ (AUTHOR), Ross, Joseph S.⁵ (AUTHOR), Taylor-Cousar, Jennifer L.⁶ (AUTHOR), Leufkens, Hubert G.M.⁷ (AUTHOR)

المصدر: Journal of Cystic Fibrosis. Jan2025, Vol. 24 Issue 1, p125-132. 8p.

مصطلحات موضوعية: *CYSTIC fibrosis transmembrane conductance regulator, *CYSTIC fibrosis, *MARKETING, *WEBSITES, *DECISION making

الشركة/الكيان: EUROPEAN Medicines Agency , UNITED States. Food & Drug Administration

Reviews & Products: NEW York Times, The (Newspaper)

13

Academic Journal

Efficacy and safety of LAU-7b in a Phase 2 trial in adults with cystic fibrosis.

المؤلفون: Konstan, Michael W.¹ (AUTHOR), Polineni, Deepika² (AUTHOR), Chmiel, James F.³ (AUTHOR), Bilodeau, Lara⁴ (AUTHOR), Middleton, Peter G.⁵ (AUTHOR), Matouk, Elias⁶ (AUTHOR), Houle, Jean-Marie⁷ (AUTHOR), Pislariu, Radu⁷ (AUTHOR), Colin, Patrick⁷ (AUTHOR), Kianicka, Irenej⁷ (AUTHOR), Potvin, Diane⁸ (AUTHOR), Radzioch, Danuta⁶ (AUTHOR), Kotsimbos, Tom⁹ (AUTHOR), Zuckerman, Jonathan B.¹⁰ (AUTHOR), Nasr, Samya Z.¹¹ (AUTHOR), Liou, Theodore G.¹² (AUTHOR), Lands, Larry C.^1,6 (AUTHOR) larry.lands@mcgill.ca

المصدر: Journal of Cystic Fibrosis. Jan2025, Vol. 24 Issue 1, p83-90. 8p.

مصطلحات موضوعية: *FORCED expiratory volume, *CYSTIC fibrosis transmembrane conductance regulator, *TREATMENT effectiveness, *CYSTIC fibrosis, *MEMBRANE lipids

14

Academic Journal

Inflammation‐induced loss of CFTR‐expressing airway ionocytes in non‐eosinophilic asthma.

المؤلفون: Chen, Ling^1,2 (AUTHOR), A. Hoefel, Gabriela^1,2 (AUTHOR), Pathinayake, Prabuddha S.^2,3 (AUTHOR), Reid, Andrew^2,3 (AUTHOR), Pillar, Amber L.^1,2 (AUTHOR), Kelly, Coady^1,2 (AUTHOR), Tan, HuiYing^1,2 (AUTHOR), Ali, Ayesha^1,2 (AUTHOR), Kim, Richard Y.^1,2,4 (AUTHOR), Hansbro, Philip M.^1,5 (AUTHOR), Brody, Steven L.⁶ (AUTHOR), Foster, Paul S.^1,2 (AUTHOR), Horvat, Jay C.^1,2 (AUTHOR), Riveros, Carlos² (AUTHOR), Awatade, Nikhil^2,3 (AUTHOR), Wark, Peter A. B.^2,3,7,8 (AUTHOR), Kaiko, Gerard E.^1,2 (AUTHOR) gerard.kaiko@newcastle.edu.au

المصدر: Respirology. Jan2025, Vol. 30 Issue 1, p25-40. 16p.

مصطلحات موضوعية: *CYSTIC fibrosis transmembrane conductance regulator, *CHRONIC obstructive pulmonary disease, *CYSTIC fibrosis, *ION transport (Biology), *AIRWAY (Anatomy)

15

Dissertation/ Thesis

Efecto de la suplementación con ácido docosahexaenoico (DHA) en pacientes pediátricos con fibrosis quística: Ensayo clínico aleatorizado controlado con placebo

المؤلفون: Ayats Vidal, Roser

Thesis Advisors: Bosque Garcia, Montserrat, Domingo i Pedrol, Joan Carles, Blanch Torra, Lluís

المصدر: TDX (Tesis Doctorals en Xarxa)

مصطلحات موضوعية: Fibrosi quística, Àcids grassos, DHA, Fibrosis quística, Ácidos grasos, Cystic fibrosis, Fatty acids, Ciències de la Salut

وصف الملف: application/pdf

URL الوصول: http://hdl.handle.net/10803/689187

View record in TDX

16

Academic Journal

Are school settings restricting access to daily physical activity for children with cystic fibrosis? Parents' perspectives and recommendations for practice.

المؤلفون: Powell, Emma¹ e.powell@newman.ac.uk, Woodfield, Lorayne A², Powell, Alexander J², Myers, Tony D², Barker, Miranda¹

المصدر: International Journal of Qualitative Studies on Health & Well-Being. Dec2024, Vol. 19 Issue 1, p1-12. 12p.

مصطلحات موضوعية: *LUNG physiology, *CYSTIC fibrosis treatment, *HEALTH services accessibility, *EMPIRICAL research, *INTERVIEWING, *PARENT attitudes, *EMOTIONS, *DESCRIPTIVE statistics, *TEACHERS, *THEMATIC analysis, *RESEARCH methodology, *PSYCHOLOGY of parents, *PHENOMENOLOGY, *DATA analysis software, *CYSTIC fibrosis, *PHYSICAL activity, *ACTIVITIES of daily living, *SCHOOL health services, *CHILDREN

مصطلحات جغرافية: UNITED Kingdom

Full Text Finder

17

Academic Journal

Achromobacter xylosoxidans totally implantable venous access device infection in a person with cystic fibrosis: Complex management considerations.

المؤلفون: Evans, Ieuan E. S.^1,2 (AUTHOR) ieuan.evans@health.qld.gov.au, Haqqani, Haris^2,3 (AUTHOR), Smith, Daniel^1,2 (AUTHOR), Reid, David W.^1,2,4 (AUTHOR)

المصدر: Respirology Case Reports. Dec2024, Vol. 12 Issue 12, p1-4. 4p.

مصطلحات موضوعية: *CYSTIC fibrosis, *COLONIZATION (Ecology), *ARTERIAL catheterization, *COAGULASE, *CYSTIC fibrosis transmembrane conductance regulator

Full Text Finder

18

Dissertation/ Thesis

Early pseudomonas aeruginosa treatment and long term lung function in pediatric cystic fibrosis

المؤلفون: Gascón Casaredi, Isabel

Thesis Advisors: Bosque Garcia, Montserrat, Monsó Molas, Eduard

المصدر: TDX (Tesis Doctorals en Xarxa)

مصطلحات موضوعية: Tractament antibiòtic, Tratamiento antibiótico, Antibiotic therapy, FIbrosi Quística, Fibrosis Quística, Cystic Fibrosis, Erradicació Pseudomonas aeruginosa, Erradicación Pseudomonas aeruginosa, Eradication Pseudomonas aeruginosa, Ciències de la Salut

Time: 616.2

وصف الملف: application/pdf

URL الوصول: http://hdl.handle.net/10803/689679

View record in TDX

19

Academic Journal

Metabolomic profiling of saliva from cystic fibrosis patients.

المؤلفون: Caterino, M.^1,2 (AUTHOR), Costanzo, M.^1,2 (AUTHOR), Castaldo, A.^3,4 (AUTHOR), Iacotucci, P.⁵ (AUTHOR), Carnovale, V.⁴ (AUTHOR), Ruoppolo, M.^1,2 (AUTHOR), Gelzo, M.^1,2 (AUTHOR) monica.gelzo@unina.it, Castaldo, G.^1,2 (AUTHOR)

المصدر: Scientific Reports. 1/4/2025, Vol. 14 Issue 1, p1-12. 12p.

مصطلحات موضوعية: *CYSTIC fibrosis, *EXOCRINE pancreatic insufficiency, *KREBS cycle, *PSEUDOMONAS aeruginosa, *LIVER diseases, *SALIVA

Full Text Finder

20

Academic Journal

Evidence for secondary ciliary dyskinesia in patients with cystic fibrosis.

المؤلفون: Bonhiver, Romane^1,2 (AUTHOR) rbonhiver@uliege.be, Bricmont, Noemie^1,2 (AUTHOR), Pirotte, Maud¹ (AUTHOR), Wuidart, Marc-Antoine³ (AUTHOR), Monseur, Justine⁴ (AUTHOR), Benchimol, Lionel⁵ (AUTHOR), Poirrier, Anne-Lise⁵ (AUTHOR), Moermans, Catherine^1,6 (AUTHOR), Calmés, Doriane⁶ (AUTHOR), Schleich, Florence^1,6 (AUTHOR), Louis, Renaud^1,6 (AUTHOR), Seghaye, Marie-Christine⁷ (AUTHOR), Kempeneers, Céline^1,2 (AUTHOR)

المصدر: Journal of Cystic Fibrosis. Jan2025, Vol. 24 Issue 1, p193-200. 8p.

مصطلحات موضوعية: *CILIARY motility disorders, *CYSTIC fibrosis, *MUCOCILIARY system, *CELL culture, *CILIA & ciliary motion

تنقيح النتائج